Actively Recruiting

Phase 1
Age: 18Years +
All Genders
ID07226726

Mesenchymal Stem Cell Exosome Treatment of Congenital Myasthenic Syndrome

Led by The Foundation for Orthopaedics and Regenerative Medicine · Updated on 2025-11-10

20

Participants Needed

3

Research Sites

N/A

Total Duration

On this page

AI-Summary

What this Trial Is About

This research focuses on patients diagnosed with Congenital Myasthenic Syndrome, aiming to evaluate the effects of a treatment using mesenchymal stem cell exosome solution. The study is a Phase 1, single-arm, non-controlled trial where patients are assessed before treatment and monitored afterward to track outcomes such as oxygen saturation over a six-month period. Participants receive an experimental intranasal treatment called AlloEx exosomes, which are derived from mesenchymal stem cells. The study involves prospective evaluation of patients, treatment administration, and follow-up assessments but does not include a control or placebo group. During the trial, participants will undergo regular monitoring from enrollment up to six months after treatment to evaluate oxygen saturation levels. The study requires patients to visit the treatment site and provide informed consent. The trial is sponsored by The Foundation for Orthopaedics and Regenerative Medicine and is designed to carefully track patient outcomes following the investigational treatment.

CONDITIONS

Brief Title

Patients With Congenital Myasthenic Syndrome Will be Treated With Mesenchymal Stem Cell Exosome Solution

Who Can Participate

Age: 18Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Patients must have a diagnosis of Congenital Myasthenic Syndrome by a licensed physician.
  • Patients must be able to provide informed consent or have a guardian who can.
  • Patients must be able to travel to the treatment site.
Not Eligible

You will not qualify if you...

  • Patients who are pregnant at the time of screening.
  • Patients with active cancer (malignancy) at the screening consultation.

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Your Study Journey

Screening

Duration - 2 to 4 weeks

Participants are screened for eligibility to participate in the trial.

Treatment

Duration - From enrollment to 6 months after treatment

Participants receive intranasal treatment with AlloEx exosomes derived from mesenchymal stem cells.

Trial Site Locations

Total: 3 locations

1

Prodromos Stem Cell Institute

Naples, Florida, United States, 34102

Actively Recruiting

2

Prodromos Stem Cell Institute

Irving, Texas, United States, 75039

Actively Recruiting

3

Medical Surgical Associates Center

St John's, Antigua and Barbuda

Actively Recruiting

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Research Team

C

Chadwick Prodromos

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NA

Model

SINGLE_GROUP

Primary Purpose

TREATMENT

Number of Arms

1

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