Actively Recruiting
Lysosomal Acid Lipase (LAL) Deficiency Registry
Led by Alexion Pharmaceuticals, Inc. · Updated on 2026-03-06
300
Participants Needed
104
Research Sites
848 weeks
Total Duration
On this page
AI-Summary
What this Trial Is About
This is an observational, multi-center, international disease registry designed to collect longitudinal data and create a knowledge base that will be utilized to improve the care and treatment of patients with LAL Deficiency. Participation in the Registry by both physicians and patients is voluntary.
CONDITIONS
Official Title
Lysosomal Acid Lipase (LAL) Deficiency Registry
Who Can Participate
Eligibility Criteria
You may qualify if you...
- Patients must have a confirmed diagnosis of LAL Deficiency.
- Informed Consent and Authorization must be obtained prior to enrollment where required by law or a waiver obtained by the ethics committee.
- Patients who have previously completed participation in an Alexion-sponsored sebelipase alfa clinical trial are eligible to enroll.
You will not qualify if you...
- Patients currently participating in an Alexion-sponsored clinical trial.
AI-Screening
AI-Powered Screening
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Trial Site Locations
Total: 104 locations
1
Clinical Trial Site
Phoenix, Arizona, United States, 85016
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2
Clinical Trial Site
Stanford, California, United States, 94305
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3
Clinical Trial Site
Miramar, Florida, United States, 33025
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4
Clinical Trial Site
Orlando, Florida, United States, 32806
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5
Clinical Trial Site
Atlanta, Georgia, United States, 30322
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6
Clinical Trial Site
Chicago, Illinois, United States, 60611
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7
Clinical Trial Site
Boston, Massachusetts, United States, 02115
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8
Clinical Trial Site
Detroit, Michigan, United States, 48236
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9
Clinical Trial Site
Minneapolis, Minnesota, United States, 55404
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10
Clinical Trial Site
Jackson, Mississippi, United States, 39216
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11
Clinical Trial Site
Hackensack, NJ, 7601, New Jersey, United States, 07601
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12
Clinical Trial Site
New York, New York, United States, 10016
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13
Clinical Trial Site
The Bronx, New York, United States, 10467
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14
Clinical Trial Site
Philadelphia, Pennsylvania, United States, 19104-6061
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15
Clinical Trial Site
Philadelphia, Pennsylvania, United States, 19104
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16
Clinical Trial Site
Philadelphia, Pennsylvania, United States, 19107
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17
Clinical Trial Site
Houston, Texas, United States, 77030
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18
Clinical Trial Site
Houston, Texas, United States, 77030
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19
Clinical Trial Site
Snyder, Texas, United States, 79549
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20
Clinical Trial Site
Tacoma, Washington, United States, 98405
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21
Clinical Trial Site
New Lambton Heights, New South Wales, Australia, 2305
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22
Clinical Trial Site
Ghent, East Flanders, Belgium, 9000
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23
Clinical Trial Site
Campinas, São Paulo, Brazil, 13083-878
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24
Clinical Trial Site
São Paulo, Brazil, 04020-041
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25
Clinical Trial Site
São Paulo, Brazil, 04543-011
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26
Clinical Trial Site
Sofia, Sofia-Grad, Bulgaria, 1612
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27
Clinical Trial Site
Edmonton, Alberta, Canada, T6G 2H7
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28
Clinical Trial Site
Halifax, Nova Scotia, Canada, B3H 1V8
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29
Clinical Trial Site
London, Ontario, Canada, NGA 5W9
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30
Clinical Trial Site
Québec, Canada, G1R 2J6
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31
Clinical Trial Site
Zagreb, Croatia, 10000
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32
Clinical Trial Site
Prague, Central Bohemia, Czechia, 128 00
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33
Clinical Trial Site
Olomouc, Czechia, 779 00
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34
Clinical Trial Site
Bron, Auvergne-Rhône-Alpes, France, 69500
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35
Clinical Trial Site
Clermont-Ferrand, Auvergne-Rhône-Alpes, France, 63003
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36
Clinical Trial Site
Clermont-Ferrand, Auvergne-Rhône-Alpes, France, 63100
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37
Clinical Trial Site
Grenoble, Auvergne-Rhône-Alpes, France, 38043
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38
Clinical Trial Site
La Rochelle, New Aquitaine, France, 17000
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39
Clinical Trial Site
Niort, New Aquitaine, France, 79021
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40
Clinical Trial Site
Caen, Normandy, France, 14033
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41
Clinical Trial Site
Nancy, Vandœuvre-lès-Nancy, France, 54500
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42
Clinical Trial Site
Dijon, France, 21000
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43
Clinical Trial Site
Nantes, France, 44093
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44
Clinical Trial Site
Paris, Île-de-France Region, France, 75743
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45
Clinical Trial Site
Munich, Bavaria, Germany, 81377
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46
Clinical Trial Site
Essen, North Rhine-Westphalia, Germany, 45122
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47
Clinical Trial Site
