Actively Recruiting

Phase 1
Age: 18Years +
All Genders
NCT04483206

Personalized Autologous Transplant for Multiple Myeloma

Led by Emory University · Updated on 2025-05-31

90

Participants Needed

2

Research Sites

293 weeks

Total Duration

On this page

Sponsors

E

Emory University

Lead Sponsor

N

National Cancer Institute (NCI)

Collaborating Sponsor

AI-Summary

What this Trial Is About

This phase I trial studies the best dose and side effects of mephalan in treating patients with multiple myeloma who are undergoing stem cell transplant. Chemotherapy drugs, such as mephalan, work in different ways to stop the growth of cancer cells, either by killing the cells, by stopping them from dividing, or by stopping them from spreading. This trial uses a new method of dosing that is based on analysis of each individual's blood levels of melphalan after receiving a part of the dose, termed pharmacokinetic analysis. This may help to learn more about how to dose melphalan correctly and which patients are likely to benefit from a personalized dose.

CONDITIONS

Official Title

Personalized Autologous Transplant for Multiple Myeloma

Who Can Participate

Age: 18Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Clinical diagnosis of a plasma cell neoplasm requiring treatment per physician using IMWG and WHO guidelines, including rare related diseases
  • For phase A enrollment: must have received at least 2 prior lines of therapy and have estimated glomerular filtration rate (eGFR) > 40 mL/min and be eligible for 200 mg/m2 melphalan
  • For phase B enrollment: transplant must be part of first line therapy
  • Absolute neutrophil count (ANC) >= 1000/uL
  • Platelet count >= 100,000
  • Total bilirubin < 1.5 x institutional upper limit of normal or < 3 mg/dL if diagnosed with Gilbert's syndrome
  • AST and ALT < 3 x institutional upper limit of normal
  • Left ventricular ejection fraction >= 45%
  • Lung function (DLCO, FEV1, FVC) > 50% of predicted (corrected for hemoglobin)
  • ECOG performance status <= 2 (Karnofsky >= 60%) with allowance for bone pain related to multiple myeloma
  • Females of childbearing potential must have negative pregnancy test and agree to use contraception; men must agree to use contraception during and 3 months after study
  • Willing to comply with fertility requirements
  • Ability to understand and sign informed consent
  • Patients with prior or concurrent malignancy without interference with safety or efficacy assessment are eligible
Not Eligible

You will not qualify if you...

  • Progressive disease or clinical relapse between screening and planned melphalan infusion on day -3
  • History of severe heart conditions including NYHA class III or IV heart failure, recent myocardial infarction within 6 months, severe cardiomyopathy, unstable angina, uncontrolled hypertension, significant arrhythmias, or ECG abnormalities including QTc > 480 msec
  • HIV positive unless controlled with CD4 > 350, undetectable viral load, and on non-interacting therapy
  • Hepatitis B surface antigen positive unless resolved infection with negative HBV DNA PCR
  • Hepatitis C positive unless sustained virologic response with no viremia for at least 12 weeks
  • Diagnosis of POEMS syndrome, amyloid light-chain amyloidosis, or Waldenstrom macroglobulinemia
  • Active medical conditions or infections that may interfere with study or pose hazard
  • Known inability to comply with study protocol due to substance abuse, psychological disorder, or other conditions
  • Pregnant or breastfeeding women due to potential risks to fetus or infant

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

1
2
3
+1

Trial Site Locations

Total: 2 locations

1

Winship Cancer Institute of Emory University

Atlanta, Georgia, United States, 30322

Actively Recruiting

2

University Illinois Chicago

Chicago, Illinois, United States, 60607

Not Yet Recruiting

Loading map...

Research Team

C

Craig Hofmeister, MD, MPH

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NA

Model

SINGLE_GROUP

Primary Purpose

TREATMENT

Number of Arms

1

Not the Right Trial for You?

Explore thousands of other clinical trials that might be a better match.
Sign up to get personalized trial recommendations delivered to your inbox.

Already have an account? Log in here