Actively Recruiting

Phase 1
Phase 2
Age: 18Years +
All Genders
NCT04752722

LEGEND Study: EG-70 in NMIBC Patients BCG-Unresponsive and High-Risk NMIBC Incompletely Treated With BCG or BCG-Naïve

Led by enGene, Inc. · Updated on 2026-04-30

350

Participants Needed

101

Research Sites

397 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

This study will evaluate the safety and efficacy of intravesical administration of EG-70 in the bladder and its effect on bladder tumors in patients with NMIBC. This study study consists of two phases; a Phase 1 dose-escalation to establish safety and recommended the phase 2 dose, followed by a Phase 2 study to establish how effective the treatment is. The Study will include patients with NMIBC with Cis for whom BCG therapy is unresponsive and patients with NMIBC with Cis who are BCG-naïve or inadequately treated.

CONDITIONS

Official Title

LEGEND Study: EG-70 in NMIBC Patients BCG-Unresponsive and High-Risk NMIBC Incompletely Treated With BCG or BCG-Naïve

Who Can Participate

Age: 18Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • BCG-unresponsive NMIBC patients with carcinoma in situ (CIS) who are ineligible for or have chosen not to undergo cystectomy, with disease present within 12 months after adequate BCG treatment
  • BCG-nafve or incompletely treated high-risk NMIBC patients with CIS or BCG-unresponsive high-grade Ta/T1 papillary disease without CIS (Phase 2 only)
  • Patients who failed prior checkpoint inhibitor therapy and are at least 30 days (Phase 1) or 3 months (Phase 2) post-treatment
  • Male or non-pregnant, non-lactating female aged 18 years or older
  • Women of childbearing potential must have a negative pregnancy test at screening
  • Females of childbearing potential must agree to use highly effective birth control; males must use condoms during treatment and for 3 months after
  • Patients with T1 lesions may be eligible after repeat TURBT if pathology shows non-invasive or no disease (Phase 2)
  • Eastern Cooperative Oncology Group performance status of 0, 1, or 2
  • Adequate blood counts: neutrophils >1,500/mm3, hemoglobin >9.0 g/dL, platelets >100,000/mm3
  • Liver function: total bilirubin ≤1.5 times upper limit of normal (ULN); AST, ALT, alkaline phosphatase ≤2.5 times ULN
  • Adequate kidney function with creatinine clearance >30 mL/min
  • Prothrombin time and partial thromboplastin time ≤1.25 times ULN or within therapeutic range if on anticoagulants
  • Satisfactory bladder function able to retain study drug for 60 minutes
Not Eligible

You will not qualify if you...

  • Active cancers progressing or requiring treatment changes in the last 24 months (exceptions possible)
  • Receiving chemotherapy currently
  • History of partial cystectomy
  • Treatment with last therapeutic agent within 30 days before screening biopsy
  • Use of systemic immunosuppressive medications including high-dose corticosteroids
  • History of severe asthma or other respiratory diseases
  • Unresolved vesicoureteral reflux or indwelling urinary stent
  • Unresolved hydronephrosis due to ureteral obstruction
  • Participation in other investigational drug studies within 30 days prior to screening or prior investigational gene or immunotherapy for NMIBC
  • Pelvic or prostate radiation within the last 12 months
  • History of interstitial lung disease or pneumonitis in patients previously treated with PD-1 or PD-L1 inhibitors
  • Evidence of metastatic disease
  • History of difficult catheterization preventing EG-70 administration
  • Active interstitial cystitis on cystoscopy or biopsy
  • Active uncontrolled infections requiring systemic therapy
  • Known HIV, Hepatitis B, or Hepatitis C infection
  • Significant cardiovascular risk, such as recent coronary stenting or myocardial infarction
  • Allergic reaction to any components of the study drug

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 101 locations

1

The University of Alabama at Birmingham Clinical Research Unit (CRU)

