Actively Recruiting

Phase 2
Age: 18Years +
All Genders
NCT04153422

IVIG in the Treatment of Autoimmune Small Fiber Neuropathy With TS-HDS, FGFR-3, or Plexin D1 Antibodies

Led by Endeavor Health · Updated on 2026-01-09

20

Participants Needed

1

Research Sites

219 weeks

Total Duration

On this page

Sponsors

E

Endeavor Health

Lead Sponsor

O

Octapharma USA, Inc.

Collaborating Sponsor

AI-Summary

What this Trial Is About

This study will enroll patients with small fiber neuropathy (SFN). The study will look at an intravenous immunoglobulin (IVIG) called Panzyga. Panzyga is approved by the FDA as a therapy for Primary humoral immunodeficiency (PI) in patients 2 years of age and older; Chronic immune thrombocytopenia (ITP) in adults and Chronic inflammatory demyelinating polyneuropathy (CIDP) in adults. It has not been approved by the FDA for use in SFN. There is mounting evidence that Intravenous Immunoglobulin (IVIG) can cause pain reduction and improve objective nerve fiber densities on skin biopsies in great numbers in SFN patients. The primary outcome is quantified improvement in intraepidermal nerve fiber density (IENFD) on repeat skin punch biopsy after 6 months of IVIG treatment.

CONDITIONS

Official Title

IVIG in the Treatment of Autoimmune Small Fiber Neuropathy With TS-HDS, FGFR-3, or Plexin D1 Antibodies

Who Can Participate

Age: 18Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Patients aged 18 years or older
  • Clinical and biopsy evidence of pure small fiber neuropathy confirmed within 12 months
  • Elevated or abnormal autoantibodies to TS-HDS-IgM, FGFR3-IgG, or Plexin-D1 measured within 12 months
  • Baseline pain score of 4 or higher on a visual analogue scale
  • Baseline Utah Early Neuropathy Scale score of 4 or higher
  • Small Fiber Neuropathy Screening List score of 11 or greater
  • Non-pregnant, non-lactating females; females of reproductive potential must use two forms of contraception or abstain from heterosexual sex during treatment
Not Eligible

You will not qualify if you...

  • Any other known cause for small fiber neuropathy besides elevated TS-HDS-IgM, FGFR3-IgG, or Plexin-D1 autoantibodies
  • Severe musculoskeletal conditions that prevent proper assessment
  • Evidence of large fiber polyneuropathy confirmed by electromyography or nerve conduction study
  • Severe heart, kidney, liver disease, or HIV infection
  • History of deep vein thrombosis within the past year or pulmonary embolism ever
  • Known significant IgA deficiency with antibodies to IgA
  • History of severe allergic reaction to immunoglobulin or blood products
  • Known blood hyperviscosity or hypercoagulable states
  • Use of IgG products within six months before enrollment
  • History of drug or alcohol abuse within the past five years
  • Unable or unwilling to comply with study protocol or understand it

AI-Screening

AI-Powered Screening

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Trial Site Locations

Total: 1 location

1

Endeavor Health

Glenview, Illinois, United States, 60026

Actively Recruiting

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Research Team

A

Anna Pham

CONTACT

M

May Aunaetitrakul

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

DOUBLE

Allocation

RANDOMIZED

Model

PARALLEL

Primary Purpose

TREATMENT

Number of Arms

2

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