Actively Recruiting

Phase 2
Age: 18Years +
All Genders
NCT03728335

Enasidenib (AG-221) Maintenance Post Allogeneic HCT in Patients With IDH2 Mutation

Led by City of Hope Medical Center · Updated on 2026-03-13

35

Participants Needed

2

Research Sites

391 weeks

Total Duration

On this page

Sponsors

C

City of Hope Medical Center

Lead Sponsor

N

National Cancer Institute (NCI)

Collaborating Sponsor

AI-Summary

What this Trial Is About

This phase II trial studies the side effects of using enasidenib as maintenance therapy in treating patients with acute myeloid leukemia with IDH2 mutation following donor stem cell transplant. Enasidenib may stop the growth of cancer cells by blocking some of the enzymes needed for cell growth.

CONDITIONS

Official Title

Enasidenib (AG-221) Maintenance Post Allogeneic HCT in Patients With IDH2 Mutation

Who Can Participate

Age: 18Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Provided informed consent or had a legally authorized representative consent
  • Agree to allow use of existing tumor biopsy tissue or have approval for exception
  • Eastern Cooperative Oncology Group (ECOG) score of 0, 1, or 2 or Karnofsky performance status of 70 or higher
  • Received allogeneic hematopoietic cell transplantation (HCT) from any stem cell source
  • Conditioning and graft-versus-host disease (GVHD) prophylaxis per investigator's choice
  • Diagnosed with acute myeloid leukemia (AML) with IDH2 mutation and showing less than 5% bone marrow blasts around day 30 post transplant
  • Patients with measurable residual disease allowed
  • Previous therapy with IDH2 inhibitors allowed
  • Absolute neutrophil count greater than 1000 within 28 days before treatment start
  • Hemoglobin level of at least 9.5 gm% within 28 days before treatment start
  • Platelet count above 50,000/mm3 or at least 20,000/mm3 if actively treating infections within 28 days before treatment start
  • Total bilirubin less than or equal to 1.5 times upper limit of normal, or less than 2.0 mg/dl if Gilbert's syndrome, within 28 days before treatment
  • Liver enzymes (AST/ALT) less than or equal to 2 times upper limit of normal and no active GVHD related liver issues
  • Creatinine clearance of at least 40/min/1.73 m2 within 28 days before treatment
  • Corrected QT interval less than or equal to 480 ms within 28 days before treatment
  • Negative tests for HIV, hepatitis B and C, and syphilis
  • Women of childbearing potential must have a negative pregnancy test and agree to effective birth control or abstain during the study and for 3 months after
  • Men of childbearing potential must agree to effective birth control or abstain during the study and for 3 months after
Not Eligible

You will not qualify if you...

  • History of allergic reactions to similar compounds as enasidenib
  • Active diarrhea that prevents taking oral medication
  • Uncontrolled serious illness
  • Active infection requiring antibiotics (treated infections allowed if controlled)
  • Known HIV or hepatitis B or C infection
  • Diagnosis of Gilbert's disease
  • Other active cancers except certain treated cancers in remission for over 2 years
  • Pregnant or breastfeeding women
  • Active grade II-IV acute graft-versus-host disease requiring high-dose steroids
  • Any condition that in the investigator's judgment would prevent safe study participation
  • Inability to comply with study procedures as judged by the investigator

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 2 locations

1

City of Hope Medical Center

Duarte, California, United States, 91010

Actively Recruiting

2

Moffitt Cancer Center

Tampa, Florida, United States, 33612

Actively Recruiting

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How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NA

Model

SINGLE_GROUP

Primary Purpose

TREATMENT

Number of Arms

1

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Enasidenib (AG-221) Maintenance Post Allogeneic HCT in Patients With IDH2 Mutation | DecenTrialz