Mainz, Rhineland-Palatinate, Germany, 55131
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48
Clinical Trial Site
Berlin, Germany, 13353
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49
Clinical Trial Site
Athens, Attica, Greece, 115 27
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50
Clinical Trial Site
Ioannina, Epirus, Greece, 455 00
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51
Clinical Trial Site
Thessaloniki, Macedonia, Greece, 564 03
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52
Clinical Trial Site
Dublin, Leinster, Ireland, D01 XD99
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53
Clinical Trial Site
Petah Tikva, Central District, Israel, 49202
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54
Clinical Trial Site
Haifa, Israel, 3436212
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55
Clinical Trial Site
Jerusalem, Israel, 9103102
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56
Clinical Trial Site
Jerusalem, Israel, 91120
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57
Clinical Trial Site
Bari, Apulia, Italy, 70126
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58
Clinical Trial Site
Naples, Campania, Italy, 80131
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59
Clinical Trial Site
Udine, Friuli Venezia Giulia, Italy, 33100
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60
Clinical Trial Site
Genoa, Liguria, Italy, 16147
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61
Clinical Trial Site
Bergamo, Lombardy, Italy, 24127
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62
Clinical Trial Site
Milan, Lombardy, Italy, 20122
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63
Clinical Trial Site
Turin, Piedmont, Italy, 10126
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64
Clinical Trial Site
Florence, Tuscany, Italy, 50139
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65
Clinical Trial Site
Padova, Veneto, Italy, 35128
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66
Clinical Trial Site
Zapopan, Jalisco, Mexico, 45116
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67
Clinical Trial Site
Aguascalientes, Mexico, 20230
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68
Clinical Trial Site
Mexico City, Mexico, 06720
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69
Clinical Trial Site
Amsterdam, North Holland, Netherlands, 1105
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70
Clinical Trial Site
Amsterdam, North Holland, Netherlands, 1105
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71
Clinical Trial Site
Guimarães, Braga District, Portugal, 4835
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72
Clinical Trial Site
Lisbon, Portugal, 1649
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73
Clinical Trial Site
Petersburg, Leningradskaya Oblast', Russia, 194100
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74
Clinical Trial Site
Moscow, Moscow Oblast, Russia, 115446
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75
Clinical Trial Site
Moscow, Moscow Oblast, Russia, 119049
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76
Clinical Trial Site
Moscow, Moscow Oblast, Russia, 119192
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77
Clinical Trial Site
Moscow, Moscow Oblast, Russia, 119296
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78
Clinical Trial Site
Nizhny Novgorod, Nizhny Novgorod Oblast, Russia, 603950
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79
Clinical Trial Site
Riyadh, Saudi Arabia, 11211
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80
Clinical Trial Site
Riyadh, Saudi Arabia, 11426
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81
Clinical Trial Site
Ljubljana, Slovenia, 1111
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82
Clinical Trial Site
Santiago de Compostela, A Coruña, Spain, 15706
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83
Clinical Trial Site
Barakaldo, Biscay, Spain, 48903
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84
Clinical Trial Site
Logroño, La Rioja, Spain, 26006
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85
Clinical Trial Site
Burela de Cabo, Lugo, Spain, 27880
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86
Clinical Trial Site
Málaga, Málaga, Spain, 29010
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87
Clinical Trial Site
Oviedo, Principality of Asturias, Spain, 33011
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88
Clinical Trial Site
Reus, Tarragona, Spain, 43204
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89
Clinical Trial Site
A Coruña, Spain, 15006
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90
Clinical Trial Site
Albacete, Spain, 02006
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91
Clinical Trial Site
Alicante, Spain, 03203
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92
Clinical Trial Site
Barcelona, Spain, 08036
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93
Clinical Trial Site
Barcelona, Spain, 08305
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94
Clinical Trial Site
Las Palmas, Spain, 35019
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95
Clinical Trial Site
Madrid, Spain, 28046
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96
Clinical Trial Site
Madrid, Spain, 28914
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97
Clinical Trial Site
Murcia, Spain, 30120
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98
Clinical Trial Site
Valladolid, Spain, 47012
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99
Clinical Trial Site
Zaragoza, Spain, 50009
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100
Clinical Trial Site
Cambridge, Cambridgeshire, United Kingdom, CB2 0QQ
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101
Clinical Trial Site
London, Greater London, United Kingdom, WC1N 3BG
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102
Clinical Trial Site
Manchester, Greater Manchester, United Kingdom, M13 9WL
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103
Clinical Trial Site
Salford, Greater Manchester, United Kingdom, M6 8HD
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104
Clinical Trial Site
Birmingham, West Midlands, United Kingdom, B4 6NH
Actively Recruiting
Research Team
A
Alexion Pharmaceuticals, Inc. (Sponsor)
CONTACT
How is the study designed?
Study Type
OBSERVATIONAL
Masking
N/A
Allocation
N/A
Model
N/A
Primary Purpose
N/A
Number of Arms
1
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