Actively Recruiting

Phase 3
Age: 18Years +
All Genders
NCT07075016

Ivosidenib and Azacitidine With or Without Venetoclax in Adult Patients With Newly Diagnosed IDH1-Mutated AML or MDS/AML Considered Ineligible for Intensive Chemotherapy

Led by Stichting Hemato-Oncologie voor Volwassenen Nederland · Updated on 2025-08-19

227

Participants Needed

119

Research Sites

186 weeks

Total Duration

On this page

Sponsors

S

Stichting Hemato-Oncologie voor Volwassenen Nederland

Lead Sponsor

G

German-Austrian Acute Myeloid Leukemia Study Group

Collaborating Sponsor

AI-Summary

What this Trial Is About

The standard treatment for patients with acute myeloid leukemia (AML) with an abnormality in the IDH1 gene, who are not eligible for intensive chemotherapy, is a combination of ivosidenib and azacitidine. In this study it is investigated whether adding venetoclax to the standard treatment can improve the outcome of the treatment of this specific form of AML. The safety is investigated and how well it works. In order to properly assess the value of venetoclax, the effect of venetoclax is compared with the effect of a placebo. A placebo is a product without an active ingredient, a 'fake medicinal product'.

CONDITIONS

Official Title

Ivosidenib and Azacitidine With or Without Venetoclax in Adult Patients With Newly Diagnosed IDH1-Mutated AML or MDS/AML Considered Ineligible for Intensive Chemotherapy

Who Can Participate

Age: 18Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Newly diagnosed IDH1-mutated AML or IDH1-mutated MDS/AML according to 2022 classification
  • Central confirmation of IDH1 mutation from a designated genetic laboratory
  • Age 18 years or older, no upper age limit
  • Ineligible for intensive chemotherapy due to age (≥75 years) or specific health conditions including ECOG status, heart issues, lung function, kidney function, liver function, or other comorbidities
  • Projected life expectancy of at least 12 weeks
  • White blood cell count less than 25 x 10^9/L (hydroxyurea allowed to reduce counts)
  • Adequate kidney function (serum creatinine ≤2.0 x ULN or creatinine clearance >30 mL/min)
  • Adequate liver function with specific bilirubin and enzyme limits unless due to Gilbert's disease or leukemic involvement
  • Female patients must be either non-childbearing or agree to pregnancy prevention measures during and for 6 months after treatment
  • Male patients must use contraception and agree to avoid fathering a child during and for 6 months after treatment
  • Able and willing to provide informed consent
  • Institutional review board/ethics committee approved consent obtained before study procedures
Not Eligible

You will not qualify if you...

  • Prior treatment for AML except hydroxyurea to control white blood cells
  • Acute promyelocytic leukemia with specific genetic translocations
  • AML with BCR-ABL1 or myeloid blast crisis of chronic myeloid leukemia
  • Significant active cardiac disease within 3 months before study including severe heart failure, recent heart attack, unstable angina, severe arrhythmias, or prolonged QT interval
  • Family history of sudden death or ventricular arrhythmia
  • Severe lung disorders
  • Stroke or brain bleeding within 6 months before randomization
  • Active or known central nervous system leukemia
  • Uncontrolled active infections such as hepatitis B, C, or HIV
  • Life-threatening leukemia complications like uncontrolled bleeding
  • Conditions limiting oral drug intake or absorption
  • Active second malignancy unless low risk or treated certain skin or cervical cancers
  • Live vaccine within 30 days before study or planned during study
  • Severe neurological or psychiatric disorders preventing informed consent
  • Contraindications to study drugs or participation in other anti-leukemic trials
  • Use of certain medications that cannot be safely changed
  • Pregnancy, breastfeeding, or plans to become pregnant during study
  • Previous ineligibility for this trial prevents re-entry

