Actively Recruiting

Phase 1
Phase 2
Age: 18Years - 65Years
All Genders
NCT06525636

A First-in-human Study of KK8123 in Adults With X-linked Hypophosphatemia

Led by Kyowa Kirin Co., Ltd. · Updated on 2025-11-14

24

Participants Needed

9

Research Sites

187 weeks

Total Duration

On this page

Sponsors

K

Kyowa Kirin Co., Ltd.

Lead Sponsor

K

Kyowa Kirin, Inc.

Collaborating Sponsor

AI-Summary

What this Trial Is About

A first-in-human study of KK8123 in adults with X-linked hypophosphatemia.

CONDITIONS

Official Title

A First-in-human Study of KK8123 in Adults With X-linked Hypophosphatemia

Who Can Participate

Age: 18Years - 65Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Male or female patients aged 18 to 65 years inclusive at the time of signing the informed consent form.
  • Body weight of at least 40 kg.
  • Diagnosed with X-linked hypophosphatemia (XLH) as documented by the investigator.
  • Fasting serum phosphorus level less than 2.5 mg/dL at Screening.
  • Renal TmP/GFR less than 2.5 mg/dL at Screening.
  • Estimated glomerular filtration rate (eGFR) of 60 mL/min or higher at Screening.
  • Corrected serum calcium level less than 10.8 mg/dL at Screening.
  • Signed informed consent form.
  • Agreement to maintain diet and exercise regimen from one week before dosing until the end of study.
  • Negative pregnancy test at Screening and willingness to have additional pregnancy tests during the study (for female participants).
  • Stable dose of chronic pain medications (if any) for at least 21 days prior to Screening, with a maximum of 60 mg oral morphine equivalents per day, and willingness to maintain stable dosing during the study.
  • Willingness to use contraception according to local guidelines during the study and for 5 months after the last dose (for sexually active participants of childbearing potential).
  • Willingness and ability to complete all study aspects and adhere to visit schedule and assessments as judged by the investigator.
Not Eligible

You will not qualify if you...

  • Use of burosumab within 7 months prior to informed consent for XLH patients previously treated with it.
  • Positive test for HIV antibody, hepatitis B surface antigen, or hepatitis C antibody at Screening.
  • Known hypersensitivity to any therapeutic monoclonal antibody ingredient.
  • Active infection at Screening.
  • Grade 3 or higher nephrocalcinosis confirmed by renal ultrasound.
  • Uncontrolled diabetes mellitus at Screening.
  • Known immunodeficiency.
  • History of alcoholism or drug abuse.
  • Blood donation within 60 days prior to Screening.
  • Use of investigational products or devices within 30 days prior to Screening.
  • Use of therapeutic monoclonal antibodies within 90 days prior to Screening.
  • Use of certain medications (active vitamin D, phosphate treatments, antacids, acetazolamide, thiazide diuretics, systemic corticosteroids) within 14 days prior to Screening without a washout period.
  • Use of parathyroid hormone suppressing medications within 2 months prior to Screening.
  • Use of denosumab within 6 months prior to Screening.
  • Use of oral bisphosphonates within 2 years prior to Screening.
  • Use of teriparatide or abaloparatide within 2 months prior to Screening.
  • Plasma intact parathyroid hormone level 2.5 times or more the upper limit of normal at Screening.
  • Planned or recommended orthopedic surgery during the study.
  • Traumatic fracture or orthopedic surgery within 6 months prior to Screening.
  • Participants who are lactating.
  • Active and symptomatic COVID-19 infection at Day -1.
  • Any condition that may increase risk of poor compliance or interfere with safety or study results as judged by the investigator.

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 9 locations

1

University of California - San Francisco

San Francisco, California, United States, 94158

Actively Recruiting

2

Yale Center for XLH/ Yale University School of Medicine

New Haven, Connecticut, United States, 06510

Actively Recruiting

3

Indiana University School of Medicine University Hospital

Indianapolis, Indiana, United States, 46202

Actively Recruiting

4

Mayo Clinic

Rochester, Minnesota, United States, 55905

Not Yet Recruiting

5

Vanderbilt University Medical Center

Nashville, Tennessee, United States, 37232

Actively Recruiting

6

Hoptial Bictre

Le Kremlin-Bicêtre, Paris, France, 94275

Actively Recruiting

7

Institute of Osteology and Biomechanics (IOBM)

Hamburg, Germany, 22529

Actively Recruiting

8

Universitaetsklinikum Wurzburg

Würzburg, Germany, 97074

Actively Recruiting

9

Hospital Universitario La Paz

Madrid, Spain, 28046

Actively Recruiting

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Research Team

K

Kyowa Kirin

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NON_RANDOMIZED

Model

SEQUENTIAL

Primary Purpose

TREATMENT

Number of Arms

5

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