Actively Recruiting

Phase 3
Age: 2Years - 55Years
All Genders
NCT05066217

An Efficacy and Safety Study of Clemizole HCl in Patients With Lennox-Gastaut Syndrome

Led by Epygenix · Updated on 2026-04-15

260

Participants Needed

20

Research Sites

238 weeks

Total Duration

On this page

Sponsors

E

Epygenix

Lead Sponsor

H

Harmony Biosciences Management, Inc.

Collaborating Sponsor

AI-Summary

What this Trial Is About

This is a multicenter, Phase 3, randomized, double-blind, placebo-controlled study designed to evaluate the efficacy and safety of clemizole HCL (EPX-100) as adjunctive therapy in children and adult participants with Lennox-Gastaut syndrome (LGS).

CONDITIONS

Official Title

An Efficacy and Safety Study of Clemizole HCl in Patients With Lennox-Gastaut Syndrome

Who Can Participate

Age: 2Years - 55Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Males or females aged 2 to 55 years at the time of screening
  • Participant or legal representative able and willing to provide written informed consent or assent
  • Diagnosis of Lennox-Gastaut Syndrome with at least one type of countable major motor seizure
  • History of EEG consistent with Lennox-Gastaut Syndrome, including abnormal background activity and either slow spike-wave discharges (<2.5 Hz) or paroxysmal fast activity during sleep
  • Abnormal cognitive development
  • Onset of seizures at 11 years of age or younger
Not Eligible

You will not qualify if you...

  • Known allergy, sensitivity, or previous exposure to clemizole HCl
  • History of long QT syndrome or significant abnormality in electrocardiogram such as recent myocardial infarction or serious arrhythmia
  • Family history of sudden cardiac death, unexplained death, or death from a primary dysrhythmia linked to QT prolongation
  • Seizures caused by illicit drug or alcohol use, infection, neoplasm, demyelinating disease, degenerative neurological disease, progressive CNS disease, metabolic illness, recent anoxic episode requiring resuscitation in last 6 months, or any condition that may affect seizure control
  • Planned epilepsy surgery during the study or epilepsy surgery within 6 months prior to screening
  • Use of fenfluramine concurrently
  • Prior or concurrent use of lorcaserin

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 20 locations

1

Arkansas Children's Hospital

Little Rock, Arkansas, United States, 72202

Active, Not Recruiting

2

UC Irvine Medical Center

Orange, California, United States, 92868

Active, Not Recruiting

3

UCI Center for Innovative Health Therapies

Orange, California, United States, 92868

Actively Recruiting

4

Nemours Children's Health

Wilmington, Delaware, United States, 19803

Not Yet Recruiting

5

Rare Disease Research

Kissimmee, Florida, United States, 34746

Suspended

6

University of Miami Miller School of Medicine

Miami, Florida, United States, 33136

Actively Recruiting

7

Pediatric Neurology and Epilepsy Specialists

Winter Park, Florida, United States, 32789

Active, Not Recruiting

8

Re:Cognition Health

Chicago, Illinois, United States, 60611

Actively Recruiting

9

Norton Children's Medical Center

Louisville, Kentucky, United States, 40202

Active, Not Recruiting

10

Henry Ford Hospital

Detroit, Michigan, United States, 48202

Active, Not Recruiting

11

Minnesota Epilepsy Group, P.A.

Roseville, Minnesota, United States, 55102

Active, Not Recruiting

12

Children's Nebraska

Omaha, Nebraska, United States, 68114

Active, Not Recruiting

13

Neurology Center for Epilepsy and Seizures

Marlboro, New Jersey, United States, 07746

Actively Recruiting

14

Tekton Research

Marlboro, New Jersey, United States, 07746

Actively Recruiting

15

Weill Cornell Medicine/New York Presbyterian Hospital

New York, New York, United States, 10021

Actively Recruiting

16

Atrium Health STRIVE Research

Charlotte, North Carolina, United States, 28207

Active, Not Recruiting

17

On-Site Clinical Solution

Charlotte, North Carolina, United States, 28211

Active, Not Recruiting

18

Duke University Medical Center

Durham, North Carolina, United States, 27705

Actively Recruiting

19

PPD Virtual-Science 37, Inc.

Morrisville, North Carolina, United States, 27560

Active, Not Recruiting

20

UTHealth Houston

Houston, Texas, United States, 77030

Active, Not Recruiting

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Research Team

J

Juby Philip

CONTACT

C

Cindy Sandy

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

TRIPLE

Allocation

RANDOMIZED

Model

PARALLEL

Primary Purpose

TREATMENT

Number of Arms

3

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An Efficacy and Safety Study of Clemizole HCl in Patients With Lennox-Gastaut Syndrome | DecenTrialz