Actively Recruiting
Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)
Led by iECURE, Inc. · Updated on 2025-02-03
13
Participants Needed
1
Research Sites
862 weeks
Total Duration
On this page
AI-Summary
What this Trial Is About
This LTFU is being conducted to assess long-term safety and durability of response in participants dosed with IP in a parent protocol, and to collect longitudinal natural history in enrolled but not dosed participants who also participated in a parent protocol.
CONDITIONS
Official Title
Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)
Who Can Participate
Eligibility Criteria
You may qualify if you...
- Enrolled in an iECURE parent protocol and have either completed or discontinued that protocol
- Participant parent(s)/legal authorized representative (LAR) is willing and able to adhere to the protocol requirements
- Consent was obtained by the participant's parent(s)/LAR (and participant assent, where applicable) before any study-related data collection
You will not qualify if you...
- Participants enrolled in an interventional drug or gene therapy clinical trial using an investigational product other than that provided in the parent protocol
AI-Screening
AI-Powered Screening
Complete this quick 3-step screening to check your eligibility
Trial Site Locations
Total: 1 location
1
Great Ormond Street Hospital
London, United Kingdom
Actively Recruiting
Research Team
G
George Diaz, M.D., Ph.D.
CONTACT
How is the study designed?
Study Type
OBSERVATIONAL
Masking
N/A
Allocation
N/A
Model
N/A
Primary Purpose
N/A
Number of Arms
2
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