Actively Recruiting

Phase Not Applicable
Age: 12Years +
All Genders
ID04055220

Efficacy and Safety of Regorafenib as Maintenance Therapy After First-line Treatment in Patients With Bone Sarcomas

Led by Centre Leon Berard · Updated on 2026-02-17

168

Participants Needed

16

Research Sites

N/A

Total Duration

On this page

AI-Summary

What this Trial Is About

Researchers are investigating whether regorafenib can help control bone sarcoma after initial treatment. Bone sarcomas are rare cancers of the bone with several types, including osteosarcomas, Ewing sarcomas, and chondrosarcomas. Despite advances, survival rates have plateaued, making new treatment options essential. This phase II study explores if adding regorafenib as maintenance therapy after first-line treatment can delay return or progression of the disease compared to standard surveillance. Participants are randomly assigned to one of two groups. One group receives regorafenib in 28-day cycles: 21 days of treatment followed by 7 days off, for up to 12 months. Dosage varies based on age and body surface area. The other group undergoes standard surveillance without additional treatment but with the same follow-up schedule. Close monitoring will evaluate disease control and safety in both groups. During the study, participants will have regular visits for assessments including relapse-free survival over up to 5 years, treatment failure, overall survival, quality of life, safety, and treatment adherence. Clinical tests will check blood counts, organ function, and possible side effects. Patients will be monitored closely to track health status and disease recurrence throughout the study duration.

CONDITIONS

Brief Title

Efficacy and Safety of Regorafenib as Maintenance Therapy After First-line Treatment in Patients With Bone Sarcomas

Who Can Participate

Age: 12Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Age 12 years or older at consent
  • Histologically confirmed primary bone sarcoma including osteosarcoma, Ewing sarcoma, chondrosarcoma, undifferentiated pleomorphic sarcoma, leiomyosarcoma, or angiosarcoma
  • Completed standard multimodal treatment (chemotherapy and/or surgery) appropriate to sarcoma subtype
  • Recovery to grade 0 or 1 toxicity level from prior treatment (except alopecia, anemia, hypothyroidism)
  • Interval of 4 weeks to 2 months since last chemotherapy before randomization
  • Confirmed complete remission or no evidence of active disease
  • Life expectancy greater than 12 months
  • Karnofsky Performance status ≥70 (under 18 years) or ECOG <2 (adults)
  • Adequate bone marrow, kidney, and liver function within 7 days before treatment start
  • INR/PTT ≤1.5 times normal or stable if on blood thinners
  • Use of adequate contraception during and after treatment as specified
  • Negative pregnancy test for women of childbearing potential
  • Signed informed consent
  • Willing and able to comply with study procedures
  • Covered by medical insurance
  • Body surface area ≥1.30 m² at consent
Not Eligible

You will not qualify if you...

  • Prior treatment with any VEGFR inhibitor (e.g., sunitinib, sorafenib, pazopanib, bevacizumab)
  • Soft tissue sarcomas or chordomas
  • Other cancers within 3 years except certain skin or cervical cancers
  • Significant heart conditions including low ejection fraction, recent heart attack, or unstable angina
  • Uncontrolled high blood pressure
  • Recent blood clots or embolic events within 6 months
  • Major surgery or injury within 28 days before treatment
  • Ongoing infections above grade 2
  • Known HIV infection not controlled as specified
  • Active or untreated hepatitis B or C
  • Dehydration grade above 1
  • Difficulty swallowing oral medications or gastrointestinal conditions affecting absorption
  • Seizure disorder requiring medication
  • Concurrent participation in another investigational trial
  • Allergic reactions to study drug components
  • Pregnant or breastfeeding women
  • Psychological or social conditions affecting study compliance
  • History of non-compliance with medical regimens
  • Interstitial lung disease with symptoms
  • Non-healing wounds or fractures
  • History of significant bleeding disorders or recent severe bleeding
  • Serious unrelated systemic illnesses
  • Use of prohibited medications
  • Under legal guardianship or curatorship

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Your Study Journey

Screening

Duration - 2 to 4 weeks

Participants are screened for eligibility to participate in the trial.

1 visit (in-person)

Treatment

Duration - Up to 12 months

Participants receive treatment by taking regorafenib orally in cycles of 21 days on treatment followed by 7 days off treatment, for up to 13 cycles (maximum 12 months). Dose adjustments may occur based on tolerance.

Monthly visits during treatment cycles

Follow-up

Duration - Up to 5 years

Participants are monitored for relapse, survival, quality of life, and safety outcomes after completing treatment or surveillance.

Regular follow-up visits over 5 years

Trial Site Locations

Total: 16 locations

1

Hôpital Jean Minjoz

Besançon, France, 25000

Actively Recruiting

2

Institut Bergonié

Bordeaux, France, 33076

Actively Recruiting

3

Centre Oscar Lambret

Lille, France, 59020

Actively Recruiting

4

Centre Léon Bérard

Lyon, France, 69373

Actively Recruiting

5

APHM - Hôpital Timone

Marseille, France, 13385

Actively Recruiting

6

ICM Val d'Aurelle

Montpellier, France, 34298

Not Yet Recruiting

7

Institut Curie

Paris, France, 75005

Actively Recruiting

8

APHP Hôpital Cochin

Paris, France, 75014

Actively Recruiting

9

Centre Hospitalier Universitaire de Poitiers

Poitiers, France, 86000

Not Yet Recruiting

10

Centre Hospitalier Universitaire de Saint-Etienne (CHUSE)

Saint-Etienne, France, 42055

Actively Recruiting

11

ICO René Gauducheau

Saint-Herblain, France, 44805

Actively Recruiting

12

Centre Paul Strauss - Strasbourg

Strasbourg, France, 67033

Actively Recruiting

13

Centre Hospitalier Régional de Strasbourg Hautepierre

Strasbourg, France, 67098

Actively Recruiting

14

IUCT-Oncopole

Toulouse, France, 31059

Not Yet Recruiting

15

ICL Alexis Vautrin

Vandœuvre-lès-Nancy, France, 54519

Not Yet Recruiting

16

Institut Gustave Roussy

Villejuif, France, 94805

Actively Recruiting

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Research Team

J

Julien GAUTIER

How is the study designed?

Study Type

INTERVENTIONAL

Masking

SINGLE

Allocation

RANDOMIZED

Model

PARALLEL

Primary Purpose

TREATMENT

Number of Arms

2

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