Actively Recruiting

Phase 2
Phase 3
Age: 29Days - 17Years
All Genders
NCT05714085

Efficacy, Safety, and Pharmacokinetics of Vericiguat in Pediatric Participants With Heart Failure Due to Left Ventricular Systolic Dysfunction (MK-1242-036)

Led by Merck Sharp & Dohme LLC · Updated on 2026-05-11

342

Participants Needed

106

Research Sites

463 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

This study aims to compare the efficacy of vericiguat versus placebo on change in n-terminal pro-brain natriuretic peptide (NTproBNP) from baseline to Week 16 of the Base Period. The primary hypothesis is that vericiguat is superior to placebo in reducing NT-proBNP at Week 16 of the Base Period.

CONDITIONS

Official Title

Efficacy, Safety, and Pharmacokinetics of Vericiguat in Pediatric Participants With Heart Failure Due to Left Ventricular Systolic Dysfunction (MK-1242-036)

Who Can Participate

Age: 29Days - 17Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Has symptomatic chronic heart failure resulting from systemic left ventricular systolic dysfunction.
  • Has biventricular physiology with a morphologic systemic left ventricle.
  • Is currently receiving stable medical therapy for heart failure.
  • Has left ventricular ejection fraction less than 45% assessed within 3 months before randomization.
  • Is any sex/gender, aged more than 28 days to less than 18 years inclusive, and weighs at least 3 kg.
  • Female participants must not be pregnant or breastfeeding and must meet additional contraceptive or pregnancy test requirements.
  • For Extension Period: Was randomized, received at least 1 dose of study drug, did not permanently stop study drug, and completed Week 52 visit and safety follow-up of the Base Period.
Not Eligible

You will not qualify if you...

  • Is clinically unstable, including symptomatic hypotension or recent intravenous inotrope, vasodilator, or diuretic use.
  • Has allergy or sensitivity to vericiguat or related substances.
  • Has single ventricle heart disease or a systemic right ventricle.
  • Has had or is awaiting heart transplantation, or has an implanted ventricular assist device.
  • Has uncontrolled sustained or symptomatic dysrhythmia.
  • Had recent cardiovascular surgery or intervention for congenital heart defects.
  • Has unoperated or residual significant congenital heart malformations.
  • Has hypertrophic or restrictive cardiomyopathy.
  • Has active or recent myocarditis.
  • Has acute coronary syndrome, recent coronary intervention, or need for coronary revascularization.
  • Has symptomatic carotid stenosis or cerebrovascular disease.
  • Has severe pulmonary hypertension.
  • Requires continuous home oxygen for lung disease or has interstitial lung disease.
  • Has severe chronic kidney disease.
  • Has serious liver disorder or Child Pugh Class C.
  • Has gastrointestinal or biliary disorders affecting medication processing.
  • Has significant bone disease affecting bone formation.
  • Uses or will use phosphodiesterase type 5 inhibitors or sGC stimulators.
  • Received COVID-19 vaccine within 1 week before randomization.

AI-Screening

AI-Powered Screening

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Trial Site Locations

Total: 106 locations

1

The Regents of the University of California - Los Angeles (UCLA Pediatrics) ( Site 0002)

Los Angeles, California, United States, 90095

Actively Recruiting

2

Lucile Packard Children's Hospital ( Site 0040)

Palo Alto, California, United States, 94304

Actively Recruiting

3

Loma Linda University Health System ( Site 0008)

San Bernardino, California, United States, 92408

Actively Recruiting

4

Children's Hospital Colorado ( Site 0012)

Aurora, Colorado, United States, 80045

Actively Recruiting

5

Children's National Medical Center ( Site 0020)

Washington D.C., District of Columbia, United States, 20010

Actively Recruiting

6

Johns Hopkins All Children's Hospital ( Site 0029)

St. Petersburg, Florida, United States, 33701

Actively Recruiting

7

Children's Healthcare of Atlanta - Arthur M. Blank Hospital ( Site 0001)

Atlanta, Georgia, United States, 30329

Actively Recruiting

8

Boston Children's Hospital ( Site 0035)

Boston, Massachusetts, United States, 02115

Actively Recruiting

9

C.S. Mott Children's Hospital ( Site 0033)

Ann Arbor, Michigan, United States, 48109

Actively Recruiting

10

Washington University-Pediatric Cardiology/ St. Louis Children's Hospital ( Site 0006)

St Louis, Missouri, United States, 63110

Actively Recruiting

11

Columbia University Medical Center-Pediatric Cardiology ( Site 0016)

New York, New York, United States, 10032

Actively Recruiting

12

The Children's Hospital at Montefiore ( Site 0030)

The Bronx, New York, United States, 10467

Actively Recruiting

13

Cincinnati Children's Hospital Medical Center ( Site 0034)