Birmingham, Alabama, United States, 35249

Actively Recruiting

2

Mayo Clinic

Scottsdale, Arizona, United States, 85259

Actively Recruiting

3

Urological Associates of South Arizona

Tucson, Arizona, United States, 85715

Completed

4

Arkansas Urology

Little Rock, Arkansas, United States, 72211

Actively Recruiting

5

University of California - Irvine Medical Center

Irvine, California, United States, 92697

Actively Recruiting

6

UC San Diego Moores Cancer Center

La Jolla, California, United States, 92037

Actively Recruiting

7

USC/Norris Comprehensive Cancer Center

Los Angeles, California, United States, 90033

Actively Recruiting

8

Tower Urology

Los Angeles, California, United States, 90048

Actively Recruiting

9

Om Research

San Diego, California, United States, 92123

Actively Recruiting

10

Colorado Clinical Research

Lakewood, Colorado, United States, 80228

Actively Recruiting

11

The George Washington Medical Faculty Associates

Washington D.C., District of Columbia, United States, 20037

Actively Recruiting

12

University of Florida

Jacksonville, Florida, United States, 32209

Actively Recruiting

13

Sylvester Comprehensive Cancer Center / University of Miami Hospital and Clinics

Miami, Florida, United States, 33136

Actively Recruiting

14

Emory University

Atlanta, Georgia, United States, 30322

Actively Recruiting

15

Rush University Medical Center

Chicago, Illinois, United States, 60607

Actively Recruiting

16

Urology of Indiana

Greenwood, Indiana, United States, 46143

Actively Recruiting

17

University of Kansas Medical Center

Kansas City, Kansas, United States, 66160

Actively Recruiting

18

John Hopkins Hospital

Baltimore, Maryland, United States, 21287

Actively Recruiting

19

Chesapeake Urology Research Associates

Hanover, Maryland, United States, 21076

Actively Recruiting

20

Brigham and Women's Hospital

Boston, Massachusetts, United States, 45227

Actively Recruiting

21

Henry Ford Health System

Detroit, Michigan, United States, 48202

Actively Recruiting

22

Corewell Health Medical Group and Spectrum Health Hospitals

Grand Rapids, Michigan, United States, 49503

Actively Recruiting

23

University of Minnesota

Minneapolis, Minnesota, United States, 55455

Actively Recruiting

24

Mayo Clinic

Rochester, Minnesota, United States, 55905

Actively Recruiting

25

Rutgers Cancer Institute of New Jersey

New Brunswick, New Jersey, United States, 08901

Actively Recruiting

26

New Jersey Urology, LLC

Voorhees Township, New Jersey, United States, 08043

Actively Recruiting

27

Albany Medical College

Albany, New York, United States, 12208

Actively Recruiting

28

Mount Sinai Medical Center

New Haven, New York, United States, 10029

Actively Recruiting

29

Laura & Isaac Perlmutter Cancer Center at NYU Langone Health

New York, New York, United States, 10016

Completed

30

Associated Medical Professionals of NY,

Syracuse, New York, United States, 13210

Actively Recruiting

31

UNC Chapel Hill Hospital

Chapel Hill, North Carolina, United States, 27514

Actively Recruiting

32

Duke Health - Duke Cancer Center

Durham, North Carolina, United States, 27710

Actively Recruiting

33

Associated Urologists of North Carolina

Raleigh, North Carolina, United States, 27612

Actively Recruiting

34

University of Cincinnati Medical Center

Cincinnati, Ohio, United States, 45219

Actively Recruiting

35

Central Ohio Urology Group

Gahanna, Ohio, United States, 43230

Actively Recruiting

36

Clinical Research Solutions - Helios Clinical Research

Middleburg Heights, Ohio, United States, 44130

Actively Recruiting

37

Oregon Health & Science University (OHSU)

Portland, Oregon, United States, 97239

Actively Recruiting

38

Thomas Jefferson University, Sidney Kimmel Cancer Center

Philadelphia, Pennsylvania, United States, 19107

Actively Recruiting

39

Carolina Urologic Research Center, LLC

Myrtle Beach, South Carolina, United States, 29572

Actively Recruiting

40

Urology Associates, P.C.

