Actively Recruiting

All Genders
NCT04920812

MITOMICS : a Multi-OMICS Approach for the Diagnosis of Mitochondrial Diseases

Led by Centre Hospitalier Universitaire de Nice · Updated on 2025-02-25

66

Participants Needed

9

Research Sites

182 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

MITOMICS aims to determine which RNA-Seq results (from muscle or fibroblasts) are the most informative for the interpretation of VUS identified by WES for patients suspected of mitochondrial myopathy. Analysis of RNA-Seq and WES results will performed with a computational approach using an autoencoder-based method

CONDITIONS

Official Title

MITOMICS : a Multi-OMICS Approach for the Diagnosis of Mitochondrial Diseases

Who Can Participate

All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Patients suspected of a mitochondrial disease with muscular signs (clinical, histological or biochemical)
  • Patients with negative mtDNA and WES NGS in trio
  • Patients with routine muscle and skin biopsies available
  • Blood samples from parents and / or relatives available for segregation studies
  • Informed consent of the study signed by the patient or the legal representatives of the minor patient or under guardianship
  • Patients affiliated to social security
Not Eligible

You will not qualify if you...

  • Patients with suspected mitochondrial disease without muscle involvement
  • Patients for whom the mtDNA NGS and WES have not been performed
  • Patients with suspected mitochondrial disease with causal variant identified
  • Refusal to sign the informed consent for the study
  • Insufficient amount of frozen material or culture failure for fibroblasts

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 9 locations

1

CHU de Nice

Nice, CHU de NICE, France, 06003

Actively Recruiting

2

C.H.R.U. Brest

Brest, France, France

Not Yet Recruiting

3

Chu de Nantes

Nantes, France, France

Actively Recruiting

4

chu Angers

Angers, France

Actively Recruiting

5

Chu Brest

Brest, France

Not Yet Recruiting

6

APHM

Marseille, France

Actively Recruiting

7

APHM

Marseille, France

Actively Recruiting

8

Chu Montpellier

Montpellier, France

Actively Recruiting

9

CHU Nantes

Nantes, France

Not Yet Recruiting

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Research Team

S

SYLVIE BANNWARTH

CONTACT

How is the study designed?

Study Type

OBSERVATIONAL

Masking

N/A

Allocation

N/A

Model

N/A

Primary Purpose

N/A

Number of Arms

1

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