Actively Recruiting

Phase Not Applicable
Age: 0 - 18Years
All Genders
Healthy Volunteers
NCT06233526

Individualized Treatment of Pediatric R/R AML Based on Transcriptomic Profile and in Vitro Drug Sensitivity Test

Led by The Children's Hospital of Zhejiang University School of Medicine · Updated on 2024-07-03

60

Participants Needed

1

Research Sites

104 weeks

Total Duration

On this page

Sponsors

T

The Children's Hospital of Zhejiang University School of Medicine

Lead Sponsor

C

College of Pharmaceutical Science at Zhejiang University

Collaborating Sponsor

AI-Summary

What this Trial Is About

Acute myeloid leukemia (AML) accounts for about 15% to 20% of childhood leukemia, but the death rate accounts for about 50%. About 20-30% of children with AML did not achieve complete response (CR) after 2 induction treatments, and about 30% of children with CR had relapse within 3 years (including recurrence after hematopoietic stem cell transplantation).Relapsed/refractory (R/R) AML is a major cause of treatment failure and refractory survival. Reinduction chemotherapy for R/R-AML to obtain CR again, followed by hematopoietic stem cell transplantation, is the current treatment. At present, there is no recognized reinduction protocol, and the reinduction remission rate of R/R-AML varies greatly among different treatment regimens, ranging from 23 to 81%. Current guidelines recommend a new combination chemotherapy regimen consisting of new drugs without cross-resistance. This method selects sensitive chemotherapeutic drugs, and then forms a new combination chemotherapy regimen according to the characteristics of drugs, which is the choice of R/R-AML reinduction therapy.This study intends to conduct a clinical study on the individualized treatment of R/R AML patients through in vitro drug sensitivity test combined with patient transcriptomic characteristics.

CONDITIONS

Official Title

Individualized Treatment of Pediatric R/R AML Based on Transcriptomic Profile and in Vitro Drug Sensitivity Test

Who Can Participate

Age: 0 - 18Years
All Genders
Healthy Volunteers

Eligibility Criteria

Eligible

You may qualify if you...

  • Refractory or recurrent acute myeloid leukemia (AML) not achieving complete remission after second-line reinduction therapy
  • Patient younger than 18 years old
  • Good organ function and able to tolerate chemotherapy
  • Physical strength score of 0-3 based on WHO standard
  • Understanding of research procedures and voluntary signed informed consent
Not Eligible

You will not qualify if you...

  • Acute promyelocytic leukemia, chronic myelogenous leukemia, acute mixed cell leukemia, or known central nervous system leukemia
  • AML associated with congenital syndromes such as Down syndrome, Fanconi anemia, Bloom syndrome, Cole's syndrome, or congenital aplastic anemia
  • Immunodeficiency or positive for human immunodeficiency virus (HIV)
  • Significant cardiac or renal dysfunction with left ventricular ejection fraction below 50%
  • Active systemic infection
  • Any medical history or condition that impairs safe study completion as judged by investigator
  • Medically unfit to receive investigational drug or for any other reason as judged by investigator
  • Known or suspected allergy to study drugs or any drugs administered in connection with the study

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Trial Site Locations

Total: 1 location

1

Children's Hospital of Zhejiang University School of Medicine

Hangzhou, Zhejiang, China, 310000

Actively Recruiting

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Research Team

X

Xiaojun Xu, MD

CONTACT

M

Meidan Ying, PhD

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NA

Model

SINGLE_GROUP

Primary Purpose

TREATMENT

Number of Arms

1

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