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 119 locations

1

AT-Feldkirch-IKHF

Feldkirch, Austria

Not Yet Recruiting

2

AT-Salzburg-SALK

Salzburg, Austria

Not Yet Recruiting

3

AT-Vienna-HANUSCH

Vienna, Austria

Not Yet Recruiting

4

BE-Antwerpen-ZAS

Antwerp, Belgium

Not Yet Recruiting

5

BE-Brussel-BORDET

Brussels, Belgium

Not Yet Recruiting

6

BE-Brussel-UZBRUSSEL

Brussels, Belgium

Not Yet Recruiting

7

BE-Bruxelles-STLUC

Brussels, Belgium

Not Yet Recruiting

8

BE-Gent-UZGENT

Ghent, Belgium

Not Yet Recruiting

9

BE-Leuven-UZLEUVEN

Leuven, Belgium

Not Yet Recruiting

10

BE-Liege-CHULIEGE

Liège, Belgium

Not Yet Recruiting

11

BE-Yvoir-MONTGODINNE

Yvoir, Belgium

Actively Recruiting

12

DK-Aalborg-AALBORGUH

Aalborg, Denmark

Not Yet Recruiting

13

DK-Aarhus N-AUH

Aarhus N, Denmark

Not Yet Recruiting

14

DK-Copenhagen-RIGSHOSPITALET

Copenhagen, Denmark

Not Yet Recruiting

15

DK-Odense-OUH

Odense, Denmark

Not Yet Recruiting

16

DK-Roskilde-ROSKILDE

Roskilde, Denmark

Not Yet Recruiting

17

EE-Tallinn-REGIONAALHAIGLA

Tallinn, Estonia

Not Yet Recruiting

18

EE-Tartu-TARTU

Tartu, Estonia

Not Yet Recruiting

19

FI-Helsinki-HUS

Helsinki, Finland

Not Yet Recruiting

20

FI-Tampere-TAYS

Tampere, Finland

Not Yet Recruiting

21

FR-Angers-CHUANGERS

Angers, France

Not Yet Recruiting

22

FR-Pessac Cedex-CHUBORDEAUX

Bordeaux, France

Not Yet Recruiting

23

FR-Caen-CHUCAEN

Caen, France

Not Yet Recruiting

24

FR-Créteil cedex-CHUMONDOR

Créteil, France

Not Yet Recruiting

25

FR-Grenoble cedex 9-CHUGRENOBLE

Grenoble, France

Not Yet Recruiting

26

FR-Lille-CHULILLE

Lille, France

Not Yet Recruiting

27

FR-Lyon Pierre Benite cedex-LYONSUD

Lyon, France

Not Yet Recruiting

28

FR-Montpellier-CHUSAINTELOIS

Montpellier, France

Not Yet Recruiting

29

FR-Nantes-CHUNANTES

Nantes, France

Not Yet Recruiting

30

FR-Nice-LARCHET

Nice, France

Not Yet Recruiting

31

FR-Rennes cedex 9-CHURENNES

Rennes, France

Not Yet Recruiting

32

FR-Rouen cedex-BECQUEREL

Rouen, France

Not Yet Recruiting

33

FR-Saint-Priest-en-Jarez-STETIENNE

Saint-Etienne, France

Not Yet Recruiting

34

FR-Le Chesnay cedex-CHVERSAILLES

Versailles, France

Not Yet Recruiting

35

DE-Berlin-CAMPUSBENFRANKLIN

Berlin, Germany

Not Yet Recruiting

36

DE-Berlin-CAMPUSVIRCHOW

Berlin, Germany

Not Yet Recruiting

37

DE-Berlin-VIVANTESNEUKOLLN

Berlin, Germany

Not Yet Recruiting

38

DE-Bochum-RUB

Bochum, Germany

Not Yet Recruiting

39

DE-Bonn-UNIBONN

Bonn, Germany

Not Yet Recruiting

40

DE-Braunschweig-KLINIKUMBRAUNSCHWEIG

Braunschweig, Germany

Not Yet Recruiting

41

DE-Bremen-KBM

Bremen, Germany

Not Yet Recruiting

42

DE-Darmstadt-KLINIKUMDARMSTADT

