Actively Recruiting

Phase 1
Age: 18Years +
All Genders
NCT04275518

A Phase Ib Study of APG-115 Single Agent or in Combination With Azacitidine or Cytarabine in Patients With AML and MDS.

Led by Ascentage Pharma Group Inc. · Updated on 2024-10-15

102

Participants Needed

14

Research Sites

286 weeks

Total Duration

On this page

Sponsors

A

Ascentage Pharma Group Inc.

Lead Sponsor

S

Suzhou Yasheng Pharmaceutical Co., Ltd.

Collaborating Sponsor

AI-Summary

What this Trial Is About

Acute myeloid leukemia is a malignant disorder characterized by the rapid, uncontrolled proliferation of malignant clonal hematopoietic stem cells that accumulate as immature, undifferentiated cells (blasts) in the bone marrow and circulation. APG-115 is a potent and orally active small-molecule MDM2 inhibitor, it binds to MDM2 protein and shows potent cell growth inhibitory activity in vitro with low nanomolar potencies in a subset of human cancer cell lines. APG-115 has demonstrated its strong antitumor activities with either daily or less frequent dosing-schedules in the acute leukemia xenograft models. This is a phase 1b, open-label, three-stages study that will initially evaluate the safety and PK/PD profile of APG-115 as a single agent, followed by a combination of APG-115 + azacytidine or cytarabine in R/R AML or MDS subjects. Patients will continue treatment for maximally 6 cycles or until progression of disease or unacceptable toxicity is observed or administrative discontinuation whichever occurs first. Patients who continue to be benefit after 6 cycles' treatment will receive additional cycles of treatment until progression of disease, unacceptable toxicity is observed or administrative discontinuation. (As long as it is proven safe).

CONDITIONS

Official Title

A Phase Ib Study of APG-115 Single Agent or in Combination With Azacitidine or Cytarabine in Patients With AML and MDS.

Who Can Participate

Age: 18Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Diagnosed with relapsed or refractory acute myeloid leukemia (AML) or relapsed/progressed high/very high risk myelodysplastic syndromes (MDS) with IPSS-R score 6.5
  • Age 18 years or older
  • Adequate organ function
  • Projected life expectancy of at least 12 weeks
  • ECOG performance status of 0 or 1
  • Able to understand study requirements and provide signed informed consent
  • White blood cell count less than 50 �d7 10^9/L (hydroxyurea allowed to meet this requirement)
Not Eligible

You will not qualify if you...

  • Diagnosis of acute promyelocytic leukemia
  • Received leukemia biotherapy within 4 weeks, small molecular targeted drug therapy within 5 half-lives, or any anti-cancer therapy within 28 days before starting study drug
  • Uncontrolled illnesses such as active infections, severe heart failure (NYHA Class III or IV), unstable angina, significant heart arrhythmia, or psychiatric/social conditions limiting study compliance
  • Active infection requiring systemic antibiotics or antifungals, known active hepatitis B or C, or HIV infection
  • Received allogeneic or autologous hematopoietic stem cell transplant within 12 months
  • Active, uncontrolled central nervous system leukemia
  • Prior treatment with systemic MDM2-p53 inhibitors
  • Other conditions making participation unsuitable per investigator judgment
  • History of other cancers within 2 years except adequately treated in situ cervical or breast carcinoma, basal or localized squamous cell skin carcinoma, or resected malignancies treated with curative intent (discussion with sponsor required)

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

1
2
3
+1

Trial Site Locations

Total: 14 locations

1

The First Hospital of Peking University

Beijing, Beijing Municipality, China, 100034

Not Yet Recruiting

2

Guangzhou panyu central hospital

Guangzhou, Guangdong, China

Actively Recruiting

3

Nanfang Hospital of Southern Medical University

Guangzhou, Guangdong, China

Actively Recruiting

4

Henan Provincial Oncology Hospital

Zhengzhou, Henan, China

Actively Recruiting

5

Union Hospital medical college Huazhong University of Science and Technology

Wuhan, Hubei, China

Actively Recruiting

6

Zhongnan Hospital of Wuhan University

Wuhan, Hubei, China

Actively Recruiting

7

Xiangya Hospital Central South University

Changsha, Hunan, China

Actively Recruiting

8

The First Affilated Hospital of Ganzhou Medical University

Suzhou, Jiangsu, China, 215636

Not Yet Recruiting

9

The First affiliated hospital of Soochow University

Suzhou, Jiangsu, China

Actively Recruiting

10

The First Affiliated Hospital of Nanchang University

Nanchang, Jiangxi, China, 330006

Not Yet Recruiting

11

First Hospital of Jilin University

Changchun, Jilin, China

Actively Recruiting

12

Shanghai Jiao Tong University school of medicine Ruijing Hospital

Shanghai, Shanghai Municipality, China

Actively Recruiting

13

Shanghai Sixth people's Hospital

Shanghai, Shanghai Municipality, China

Actively Recruiting

14

Blood Diseases Hospital Chinese Academy of Medical Sciences

Tianjin, Tianjin Municipality, China, 300020

Actively Recruiting

Loading map...

Research Team

J

Junyuan Qi, M.D.

CONTACT

B

Bo Jiang, M.D.

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NON_RANDOMIZED

Model

PARALLEL

Primary Purpose

TREATMENT

Number of Arms

2

Not the Right Trial for You?

Explore thousands of other clinical trials that might be a better match.
Sign up to get personalized trial recommendations delivered to your inbox.

Already have an account? Log in here