Actively Recruiting
Long-Term Development of Muscular Dystrophy Outcome Assessments
Led by Virginia Commonwealth University · Updated on 2025-11-18
1000
Participants Needed
1
Research Sites
288 weeks
Total Duration
On this page
Sponsors
V
Virginia Commonwealth University
Lead Sponsor
M
Muscular Dystrophy Association
Collaborating Sponsor
AI-Summary
What this Trial Is About
This is a 24-month, observational study of up to 1000 participants with Limb Girdle Muscular Dystrophy (LGMD), Myotonic Dystrophy Type 2 (DM2), and late onset Pompe disease (LOPD).
CONDITIONS
Official Title
Long-Term Development of Muscular Dystrophy Outcome Assessments
Who Can Participate
Eligibility Criteria
You may qualify if you...
- Age between 6 and 50 years at enrollment
- Clinically affected with weakness consistent with proximal muscle weakness
- Genetic confirmation of LGMD, DM2, or LOPD
- Forced vital capacity (FVC) above 30% of predicted
You will not qualify if you...
- Any other illness that would interfere with safe testing or result interpretation as judged by the site investigator
- Participation in a clinical trial receiving an investigational product
AI-Screening
AI-Powered Screening
Complete this quick 3-step screening to check your eligibility
Trial Site Locations
Total: 1 location
1
Virginia Commonwealth University
Richmond, Virginia, United States, 23298
Actively Recruiting
Research Team
J
Jennifer Raymond
CONTACT
R
Ruby Langeslay
CONTACT
How is the study designed?
Study Type
OBSERVATIONAL
Masking
N/A
Allocation
N/A
Model
N/A
Primary Purpose
N/A
Number of Arms
1
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