Darmstadt, Germany

Not Yet Recruiting

43

DE-Flensburg-MALTESER

Flensburg, Germany

Not Yet Recruiting

44

DE-Freiburg-UNIKLINIKFREIBURG

Freiburg im Breisgau, Germany

Not Yet Recruiting

45

DE-Greifswald-UNIGREIFSWALD

Greifswald, Germany

Not Yet Recruiting

46

DE-Halle-UMH

Halle, Germany

Not Yet Recruiting

47

DE-Hamburg-ASKLEPIOSSTGEORG

Hamburg, Germany

Not Yet Recruiting

48

DE-Hamburg-UKE

Hamburg, Germany

Not Yet Recruiting

49

DE-Hannover-MHHANNOVER

Hanover, Germany

Not Yet Recruiting

50

DE-Hannover-SILOAHKRH

Hanover, Germany

Not Yet Recruiting

51

DE-Heilbronn-SLK

Heilbronn, Germany

Not Yet Recruiting

52

DE-Karlsruhe-KLINIKUMKARLSRUHE

Karlsruhe, Germany

Not Yet Recruiting

53

DE-Mainz-UNIMEDIZINMAINZ

Mainz, Germany

Not Yet Recruiting

54

DE-Minden-MUEHLENKREISKLINKEN

Minden, Germany

Not Yet Recruiting

55

DE-München-IRZTUM

München, Germany

Not Yet Recruiting

56

DE-Oldenburg-KLINIKUMOLDENBURG

Oldenburg, Germany

Not Yet Recruiting

57

DE-Regensburg-UKR

Regensburg, Germany

Not Yet Recruiting

58

DE-Stuttgart-KLINIKUMSTUTTGART

Stuttgart, Germany

Not Yet Recruiting

59

DE-Tübingen-MEDUNITUEBINGEN

Tübingen, Germany

Not Yet Recruiting

60

DE-Ulm-UNIKLINKULM

Ulm, Germany

Not Yet Recruiting

61

IE-Cork-CUH

Cork, Ireland

Not Yet Recruiting

62

IE-Dublin 7-MATER

Dublin, Ireland

Not Yet Recruiting

63

IE-Dublin 8-ST JAMES

Dublin, Ireland

Not Yet Recruiting

64

IE-Galway-UHGALWAY

Galway, Ireland

Not Yet Recruiting

65

IT-Bologna-MALPHIGI

Bologna, Italy

Not Yet Recruiting

66

IT-Milano-NIGUARDA

Milan, Italy

Not Yet Recruiting

67

IT-Roma-SAPIENZA

Roma, Italy

Not Yet Recruiting

68

IT-Roma-TORVERGATA

Roma, Italy

Not Yet Recruiting

69

IT-Torino-CITTADELLASALUTE

Torino, Italy

Not Yet Recruiting

70

LT-Vilnius-SANTA

Vilnius, Lithuania

Not Yet Recruiting

71

NL-Den Bosch-JBZ

's-Hertogenbosch, Netherlands

Not Yet Recruiting

72

NL-Amsterdam-VUMC

Amsterdam, Netherlands

Not Yet Recruiting

73

NL-Arnhem-RIJNSTATE

Arnhem, Netherlands

Not Yet Recruiting

74

NL-Breda-AMPHIA

Breda, Netherlands

Not Yet Recruiting

75

NL-Dordrecht-ASZ

Dordrecht, Netherlands

Not Yet Recruiting

76

NL-Eindhoven-CATHARINA

Eindhoven, Netherlands

Not Yet Recruiting

77

NL-Enschede-MST

Enschede, Netherlands

Not Yet Recruiting

78

NL-Sittard-Geleen-ZUYDERLAND

Geleen, Netherlands

Not Yet Recruiting

79

NL-Groningen-UMCG

Groningen, Netherlands

Actively Recruiting

80

NL-Nijmegen-RADBOUDUMC

Nijmegen, Netherlands

Not Yet Recruiting

81

NL-Rotterdam-ERASMUSMC

Rotterdam, Netherlands

Not Yet Recruiting

82

NL-DenHaag-HAGA

The Hague, Netherlands

Not Yet Recruiting

83

NL-Utrecht-UMCU

Utrecht, Netherlands

Not Yet Recruiting

84

