Actively Recruiting
A Phase II, Placebo Controlled, Clinical Trial of Topical TolaSure Targeting Aggregated Mutant Keratin in Epidermolysis Bullosa Simplex
Led by BioMendics, LLC · Updated on 2025-09-11
40
Participants Needed
2
Research Sites
52 weeks
Total Duration
On this page
Sponsors
B
BioMendics, LLC
Lead Sponsor
N
Northwestern University Feinberg School of Medicine
Collaborating Sponsor
AI-Summary
What this Trial Is About
This Phase II clinical study will assess the efficacy, safety and tolerability of topical TolaSure Gel in adults and pediatric patients (4 years of age and older) diagnosed with generalized intermediate to severe epidermolysis bullosa simplex (EBS). Each patient (40 to complete) will be enrolled in the study and will be randomized to receive either TolaSure Gel or a topical Placebo for daily application for 2-months. After 2-months, all patients will receive TolaSure Gel to daily apply for an additional 2-months. A remote follow-up visit will occur 2-months after the end of study. Total time in the study is 6-months. Patients will be applying study medication to randomized treatment area(s) (a minimum of \~2-3% Body Surface Area (BSA)), with the option to treat their feet as well throughout the study.
CONDITIONS
Official Title
A Phase II, Placebo Controlled, Clinical Trial of Topical TolaSure Targeting Aggregated Mutant Keratin in Epidermolysis Bullosa Simplex
Who Can Participate
Eligibility Criteria
You may qualify if you...
- Patient is male or female aged 4 years or older.
- Diagnosed with generalized intermediate to severe epidermolysis bullosa simplex (EBS) or genetic mutation in K14 or K5 genes consistent with this severity.
- Actively experiencing a blistering flare in lower extremities (between knee and ankle or thigh) or torso (excluding groin/apocrine areas).
- Flare area covers about 2-3% of body surface area with intact or recently ruptured blisters.
- Target lesional area is not infected and has not been treated with topical antibiotics within 14 days.
- Women of childbearing potential must have a negative pregnancy test, agree to use effective birth control during and 3 months after the study, and not be nursing.
- Laboratory blood and urine values are within normal or acceptable ranges.
- In good general health without conditions that impair study evaluation or increase risk.
- Agree to avoid other topical therapies or dressings on target areas during the study.
- Able and willing to follow study procedures and sign informed consent or assent.
You will not qualify if you...
- Use of any investigational drug or therapy within 30 days.
- Use of systemic steroids within 30 days.
- Use of topical steroids within 14 days (except inhaled or ophthalmic steroids).
- Use of systemic antibiotics within 7 days.
- Currently undergoing chemotherapy or radiation.
- Surgery within the last 2 weeks except minor, cosmetic, or dental procedures.
- Starting chronic medications less than 30 days before study medication.
- Current cancer treatment.
- History of severe vitamin, mineral, or protein deficiency.
- Current systemic infection.
- HIV/AIDS.
- Non-EBS skin diseases or conditions that pose risk or interfere with treatment or assessments.
- Illness or conditions likely to interfere with study participation.
- Inability to attend visits or follow study protocol.
- Investigator or immediate family member of investigational team.
- Other reasons deemed unsuitable by the investigator.
AI-Screening
AI-Powered Screening
Complete this quick 3-step screening to check your eligibility
Trial Site Locations
Total: 2 locations
1
Stanford University School of Medicine, Dermatology Department
Palo Alto, California, United States, 94304
Actively Recruiting
2
NU Dermatolgy CTU
Chicago, Illinois, United States, 60611
Actively Recruiting
How is the study designed?
Study Type
INTERVENTIONAL
Masking
QUADRUPLE
Allocation
RANDOMIZED
Model
CROSSOVER
Primary Purpose
TREATMENT
Number of Arms
2
Not the Right Trial for You?
Explore thousands of other clinical trials that might be a better match.
Sign up to get personalized trial recommendations delivered to your inbox.
Already have an account? Log in here