Actively Recruiting

Phase 1
Phase 2
Age: 12Years +
All Genders
NCT04585750

The Evaluation of PC14586 in Patients With Advanced Solid Tumors Harboring a TP53 Y220C Mutation (PYNNACLE)

Led by PMV Pharmaceuticals, Inc · Updated on 2026-03-12

300

Participants Needed

76

Research Sites

374 weeks

Total Duration

On this page

Sponsors

P

PMV Pharmaceuticals, Inc

Lead Sponsor

M

Merck Sharp & Dohme LLC

Collaborating Sponsor

AI-Summary

What this Trial Is About

The Phase 2 monotherapy portion of this study is currently enrolling and will evaluate the efficacy and safety of PC14586 (INN rezatapopt) in participants with locally advanced or metastatic solid tumors harboring a TP53 Y220C mutation. The Phase 1 portion of the study will assess the safety, tolerability and preliminary efficacy of multiple dose levels of rezatapopt as monotherapy and in Phase 1b in combination with pembrolizumab.

CONDITIONS

Official Title

The Evaluation of PC14586 in Patients With Advanced Solid Tumors Harboring a TP53 Y220C Mutation (PYNNACLE)

Who Can Participate

Age: 12Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • At least 18 years old or 12 to 17 years old with Safety Review Committee approval
  • Have a locally advanced or metastatic solid tumor with a TP53 Y220C mutation
  • Eastern Cooperative Oncology Group (ECOG) status of 0 or 1
  • Previously treated with one or more anticancer therapies and have progressive disease
  • Have adequate organ function
  • Have measurable disease per RECIST v1.1 (Phase 2 only)
  • For Phase 1b combination therapy, must be anti-PD-1/PD-L1 naive or have progressed on such treatment
  • Have measurable disease (Phase 1b combination therapy)
Not Eligible

You will not qualify if you...

  • Received anticancer therapy within 21 days (or 5 half-lives) before study drug
  • Received radiotherapy within 14 days before study drug
  • Have a primary central nervous system tumor
  • History of leptomeningeal disease or spinal cord compression
  • Have brain metastases unless neurologically stable and not requiring steroids
  • Stroke or transient ischemic attack within 6 months before screening
  • Certain heart conditions within 6 months before screening, including unstable angina, heart attack, uncontrolled hypertension, congestive heart failure, QT prolongation, or rhythm abnormalities
  • Use of strong CYP3A4 inhibitors or CYP2C9 inducers within 14 days before first dose
  • History of gastrointestinal disease affecting drug absorption or inability to take oral medication
  • History of prior organ transplant
  • Active malignancy except treated cervical intraepithelial neoplasia or non-melanoma skin cancer
  • Active uncontrolled Hepatitis B, Hepatitis C, or HIV infection
  • Known KRAS mutation (Phase 2 only)
  • Prior therapy with anti-PD-1/PD-L1/PD-L2 or other T-cell receptor agents discontinued due to severe immune-related adverse event (Phase 1b combination)
  • Received live or live-attenuated vaccine within 30 days before first dose (Phase 1b combination)
  • Immunodeficiency or chronic systemic steroid therapy within 7 days before first dose (Phase 1b combination)
  • Severe hypersensitivity to pembrolizumab or its components (Phase 1b combination)
  • Active autoimmune disease requiring systemic treatment in past 2 years (Phase 1b combination)
  • History of radiation pneumonitis or active pneumonitis/interstitial lung disease requiring steroids (Phase 1b combination)
  • Active infection requiring systemic therapy (Phase 1b combination)
  • Known history of HIV infection (Phase 1b combination)
  • Previous treatment with rezatapopt