NL-Zwolle-ISALA

Zwolle, Netherlands

Not Yet Recruiting

85

NO-Bergen-HELSEBERGEN

Bergen, Norway

Not Yet Recruiting

86

NO-Oslo-OSLOUH

Oslo, Norway

Not Yet Recruiting

87

NO-Tromsø-NORTHNOORWEGEN

Tromsø, Norway

Not Yet Recruiting

88

NO-Trondheim-STOLAV

Trondheim, Norway

Not Yet Recruiting

89

ES-Barcelona-CLINICUB

Barcelona, Spain

Not Yet Recruiting

90

ES-Barcelona-GERMANTRIALS

Barcelona, Spain

Not Yet Recruiting

91

ES-Barcelona-SANTPAU

Barcelona, Spain

Not Yet Recruiting

92

ES-Girona-ICSTRUETA

Girona, Spain

Not Yet Recruiting

93

ES-Valencia-MALVARROSA

Valencia, Spain

Not Yet Recruiting

94

SE-Goteborg-SAHLGRENSKA

Gothenburg, Sweden

Not Yet Recruiting

95

SE-Lund-SUH

Lund, Sweden

Not Yet Recruiting

96

SE-Stockholm-KAROLINSKAHUDDINGE

Stockholm, Sweden

Not Yet Recruiting

97

SE-Uppsala-UPPSALAUH

Uppsala, Sweden

Not Yet Recruiting

98

CH-Basel-USB

Basel, Switzerland

Not Yet Recruiting

99

CH-Bellinzona-IOSI

Bellinzona, Switzerland

Not Yet Recruiting

100

CH-Bern-INSEL

Bern, Switzerland

Not Yet Recruiting

101

CH-Zurich-USZ

Zurich, Switzerland

Not Yet Recruiting

102

UK-Birmingham-QE

Birmingham, United Kingdom

Not Yet Recruiting

103

UK-Blackpool-BLACKPOOLVICTORIA

Blackpool, United Kingdom

Not Yet Recruiting

104

UK-Bristol-BRISTOLCENTRE

Bristol, United Kingdom

Not Yet Recruiting

105

UK-Cardiff-UHW

Cardiff, United Kingdom

Not Yet Recruiting

106

UK-Glasgow-BEATSON

Glasgow, United Kingdom

Not Yet Recruiting

107

UK-Leeds-STJAMESUH

Leeds, United Kingdom

Not Yet Recruiting

108

UK-Leicester-LEICESTERRI

Leicester, United Kingdom

Not Yet Recruiting

109

UK-London-KCH

London, United Kingdom

Not Yet Recruiting

110

UK-London-ROYALMARSDEN

London, United Kingdom

Not Yet Recruiting

111

UK-London-UNICOLLEGEHOSP

London, United Kingdom

Not Yet Recruiting

112

UK-Manchester-CHRISTIE

Manchester, United Kingdom

Not Yet Recruiting

113

UK-Manchester-ROYALINFIRMARY

Manchester, United Kingdom

Not Yet Recruiting

114

UK-Newcastle on Tyne-FREEMAN

Newcastle upon Tyne, United Kingdom

Not Yet Recruiting

115

UK-Nottingham-NOTTINGHAMCH

Nottingham, United Kingdom

Not Yet Recruiting

116

UK-Oxford-CHURCHILL

Oxford, United Kingdom

Not Yet Recruiting

117

UK-Portsmouth-QUEENALEXANDRA

Portsmouth, United Kingdom

Not Yet Recruiting

118

UK-Southampton-SOUTHAMPTONGH

Southampton, United Kingdom

Not Yet Recruiting

119

UK-Wolverhampton-NEWCROSSH

Wolverhampton, United Kingdom

Not Yet Recruiting

Loading map...

How is the study designed?

Study Type

INTERVENTIONAL

Masking

TRIPLE

Allocation

RANDOMIZED

Model

SINGLE_GROUP

Primary Purpose

TREATMENT

Number of Arms

2

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