Actively Recruiting

Phase 1
Age: 18Years +
All Genders
ID04294043

A Phase 1b Multi-center Study of Intravenous Gallium Nitrate in Adults With Cystic Fibrosis Colonized With Nontuberculous Mycobacteria

Led by Chris Goss · Updated on 2025-10-01

40

Participants Needed

10

Research Sites

N/A

Total Duration

On this page

Sponsors

C

Chris Goss

Lead Sponsor

C

Cystic Fibrosis Foundation

Collaborating Sponsor

AI-Summary

What this Trial Is About

This research aims to assess the safety and tolerability of two 5-day cycles of intravenous (IV) gallium in adults with cystic fibrosis (CF) who are infected with nontuberculous mycobacteria (NTM). The study focuses on patients colonized with Mycobacterium avium complex and/or Mycobacterium abscessus complex, including those who are treatment-naefve and those with treatment-refractory infections. This phase 1b, multicenter, open-label study is funded by the FDA Office of Orphan Products Development (OOPD).

CONDITIONS

Brief Title

IV Gallium Study for Patients With Cystic Fibrosis Who Have NTM (ABATE Study)

Who Can Participate

Age: 18Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Written informed consent obtained from participant or legal representative
  • Willing and able to follow study schedule and protocol requirements
  • Adults aged 18 years or older
  • Confirmed diagnosis of cystic fibrosis with clinical features consistent with CF
  • Persistently positive NTM culture results for M. avium complex, M. abscessus complex, or both
  • For treatment-na�efve cohort: no prior treatment for current NTM species or previous treatment cleared NTM and completed over 2 years ago
  • For treatment-refractory cohort: history of treatment with guideline-based antibiotics for over 12 months without clearance or currently receiving such treatment
  • Forced expiratory volume in 1 second (FEV1) at least 25% of predicted value at screening
  • Able to expectorate sputum
  • Clinically stable with no significant health changes within 7 days before Day 1
  • Enrolled in the Cystic Fibrosis Foundation Patient Registry
  • Willing to discontinue chronic azithromycin use during study (na�efve cohort)
  • Willing to continue guideline-based antibiotic therapy concurrent with IV gallium if currently on treatment (refractory cohort)
Not Eligible

You will not qualify if you...

  • Abnormal lab values at screening including low hemoglobin, low platelets, low neutrophil count, elevated liver enzymes or bilirubin, high serum creatinine, or low ionized calcium
  • History of solid organ or blood cell transplantation
  • Use of bisphosphonates within 7 days before Day 1
  • Known allergy or sensitivity to gallium
  • Participation in other investigational drug studies within 28 days before Day 1
  • Signs of active NTM disease or clinical worsening despite treatment
  • Currently undergoing or planning treatment for NTM disease within 3 months (na�efve cohort)
  • Current diagnosis of osteoporosis
  • For people who can become pregnant: positive pregnancy test, breastfeeding, or unwillingness to use effective contraception during study
  • For people who can father a child: unwillingness to use adequate contraception during study
  • Other conditions that would make participation unsafe or affect study results as judged by investigator
  • Recent new initiation of chronic CF therapies within 28 days before study start
  • Use of azithromycin within 14 days before screening (na�efve cohort)
  • Hospitalization within 7 days before Day 1 (refractory cohort)

AI-Screening

AI-Powered Screening

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Your Study Journey

Screening

Duration - 2 to 4 weeks

Participants are screened for eligibility to participate in the trial.

1 visit (in-person)

Treatment

Duration - Approximately 2 cycles of 5 days each

Participants receive two cycles of intravenous gallium nitrate infusions, each cycle lasting 5 days. The infusions are administered continuously over 24 hours using an ambulatory infusion pump.

2 infusion cycles, each lasting 5 days

Follow-up

Duration - Up to 57 days after baseline

Participants are monitored for safety and treatment effects following completion of the gallium infusions.

Visits for safety and efficacy assessments up to Day 57 and Day 111

Trial Site Locations

Total: 10 locations

1

University of Alabama at Birmingham

Birmingham, Alabama, United States, 35294

Actively Recruiting

2

National Jewish Health

Denver, Colorado, United States, 80206

Actively Recruiting

3

Johns Hopkins University

Baltimore, Maryland, United States, 21205

Actively Recruiting

4

The Minnesota Cystic Fibrosis Center

Minneapolis, Minnesota, United States, 55455

Actively Recruiting

5

Nationwide Children's Hospital

Columbus, Ohio, United States, 43205

Actively Recruiting

6

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, United States, 15224

Actively Recruiting

7

Medical University of South Carolina

Charleston, South Carolina, United States, 29425

Actively Recruiting

8

University of Texas Southwestern

Dallas, Texas, United States, 75390

Actively Recruiting

9

University of Vermont Medical Center

Burlington, Vermont, United States, 05401

Actively Recruiting

10

University of Washington Medical Center

Seattle, Washington, United States, 98195

Actively Recruiting

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Research Team

N

Natallia Cameron

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NA

Model

SINGLE_GROUP

Primary Purpose

TREATMENT

Number of Arms

1

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