Actively Recruiting

Phase 3
Age: 1Day - 18Years
All Genders
NCT07232134

The Efficacy of Therapy in Patients With Acute Myeloid Leukemia and Down Syndrome in Russia

Led by Federal Research Institute of Pediatric Hematology, Oncology and Immunology · Updated on 2025-11-20

100

Participants Needed

1

Research Sites

388 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

This prospective non-randomized multicenter trial created based on protocol ML DS 2006 and aimed at standardization of current therapy approaches and creating a national network for diagnostic, treatment and monitoring of children (0-18 years) with AML and Down syndrome in Russia. Based on the results the investigators expect to increase long-term overall and event-free survival in children with AML and DS and reduce the immediate and remote toxicity of chemotherapy by reducing the dose load of chemotherapeutic drugs. The study protocol therapy for all patients includes four chemotherapy blocks: Course 1 AIE (cytarabine/idarubicin/etoposide) Course 2 AI (cytarabine/idarubicin) Course 3 HAD (high -dose cytarabine (1g)/daunorubicin) Course 4 HA (high-dose cytarabine) Safety to be monitored based on CTCAE v5.0

CONDITIONS

Official Title

The Efficacy of Therapy in Patients With Acute Myeloid Leukemia and Down Syndrome in Russia

Who Can Participate

Age: 1Day - 18Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Age 0-18 years
  • Diagnosis of AML or MDS with Down syndrome (constitutional trisomy 21 and mutation in the GATA1 gene)
  • Signed informed consent
Not Eligible

You will not qualify if you...

  • Children with Down syndrome and acute lymphoblastic leukemia (ALL)
  • Severe comorbidities contraindicating treatment according to the protocol
  • More than 14 days of prior intensive induction therapy
  • Refusal of all or important parts of therapy

AI-Screening

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Trial Site Locations

Total: 1 location

1

National medical research center of pediatric haematology, oncology and immulogy named after Dmytriy Rogachyov, Moscow, 117198

Moscow, Russia

Actively Recruiting

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Research Team

Z

Zalina A Abashidze, MD

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NA

Model

SINGLE_GROUP

Primary Purpose

TREATMENT

Number of Arms

1

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