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 76 locations

1

University of California Irvine Chao Family Comprehensive Cancer Center

Irvine, California, United States, 92868

Actively Recruiting

2

University of San Diego Moores Cancer Center

La Jolla, California, United States, 92093

Not Yet Recruiting

3

UCLA Jonsson Comprehensive Cancer Center

Los Angeles, California, United States, 90024

Actively Recruiting

4

USC Norris Comprehensive Cancer Center

Los Angeles, California, United States, 90033

Actively Recruiting

5

Rocky Mountain Cancer Center

Denver, Colorado, United States, 80218

Actively Recruiting

6

Yale Cancer Center

New Haven, Connecticut, United States, 06519

Actively Recruiting

7

Medical Oncology Hematology Consultants

Newark, Delaware, United States, 19713

Actively Recruiting

8

University of Miami - Sylvester Comprehensive Cancer Center

Miami, Florida, United States, 33136

Actively Recruiting

9

Advent Health

Orlando, Florida, United States, 32803

Not Yet Recruiting

10

Florida Cancer Specialists South

Port Charlotte, Florida, United States, 33980

Actively Recruiting

11

Massachusetts General Hospital

Boston, Massachusetts, United States, 02114

Actively Recruiting

12

Dana Farber Cancer Institute

Boston, Massachusetts, United States, 02215

Actively Recruiting

13

Karmanos Cancer Institute

Detroit, Michigan, United States, 48201

Actively Recruiting

14

Columbia University

New York, New York, United States, 10032

Not Yet Recruiting

15

Memorial Sloan Kettering

New York, New York, United States, 10065

Actively Recruiting

16

Duke University

Durham, North Carolina, United States, 27705

Actively Recruiting

17

The Cleveland Clinic Taussig Cancer Center

Cleveland, Ohio, United States, 44195

Actively Recruiting

18

University of Oklahoma

Oklahoma City, Oklahoma, United States, 73104

Actively Recruiting

19

Oregon Health & Science University (OHSU)