Cincinnati, Ohio, United States, 45229

Actively Recruiting

14

Cleveland Clinic-Cleveland Clinic Chidren's ( Site 0022)

Cleveland, Ohio, United States, 44195

Actively Recruiting

15

Children's Hospital of Philadelphia (CHOP) ( Site 0004)

Philadelphia, Pennsylvania, United States, 19104

Actively Recruiting

16

Children's Hospital of Pittsburgh ( Site 0010)

Pittsburgh, Pennsylvania, United States, 15224

Actively Recruiting

17

Le Bonheur Children's Hospital ( Site 0007)

Memphis, Tennessee, United States, 38103

Actively Recruiting

18

Children's Health-The Heart Center ( Site 0015)

Dallas, Texas, United States, 75235

Actively Recruiting

19

Texas Children's Hospital ( Site 0039)

Houston, Texas, United States, 77030

Actively Recruiting

20

Seattle Children's Hospital-Cardiology/Fetal Therapy ( Site 0019)

Seattle, Washington, United States, 98105

Actively Recruiting

21

Centre Hospitalier Régional de la Citadelle ( Site 0302)

Liège, Liege, Belgium, 4000

Actively Recruiting

22

UZ Gent ( Site 0301)

Ghent, Oost-Vlaanderen, Belgium, 9000

Actively Recruiting

23

UZ Leuven ( Site 0300)

Leuven, Vlaams-Brabant, Belgium, 3000

Actively Recruiting

24

Instituto Dante Pazzanese de Cardiology ( Site 0402)

São Paulo, São Paulo, Brazil, 04012-909

Actively Recruiting

25

Incor - Instituto do Coracao ( Site 0400)

São Paulo, Brazil, 05403-000

Actively Recruiting

26

Stollery Children's Hospital ( Site 0501)

Edmonton, Alberta, Canada, T6G 2B7

Actively Recruiting

27

Centre intégré universitaire de santé et de services sociaux-Centre de recherche du CHUS ( Site 0502)

Sherbrooke, Quebec, Canada, J1H 5H4

Actively Recruiting

28

Clinica Somer ( Site 0607)

Rionegro, Antioquia, Colombia, 054040

Actively Recruiting

29

Ciensalud Ips S A S ( Site 0608)

Barranquilla, Atlántico, Colombia, 08001

Actively Recruiting

30

Fundación Cardioinfantil Instituto de Cardiología ( Site 0603)

Bogotá, Bogota D.C., Colombia, 110131

Actively Recruiting

31

Fundación Valle del Lili ( Site 0604)

Cali, Valle del Cauca Department, Colombia, 760032

Actively Recruiting

32

Clínica Imbanaco S.A.S ( Site 0602)

Cali, Valle del Cauca Department, Colombia, 760042

Actively Recruiting

33

Klinički bolnički centar Zagreb ( Site 3700)

Zagreb, City of Zagreb, Croatia, 10000

Actively Recruiting

34

Rigshospitalet-BørneUngeAfdelingen ( Site 0800)

Copenhagen, Capital Region, Denmark, DK-2100

Actively Recruiting

35

Tampereen yliopistollinen sairaala-Pediatric Early Phase Trials Unit ( Site 0900)

Tampere, Pirkanmaa, Finland, 33520

Actively Recruiting

36

CHU Bordeaux Haut-Leveque ( Site 1000)

Pessac, Aquitaine, France, 33600

Completed

37

Centre Hospitalier Universitaire de Nantes - Hôpital Femme-Enfant-Adolescent Chu De Nantes ( Site 1002)

Nantes, Loire-Atlantique, France, 44093

Completed

38

CHU Lille - Institut Coeur Poumon ( Site 1005)

Lille, Nord, France, 59037

Completed

39

Assistance Publique Hôpitaux de Marseille - Hôpital de la Timone ( Site 1003)

Marseille, Provence-Alpes-Côte d'Azur Region, France, 13005

Completed

40

Hôpital Universitaire Necker Enfants Malades ( Site 1001)

Paris, France, 75015

Completed

41

Assistance Publique - Hopitaux de Paris (AP-HP) - Hopital Robert Debre - Centre Hospitalo Universita ( Site 1004)

Paris, France, 75019

Completed

42

Universitaetsklinikum Freiburg ( Site 1102)

Freiburg im Breisgau, Baden-Wurttemberg, Germany, 79106

Actively Recruiting

43

Universitaetsklinikum Heidelberg ( Site 1100)

Heidelberg, Baden-Wurttemberg, Germany, 69120

Completed

44

Kinderklinik des Uni-Klinikums Erlangen ( Site 1104)

Erlangen, Bavaria, Germany, 91054

Actively Recruiting

45

Medizinische Hochschule Hannover ( Site 1108)