Nashville, Tennessee, United States, 37209

Actively Recruiting

41

Vanderbilt Univerity Medical Center

Nashville, Tennessee, United States, 37232

Actively Recruiting

42

Urology Austin

Austin, Texas, United States, 78745

Actively Recruiting

43

UT Southwestern Medical Center

Dallas, Texas, United States, 75390

Actively Recruiting

44

Houston Metro Urology

Houston, Texas, United States, 77027

Actively Recruiting

45

Houston Methodist Hospital - Department of Urology

Houston, Texas, United States, 77030

Actively Recruiting

46

University of Texas - MD Anderson Cancer Center

Houston, Texas, United States, 77030

Actively Recruiting

47

Huntsman Cancer Institute, University of Utah

Salt Lake City, Utah, United States, 84112

Actively Recruiting

48

University of Virginia Comprehensive Cancer Center

Charlottesville, Virginia, United States, 22903

Actively Recruiting

49

Froedtert Hospital / Medical College of Wisconsin

Milwaukee, Wisconsin, United States, 52336

Actively Recruiting

50

Sydney Adventist Hospital

Wahroonga, New South Wales, Australia, 2076

Actively Recruiting

51

Gold Coast University Hospital

Southport, Queensland, Australia, 4215

Actively Recruiting

52

Icon Cancer Center Windsor Gardens

Windsor Gardens, South Australia, Australia, 5087

Actively Recruiting

53

Prostate Cancer Centre

Calgary, Alberta, Canada, T2V1P9

Actively Recruiting

54

Vancouver Prostate Centre

Vancouver, British Columbia, Canada, V5Z1M9

Actively Recruiting

55

Nova Scotia Health Authority

Halifax, Nova Scotia, Canada, B3H2Y9

Actively Recruiting

56

University Health Network, Princess Margaret Cancer Centre

Toronto, Ontario, Canada, M5G 2M9

Actively Recruiting

57

McGill University Health Center - Glen site

Montreal, Quebec, Canada, H4A3J1

Actively Recruiting

58

CHUM Centre Hospitalier de l Universite de Montreal

Montreal, Quebec, Canada

Actively Recruiting

59

CHU d'Angers

Angers, France, 49933

Actively Recruiting

60

CHU Bordeaux Pellegrin

Bordeaux, France, 33076

Actively Recruiting

61

lnstitut Bergonie 229 Cour de l'Argonne

Bordeaux, France, 33076

Actively Recruiting

62

CHU de Lille

Lille, France, 59000

Actively Recruiting

63

Hospices Civils de Lyon

Lyon, France, 69002

Actively Recruiting

64

Hopital Bichat Claude-Bernard

Paris, France, 75018

Actively Recruiting

65

CHU de Rauen- Hopital Charles Nicolle

Rouen, France, 76031

Actively Recruiting

66

Klinik fur Urologie, Uro-Onkologie, spezielle urologische und Roboter-assistierte Chirurgie Universitatsklinikum Koln (AOR)

Cologne, Germany, 50937

Actively Recruiting

67

Urologicum Duisburg

Duisburg, Germany, 47169

Actively Recruiting

68

Universitaetsklinikum Erlangen

Erlangen, Germany, 91054

Actively Recruiting

69

Urologie Neandertal Mettmann

Mettmann, Germany, 40822

Actively Recruiting

70

Studienpraxis Urologie

Nürtingen, Germany, 72622

Actively Recruiting

71

Universitaetsklinikum Tubingen

Tübingen, Germany, 72076

Actively Recruiting

72

Clinic Unit of Urology, IRCCS Ospedale San Raffaele

Milan, MI, Italy, 20132

Actively Recruiting

73

Istituto Europeo di Oncologia

Milan, Italy, 20141

Actively Recruiting

74

Istituto Nazionale Tumori IRCCS Fondazione G. Pascale

Naples, Italy, 80131

Actively Recruiting

75

Fondazione Policlinico Universitario "A.Gemelli" IRCCS, Largo

Rome, Italy, 00168

Actively Recruiting

76

Azienda Ospedaliero-Universitaria Sant'Andrea

Rome, Italy, 00189

Actively Recruiting

77

UOC Urologia, IFO- lstituto Tumori "Regina Elena"

Rome, Italy, 53 00144

Actively Recruiting

78

Ospedelae Molinette San Giovanni Battista Di Torino

Torino, Italy, 10126

Actively Recruiting

79

Seoul National University Bundang Hospital

Seongnam, Gyunggi-do, South Korea, 13620

Actively Recruiting

80

Chonnam National University Hwasun Hospital

Hwasun, Jeollanam-do, South Korea, 58128

Actively Recruiting

81

Seoul National University Hospital

Seoul, South Korea, 03080

Actively Recruiting

82

Severance Hospital, Yonsei University Health System

Seoul, South Korea, 03722

Actively Recruiting

83

The Catholic University of Korea, Soul St. Mary's Hospital

Seoul, South Korea, 06591

Actively Recruiting

84

IOB - Hospital Quironsalud Barcelona

Barbera Del Valles, Spain, 5-7

Actively Recruiting

85

Fundacio Puigvert

Barcelona, Spain, 08025

Actively Recruiting

86

Hospital Clinic Barcelona

Barcelona, Spain, 08036

Actively Recruiting

87

Hospital Germans Trias i Pujol

Barcelona, Spain, 08916

Actively Recruiting

88

Hospital Universitari de Bellvitge

L'Hospitalet de Llobregat, Spain, 08907

Actively Recruiting

89

Hospital General Universitario Gregorio Maranon

Madrid, Spain, 28007

Actively Recruiting

90

Hospital Universitario 12 de Octubre

Madrid, Spain, 28041

Actively Recruiting

91

Hospital Universitario La Paz

Madrid, Spain, 28046

Actively Recruiting

92

Hospital Quironsalud Madrid (Next Oncology)

Madrid, Spain, 28223

Actively Recruiting

93

Hospital Universitario Infanta Sofia

Madrid, Spain, 28702

Actively Recruiting

94

Hospital General Universitario Morales Meseguer

Murcia, Spain, 30008

Actively Recruiting

95

Hospital Universitario Marqués de Valdecilla,

Santander, Spain, 39008

Actively Recruiting

96

Kaohsiung Medical University Chung-Ho Memorial Hospital

Kaohsiung City, Taiwan, 807

Actively Recruiting

97

China Medical University Hospital

Taichung, Taiwan, 40447

Actively Recruiting

98

Taichung Veterans General Hospital

Taichung, Taiwan, 40705

Actively Recruiting

99

Chi Mei Medical Center

Tainan, Taiwan, 71004

Actively Recruiting

100

National Taiwan University Hospital

Taipei, Taiwan, 100

Actively Recruiting

101

The Royal Marsden NHS Foundation Trust

London, United Kingdom, SW3 6JJ

Actively Recruiting

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Research Team

E

enGene clinical trials

CONTACT

C

Chris Tosone

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NON_RANDOMIZED

Model

SEQUENTIAL

Primary Purpose

TREATMENT

Number of Arms

2

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