Actively Recruiting

Phase 2
Age: 18Years +
All Genders
NCT06985147

A Phase 2, Open-Label Study of DISC-3405 in Participants With Polycythemia Vera (PV)

Led by Disc Medicine, Inc · Updated on 2026-03-04

60

Participants Needed

14

Research Sites

181 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

This open-label, multicenter, within-participant dose escalation study examining up to 2 dose levels of DISC-3405 will assess the safety, tolerability, efficacy, pharmacokinetics, and pharmacodynamics of DISC-3405 in participants with polycythemia vera (PV).

CONDITIONS

Official Title

A Phase 2, Open-Label Study of DISC-3405 in Participants With Polycythemia Vera (PV)

Who Can Participate

Age: 18Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Aged 18 years or older at the time of signing the informed consent form
  • Meet revised 2022 World Health Organization criteria for diagnosis of polycythemia vera
  • Screening blood counts with hematocrit less than 45% or less than 48% if followed by phlebotomy within 2 weeks
  • White blood cells between 4000/µL and 20,000/µL, platelets between 100,000/µL and 1,000,000/µL
  • At least 3 phlebotomies in the 26 weeks before screening or at least 5 in the 52 weeks before screening, with at least 1 within 12 weeks prior
  • If receiving cytoreductive therapy, must have been on stable dose for at least 2 months and therapy for at least 6 months or have decreasing dose with approval
  • If treated with phlebotomy alone, must have stopped cytoreductive therapy 6 months before screening
  • Eastern Cooperative Oncology Group performance status 0 or 1, or 2 with approval
  • If male with female partner(s) of childbearing potential, agree to use effective contraception during study and for 120 days after last dose
  • If female, must be postmenopausal, surgically sterile, or agree to use effective contraception during study and for 120 days after last dose
  • Negative pregnancy test for females of childbearing potential
  • Able to understand study aims and provide written informed consent
  • Able to comply with all study procedures
Not Eligible

You will not qualify if you...

  • Clinically significant laboratory abnormalities at screening
  • Require phlebotomy at hematocrit levels less than 45%
  • Significant blood clots within 2 months before treatment
  • Active or chronic bleeding within 6 months before treatment
  • Severe kidney dysfunction with estimated glomerular filtration rate below 30 mL/min/1.73 m2
  • History of invasive cancers within 5 years except some localized cured cancers
  • Certain early skin cancers unless adequately treated before entry
  • Use of busulfan, pipobroman, or phosphorus-32 within 7 months before screening
  • Major surgery within 8 weeks before screening or incomplete recovery
  • Allergic reactions or anaphylaxis to investigational product or foods
  • History of alcohol dependence or excessive use
  • Active HIV, hepatitis B or C infections
  • Other medical or psychiatric conditions that pose unacceptable risk
  • Conditions or medications that interfere with data interpretation, including recent major psychiatric exacerbations
  • Pregnant or breastfeeding females
  • Participation in other investigational studies within 30 days or 5 drug half-lives
  • Previous use of certain hepcidin-inducing agents not allowed without sponsor discussion

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 14 locations

1

Mayo Clinic in Arizona

Phoenix, Arizona, United States, 85054

Actively Recruiting

2

USC Norris Comprehensive Cancer Center

Los Angeles, California, United States, 90033

Actively Recruiting

3

UCLA Health

Los Angeles, California, United States, 90095

Actively Recruiting

4

Keck Medicine of USC - Cancer Clinic- Newport Beach

Newport Beach, California, United States, 92663

Actively Recruiting

5

Mayo Clinic in Florida

Jacksonville, Florida, United States, 32224

Actively Recruiting

6

Mayo Clinic in Minnesota

Rochester, Minnesota, United States, 55905

Actively Recruiting

7

Siteman Cancer Center - Washington University St. Louis

St Louis, Missouri, United States, 63110

Actively Recruiting

8

Atrium Health - Levine Cancer Center

Charlotte, North Carolina, United States, 28204

Actively Recruiting

9

Duke University

Durham, North Carolina, United States, 27705

Actively Recruiting

10

Atrium Health Wake Forest Baptist Medical Center

Winston-Salem, North Carolina, United States, 27157

Actively Recruiting

11

Ohio State University

Columbus, Ohio, United States, 43210

Actively Recruiting

12

Oregon Health & Science University

Portland, Oregon, United States, 97239

Actively Recruiting

13

MD Anderson Cancer Center

Houston, Texas, United States, 77030

Actively Recruiting

14

University of Washington - Fred Hutchinson Cancer Research Center

Seattle, Washington, United States, 98109

Actively Recruiting

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Research Team

D

Disc Medicine Clinical Trials

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NA

Model

SEQUENTIAL

Primary Purpose

TREATMENT

Number of Arms

1

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