Hanover, Lower Saxony, Germany, 30625

Actively Recruiting

46

Deutsches Herzzentrum Berlin ( Site 1101)

Berlin, Germany, 13353

Actively Recruiting

47

Gottsegen György Országos Kardiovaszkuláris Intézet-Gyermeksziv Kozpont ( Site 1300)

Budapest, Hungary, 1096

Actively Recruiting

48

Children's Health Ireland (CHI) at Crumlin ( Site 1400)

Dublin, Ireland, D12 N512

Actively Recruiting

49

IRCCS Istituto Giannina Gaslini ( Site 1603)

Genoa, Liguria, Italy, 16147

Actively Recruiting

50

Ospedale dei Bambini "Vittore Buzzi" ( Site 1606)

Milan, Lombardy, Italy, 20154

Actively Recruiting

51

Ospedale Infantile Regina Margherita ( Site 1604)

Turin, Piedmont, Italy, 10126

Actively Recruiting

52

Ospedale Pediatrico Bambino Gesù IRCCS ( Site 1602)

Rome, Roma, Italy, 00165

Actively Recruiting

53

A.O.Universitaria Meyer ( Site 1600)

Florence, Tuscany, Italy, 50139

Completed

54

Azienda Ospedale - Università Padova ( Site 1601)

Padova, Veneto, Italy, 35128

Actively Recruiting

55

Hospital Universiti Sains Malaysia ( Site 1703)

Kota Bharu, Kelantan, Malaysia, 16150

Actively Recruiting

56

University Malaya Medical Centre ( Site 1701)

Lembah Pantai, Kuala Lumpur, Malaysia, 59100

Actively Recruiting

57

Hospital Queen Elizabeth II ( Site 1706)

Kota Kinabalu, Sabah, Malaysia, Kota Kinab

Actively Recruiting

58

Hospital Tunku Azizah-Paediatric ( Site 1700)

Kuala Lumpur, Malaysia, 50300

Actively Recruiting

59

Institut Jantung Negara ( Site 1705)

Kuala Lumpur, Malaysia, 50400

Actively Recruiting

60

Morales Vargas Centro de Investigacion ( Site 1810)

León, Guanajuato, Mexico, 37000

Actively Recruiting

61

CINVEC Medica ( Site 1814)

Guadalajara, Jalisco, Mexico, 44690

Actively Recruiting

62

Instituto Nacional de Pediatria ( Site 1803)

Mexico City, Mexico City, Mexico, 04530

Actively Recruiting

63

Hospital Universitario "Dr. Jose Eleuterio Gonzalez"-Pediatria ( Site 1816)

Monterrey, Nuevo León, Mexico, 66460

Actively Recruiting

64

INVECORDIS S.C. ( Site 1808)

Hacienda de Las Palmas, State of Mexico, Mexico, 52763

Actively Recruiting

65

Centro de Estudios de Investigacion Metabolicos y Cardiovasculares ( Site 1800)

Ciudad Madero, Tamaulipas, Mexico, 89440

Actively Recruiting

66

Centro de Atención e Investigación Clínica ( Site 1813)

Aguascalientes, Mexico, 20129

Actively Recruiting

67

UROLAP ( Site 1812)

Colima, Mexico, 28000

Actively Recruiting

68

Instituto Nacional de Cardiologia Ignacio Chavez ( Site 1804)

México, Mexico, 14080

Actively Recruiting

69

Erasmus Medisch Centrum ( Site 1900)

Rotterdam, South Holland, Netherlands, 3015 CN

Actively Recruiting

70

University Medical Center Groningen ( Site 1901)

Groningen, Netherlands, 9713 GZ

Actively Recruiting

71

Universitair Medisch Centrum Utrecht ( Site 1902)

Utrecht, Netherlands, 3584 CX

Actively Recruiting

72

Auckland City Hospital ( Site 2000)

Auckland, New Zealand, 1023

Actively Recruiting

73

Instituto Nacional Cardiovascular INCOR Carlos Peschiera Carrillo - EsSalud ( Site 2100)

Jesús María, Lima, Peru, 15072

Actively Recruiting

74

Uniwersyteckie Centrum Kliniczne-Klinika Kardiologii Dziecięcej i Wad Wrodzonych Serca ( Site 2302)

Gdansk, Pomeranian Voivodeship, Poland, 80-952

Completed

75

Unidade Local de Saude Lisboa Ocidental - Hospital de Santa Cruz ( Site 2401)

Lisbon, Lisbon District, Portugal, 2790-134

Actively Recruiting

76

Unidade Local de Saude de Santa Maria - Hospital de Santa Maria ( Site 2402)

Lisbon, Portugal, 1649-035

Actively Recruiting

77

Unidade Local de Saúde de São João ( Site 2403)

