Actively Recruiting

Phase 1
Phase 2
Age: 18Years +
All Genders
NCT04422912

A Phase 1/2, Open-label, Safety and Dosing Study of Autologous CART Cells (Desmoglein 3 Chimeric Autoantibody Receptor T Cells [DSG3-CAART] or CD19-specific Chimeric Antigen Receptor T Cells [CABA-201]) in Subjects With Active, Pemphigus Vulgaris (RESET-PV)

Led by Cabaletta Bio · Updated on 2025-12-17

40

Participants Needed

13

Research Sites

430 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

A phase 1/2, open-label, safety and dosing study of autologous CART cells (desmoglein 3 chimeric autoantibody receptor T cells \[DSG3-CAART\] or CD19-specific Chimeric Antigen Receptor T cells \[CABA-201\]) in subjects with active, pemphigus vulgaris

CONDITIONS

Official Title

A Phase 1/2, Open-label, Safety and Dosing Study of Autologous CART Cells (Desmoglein 3 Chimeric Autoantibody Receptor T Cells [DSG3-CAART] or CD19-specific Chimeric Antigen Receptor T Cells [CABA-201]) in Subjects With Active, Pemphigus Vulgaris (RESET-PV)

Who Can Participate

Age: 18Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Confirmed diagnosis of mucosal pemphigus vulgaris (mPV) by biopsy and positive anti-DSG3 antibody test (for DSG3-CAART; closed to enrollment)
  • mPV inadequately managed by at least one standard immunosuppressive therapy (for DSG3-CAART; closed to enrollment)
  • Active mucosal pemphigus vulgaris at screening (for DSG3-CAART; closed to enrollment)
  • Positive anti-DSG3 antibody test at screening (for DSG3-CAART; closed to enrollment)
  • Age 18 years or older (for CABA-201 sub-study; open to enrollment)
  • Confirmed diagnosis of pemphigus vulgaris by biopsy and positive DSG3 ELISA, IIF, or DIF test (for CABA-201 sub-study; open to enrollment)
  • Pemphigus vulgaris inadequately managed by at least one standard immunosuppressive therapy (for CABA-201 sub-study; open to enrollment)
  • Active pemphigus vulgaris at screening (for CABA-201 sub-study; open to enrollment)
  • Positive DSG3 ELISA test at screening (for CABA-201 sub-study; open to enrollment)
Not Eligible

You will not qualify if you...

  • Active cutaneous lesions indicating mucocutaneous rather than mucosal-dominant pemphigus vulgaris
  • Received rituximab in the last 12 months unless symptoms have worsened or antibody levels have increased recently
  • Taking prednisone at a dose higher than 0.25 mg/kg/day
  • Having another autoimmune disorder requiring immunosuppressive therapy
  • Received any investigational treatment within the last 3 months
  • For CABA-201 sub-study: having paraneoplastic pemphigus or active cancer (except non-melanoma skin cancer) or cancer diagnosed within the last 5 years
  • For CABA-201 sub-study: received rituximab or other anti-CD20 or anti-CD19 therapies within 12 months unless symptoms or antibody levels have worsened
  • For CABA-201 sub-study: treatment with any investigational agent within 4 weeks or 5 half-lives, whichever is longer

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 13 locations

1

Stanford University, Dept. of Dermatology

Redwood City, California, United States, 94063

Actively Recruiting

2

UC Davis, Dept. of Dermatology

Sacramento, California, United States, 95816

Actively Recruiting

3

Yale University

New Haven, Connecticut, United States, 06520

Actively Recruiting

4

Northwestern University

Chicago, Illinois, United States, 60611

Actively Recruiting

5

University of Iowa

Iowa City, Iowa, United States, 52242

Actively Recruiting

6

Brigham and Women's Hospital

Boston, Massachusetts, United States, 02115

Actively Recruiting

7

Mount Sinai - Icahn School of Medicine

New York, New York, United States, 10029

Withdrawn

8

Columbia University

New York, New York, United States, 10032

Actively Recruiting

9

University of North Carolina, Department of Dermatology

Chapel Hill, North Carolina, United States, 27516

Withdrawn

10

University of Pennsylvania

Philadelphia, Pennsylvania, United States, 19104

Actively Recruiting

11

UT Southwestern Medical Center, Dept. of Dermatology

Dallas, Texas, United States, 75235

Actively Recruiting

12

MD Anderson Texas Medical Center

Houston, Texas, United States, 77030

Actively Recruiting

13

University of Washington

Seattle, Washington, United States, 98109

Completed

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Research Team

C

Cabaletta Bio

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NON_RANDOMIZED

Model

SEQUENTIAL

Primary Purpose

TREATMENT

Number of Arms

2

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