Portland, Oregon, United States, 97210

Actively Recruiting

20

Abramson Cancer Center of the University of Pennsylvania

Philadelphia, Pennsylvania, United States, 19104

Actively Recruiting

21

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, United States, 15213

Not Yet Recruiting

22

WellSpan York Cancer Center

York, Pennsylvania, United States, 17403

Actively Recruiting

23

Medical University of South Carolina

Charleston, South Carolina, United States, 29425

Terminated

24

Sarah Cannon Research Institute

Nashville, Tennessee, United States, 37203

Actively Recruiting

25

New Experimental Therapeutics - NEXT Oncology

Austin, Texas, United States, 78705

Actively Recruiting

26

UTSW - Moody Outpatient Center - Parkland Health

Dallas, Texas, United States, 75235

Not Yet Recruiting

27

UT Southwest Simmons Cancer Center

Dallas, Texas, United States, 75390

Actively Recruiting

28

The University of Texas MD Anderson Cancer Center

Houston, Texas, United States, 77030

Actively Recruiting

29

New Experimental Therapeutics of San Antonio - NEXT Oncology

San Antonio, Texas, United States, 78229

Actively Recruiting

30

Virginia Cancer Specialists

Fairfax, Virginia, United States, 22031

Actively Recruiting

31

University of Washington, Fred Hutchinson Cancer Center

Seattle, Washington, United States, 98109

Actively Recruiting

32

University of Wisconsin Carbone Cancer Center

Madison, Wisconsin, United States, 53705

Actively Recruiting

33

Chris O'Brien Lifehouse Hospital

Camperdown, New South Wales, Australia

Actively Recruiting

34

Mater Cancer Care Centre

South Brisbane, Queensland, Australia

Actively Recruiting

35

Flinders Medical Center

Bedford Park, South Australia, Australia

Actively Recruiting

36

Monash Medical Centre

Clayton, Victoria, Australia

Actively Recruiting

37

Linear Clinical Research

Nedlands, Western Australia, Australia

Actively Recruiting

38

ICANS - Institut de cancérologie Strasbourg Europe

Strasbourg, Bas-Rhin, France

Actively Recruiting

39

Institut Bergonie

Bordeaux, Gironde, France

Actively Recruiting

40

Institut Claudius Regaud

Toulouse, Haute-Garonne, France

Actively Recruiting

41

EDOG Institut de Cancerologie de l'Ouest

Saint-Herblain, Loire-Atlantique, France

Actively Recruiting

42

Centre Jean Perrin

Clermont-Ferrand, Puy-de-Dôme, France

Actively Recruiting

43

Institut Gustave Roussy

Villejuif, Val-de-Marne, France

Actively Recruiting

44

Centre Léon Bérard Centre Régional de Lutte Contre Le Cancer

Lyon, France

Actively Recruiting

45

CHU de Nîmes

Nîmes, France, 30900

Actively Recruiting

46

Institute Cancer De Lorraine

Vandœuvre-lès-Nancy, France, 54519

Actively Recruiting

47

Nationale Centrum für Tumorerkrankungen (NCT) Heidelberg

Heidelberg, Baden-Wurttemberg, Germany

Actively Recruiting

48

Universitätsklinikum Augsburg

Augsburg, Bavaria, Germany

Actively Recruiting

49

Asklepios Klinik Altona

Hamburg, Free and Hanseatic City of Hamburg, Germany

Actively Recruiting

50

Universitätsklinikum Frankfurt

Frankfurt am Main, Hesse, Germany

Withdrawn

51

Universitätsklinikum Essen

Essen, North Rhine-Westphalia, Germany

Actively Recruiting

52

Fondazione Policlinico Universitario Agostino Gemelli IRCCS

Rome, Lazio, Italy

Actively Recruiting

53

Istituti Fisioterapici Ospitalieri - Istituto Nazionale Tumori Regina Elena

Rome, Lazio, Italy

Actively Recruiting

54

ASST Grande Ospedale Metropolitano Niguarda

Milan, Lombardy, Italy

Actively Recruiting

55

Fondazione IRCCS Istituto Nazionale Dei Tumori

Milan, Lombardy, Italy

Actively Recruiting

56

Istituto Europeo Di Oncologia

Milan, Lombardy, Italy

Actively Recruiting

57

Istituto Clinico Humanitas

Rozzano, Lombardy, Italy

Actively Recruiting

58

Fondazione del Piemonte per l'Oncologia (IRCCS)

Candiolo, Torino, Italy

Actively Recruiting

59

Humanitas San Pio X

Milan, Italy

Actively Recruiting

60

IRCCS - lstituto Nazionale Tumori - Fondazione G. Pascale

Naples, Italy, 80131

Actively Recruiting

61

National University Hospital

Kent Ridge, Singapore

Actively Recruiting

62

National Cancer Center of Singapore

Singapore, Singapore, 168582

Actively Recruiting

63

Asan Medical Center

Seoul, South Korea

Actively Recruiting

64

National Cancer Center

Seoul, South Korea

Actively Recruiting

65

Samsung Medical Center

Seoul, South Korea

Actively Recruiting

66

Seoul University Hospital

Seoul, South Korea

Actively Recruiting

67

Severance Hospital Yonsei University

Seoul, South Korea

Actively Recruiting

68

START MADRID_Hospital Universitario Fundacion Jimenez Diaz

Madrid, Madrid, Spain

Actively Recruiting

69

START MADRID_Hospital Universitario HM Sanchinarro - CIOCC

Madrid, Madrid, Spain

Actively Recruiting

70

Instituto de Investigacion Oncologica Vall d'Hebron (VHIO) - EPON

Barcelona, Spain

Actively Recruiting

71

NEXT Oncology-Hospital Quironsalud Barcelona

Barcelona, Spain

Actively Recruiting

72

Hospital Universitario 12 de Octubre

Madrid, Spain, 28041

Actively Recruiting

73

START Rioja

Rioja, Spain

Actively Recruiting

74

Hospital Clinico Universitario de Valencia

Valencia, Spain

Actively Recruiting

75

Sarah Cannon Research Institute UK

London, Middlesex, United Kingdom

Actively Recruiting

76

Freeman Hospital

Newcastle upon Tyne, Tyne and Wear, United Kingdom

Actively Recruiting

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Research Team

P

PMV Pharma Clinical Study Information Center

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NON_RANDOMIZED

Model

PARALLEL

Primary Purpose

TREATMENT

Number of Arms

9

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