Porto, Portugal, 4200-319

Actively Recruiting

78

Childrens University Hospital ( Site 4200)

Belgrade, Beograd, Serbia, 11000

Actively Recruiting

79

Institut za zdravstvenu zastitu majke i deteta Srbije ( Site 4220)

Belgrade, Beograd, Serbia, 11000

Actively Recruiting

80

Institute for Child and Youth Helth Care of Vojvodina ( Site 4210)

Novi Sad, Vojvodina, Serbia, 21000

Actively Recruiting

81

National University Hospital-Paediatrics ( Site 2600)

Singapore, South West, Singapore, 119074

Actively Recruiting

82

KK Women's and Children's Hospital ( Site 2601)

Singapore, South West, Singapore, 229899

Actively Recruiting

83

TREAD Research ( Site 2700)

Cape Town, Western Cape, South Africa, 7500

Actively Recruiting

84

Children's Heart Disease Research Unit ( Site 2704)

Cape Town, Western Cape, South Africa, 7700

Actively Recruiting

85

Pusan National University Yangsan Hospital ( Site 2802)

Pusan, Kyongsangnam-do, South Korea, 50612

Actively Recruiting

86

Seoul National University Hospital ( Site 2803)

Seoul, South Korea, 03080

Actively Recruiting

87

Severance Hospital, Yonsei University Health System ( Site 2800)

Seoul, South Korea, 03722

Actively Recruiting

88

Samsung Medical Center ( Site 2801)

Seoul, South Korea, 06351

Actively Recruiting

89

Hospital Sant Joan de Déu-Pediatric cardiology ( Site 2902)

Esplugues de Llobregat, Barcelona, Spain, 08950

Actively Recruiting

90

Hospital Universitari Vall d'Hebron ( Site 2903)

Barcelona, Catalonia, Spain, 08035

Actively Recruiting

91

Hospital Materno-Infantil Teresa Herrera ( Site 2905)

A Coruña, La Coruna, Spain, 15009

Actively Recruiting

92

HOSPITAL GENERAL UNIVERSITARIO GREGORIO MARAÑON ( Site 2904)

Madrid, Madrid, Comunidad de, Spain, 28007

Actively Recruiting

93

Hospital Universitario La Paz ( Site 2912)

Madrid, Spain, 28046

Actively Recruiting

94

HOSPITAL UNIVERSITARIO VIRGEN DEL ROCIO ( Site 2907)

Seville, Spain, 41013

Actively Recruiting

95

Skånes Universitetssjukhus Lund ( Site 3000)

Lund, Skåne County, Sweden, 22185

Actively Recruiting

96

Astrid Lindgrens Barnsjukhus ( Site 3001)

Solna, Stockholm County, Sweden, 171 64

Actively Recruiting

97

Faculty of Medicine Siriraj Hospital ( Site 3200)

Bangkoknoi, Bangkok, Thailand, 10700

Actively Recruiting

98

Faculty of Medicine - Khon Kaen University ( Site 3202)

Muang, Changwat Khon Kaen, Thailand, 40002

Completed

99

Maharaj Nakorn Chiang Mai Hospital-Department of Pediatrics ( Site 3201)

Chiang Mai, Thailand, 50200

Actively Recruiting

100

Hacettepe Universite Hastaneleri ( Site 3304)

Ankara, Turkey (Türkiye), 06230

Actively Recruiting

101

Baskent Universitesi Ankara Hastanesi ( Site 3301)

Ankara, Turkey (Türkiye), 06490

Actively Recruiting

102

Ankara Bilkent Şehir Hastanesi. ( Site 3300)

Ankara, Turkey (Türkiye), 06800

Actively Recruiting

103

Dr. Siyami Ersek Göğüs Kalp Ve Damar Cerrahisi Eğitim Ve Araştırma Hastanesi ( Site 3302)

Istanbul, Turkey (Türkiye), 34668

Actively Recruiting

104

S.B.Ü. DR. BEHÇET UZ ÇOCUK HASTALIKLARI VE CERRAHİSİ EĞİTİM VE ARAŞTIRMA HASTANESİ ( Site 3303)

Izmir, Turkey (Türkiye), 35210

Actively Recruiting

105

Great Ormond Street Hospital For Children NHS Foundation Trust ( Site 3401)

London, London, City of, United Kingdom, WC1N 3JH

Actively Recruiting

106

Freeman Hospital ( Site 3400)

Newcastle upon Tyne, United Kingdom, NE7 7DN

Actively Recruiting

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Research Team

T

Toll Free Number

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

QUADRUPLE

Allocation

RANDOMIZED

Model

PARALLEL

Primary Purpose

TREATMENT

Number of Arms

3

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