Actively Recruiting

Early Phase 1
Age: 6Years +
All Genders
NCT03587961

Personalized Theratyping Trial

Led by George Solomon · Updated on 2026-02-02

20

Participants Needed

1

Research Sites

421 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

The purpose of this study is to explore the use of off-label CFTR modulators that may affect CFTR function in patients with CFTR mutations that are not currently approved for these drugs.

CONDITIONS

Official Title

Personalized Theratyping Trial

Who Can Participate

Age: 6Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Diagnosis of CF
  • Age 6 years or older
  • CFTR mutation that may respond to approved correctors or potentiators as judged by study investigators
  • Signed informed consent or assent
  • Stable cystic fibrosis pulmonary regimen
Not Eligible

You will not qualify if you...

  • Lung exacerbation requiring antibiotics or steroids within 28 days before trial entry
  • Current participation in another CFTR modulator study
  • Active smoking within the past 6 months
  • History of solid organ transplant
  • Conditions preventing use of CFTR modulators such as advanced cirrhosis or end-stage renal disease
  • Any condition that prevents participation as determined by the investigator
  • Use of medications with significant drug interactions or other off-label CFTR modulator use

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 1 location

1

University of Alabama at Birmingham

Birmingham, Alabama, United States, 35233

Actively Recruiting

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Research Team

H

Heather Hathorne, PhD

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NON_RANDOMIZED

Model

PARALLEL

Primary Purpose

TREATMENT

Number of Arms

3

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Personalized Theratyping Trial | DecenTrialz