Actively Recruiting

Phase 2
Age: 18Years - 70Years
All Genders
ID07219407

An Open-label, Long-term Study Evaluating RAP-219 in Adult Participants With Refractory Onset Seizures

Led by Rapport Therapeutics Inc. · Updated on 2026-01-23

30

Participants Needed

7

Research Sites

N/A

Total Duration

On this page

AI-Summary

What this Trial Is About

Researchers are evaluating RAP-219, an investigational drug, for adults with refractory focal epilepsy, a condition involving difficult-to-control focal seizures. This open-label, multi-center study aims to assess the long-term safety, tolerability, how the drug behaves in the body, and its antiseizure activity in adults who have not responded well to previous treatments. Participants will receive RAP-219 starting with one 0.125 mg capsule daily for 3 days, then one 0.25 mg tablet daily for 28 days, followed by one 0.75 mg tablet daily for the rest of the treatment period. The study is open-label, meaning all participants know they are receiving RAP-219, and the treatment period may last up to 112 weeks with ongoing monitoring. During the study, participants will be regularly assessed for treatment-related side effects and seizure frequency compared to their baseline before treatment. Researchers will monitor seizure-free days, longest seizure-free intervals, and other seizure-related measures using clinical assessments and RNS system data. Safety will be tracked through adverse event reporting up to 8 weeks after the last dose. The total participation duration can be up to about 2 years, with ongoing evaluations throughout.

CONDITIONS

Brief Title

A Long-term Study of the Safety and Effectiveness of RAP-219 in Adults With Focal Onset Seizures

Who Can Participate

Age: 18Years - 70Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Completed the treatment period of the related RAP-219 parent study with acceptable tolerability as assessed by the investigator
  • Diagnosed with refractory focal epilepsy
  • Stable Responsive Neurostimulation (RNS) system settings
  • History of compliance with RNS system data interrogation and upload
  • Generally good health aside from focal epilepsy, as determined by the investigator
  • Body mass index (BMI) between 18 and 45 kg/m^2
  • Willing and able to follow all aspects of the study protocol
Not Eligible

You will not qualify if you...

  • Known allergy or hypersensitivity to RAP-219
  • Any unstable or serious medical, neurological (other than epilepsy), psychological, or behavioral condition that increases risk or disqualifies participation, as assessed by the investigator
  • Pregnancy or breastfeeding, or unwillingness to use two effective birth control methods if of reproductive potential

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Your Study Journey

Screening

Duration - 2 to 4 weeks

Participants are screened for eligibility to participate in the trial.

1 visit (in-person)

Treatment

Duration - Up to 112 weeks

Participants receive RAP-219 capsules and tablets daily with increasing doses over the treatment period to evaluate safety and effectiveness for refractory focal seizures.

Regular visits throughout the treatment period

Follow-up

Duration - 8 weeks

Participants are monitored for safety and effectiveness for 8 weeks after the last dose of RAP-219.

Multiple visits during the follow-up period

Trial Site Locations

Total: 7 locations

1

Consultants in Epilepsy and Neurology, PLLC

Boise, Idaho, United States, 83702

Actively Recruiting

2

Mayo Clinic

Rochester, Minnesota, United States, 55905

Actively Recruiting

3

NYU Langone Comprehensive Epilepsy Center

New York, New York, United States, 10016

Actively Recruiting

4

Cleveland Clinic Foundation

Cleveland, Ohio, United States, 44195

Actively Recruiting

5

University of Pennsylvania - Department of Neurology

Philadelphia, Pennsylvania, United States, 19104

Actively Recruiting

6

Vanderbilt University Medical Center

Nashville, Tennessee, United States, 37232

Actively Recruiting

7

Baylor College of Medicine

Houston, Texas, United States, 770300

Actively Recruiting

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Research Team

D

Daniela Moreno

B

Beth Bowers

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NA

Model

SINGLE_GROUP

Primary Purpose

TREATMENT

Number of Arms

1

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