Actively Recruiting

Phase 1
Age: 18Years +
All Genders
NCT04827810

A Phase I Safety and Pharmacokinetic Study of Gamitrinib Administered Intravenously to Patients With Advanced Cancer

Led by Fox Chase Cancer Center · Updated on 2025-06-29

42

Participants Needed

1

Research Sites

268 weeks

Total Duration

On this page

Sponsors

F

Fox Chase Cancer Center

Lead Sponsor

N

National Institutes of Health (NIH)

Collaborating Sponsor

AI-Summary

What this Trial Is About

This is a first-in-human, phase I, open-label, non-randomized dose-escalation and dose-expansion study with the primary objective to determine the safety profile of small molecule, mitochondrial-targeted Hsp90 inhibitor, gamitrinib, including identification of dose-limiting toxicities (DLT) and maximum tolerated dose (MTD) in patients with advanced cancers. A secondary objective of the study is to determine the recommended dose and regimen(s) for a phase II study. This study is based on preclinical data demonstrating the anticancer activity, unique mechanism of action and preliminary safety of gamitrinib. In the dose-finding portion of this study, gamitrinib formulated in Lipoid S100®-based formulation will be administered as a 1-hour IV infusion once weekly for four weeks as 28-day treatment cycles. Up to 36 patients will be enrolled in the dose-escalation component of the study based on anticipated cohorts. The starting dose will be 10 mg, corresponding to allometric scaling) from the most sensitive species (rats) in the 29-day GLP toxicology and toxicokinetic studies with 14-day recovery period of gamitrinib. Dose-escalation will follow a 3+3 design. Six patients will be enrolled in the dose-expansion component of the study at MTD for the purpose of exploring pharmacodynamic effects via tumor pre and on-therapy biopsies.

CONDITIONS

Official Title

A Phase I Safety and Pharmacokinetic Study of Gamitrinib Administered Intravenously to Patients With Advanced Cancer

Who Can Participate

Age: 18Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Histologically confirmed advanced cancer refractory to standard therapy or with no available standard therapy
  • For dose escalation, solid tumors and lymphoma may have measurable or evaluable disease per RECIST v1.1 or RECIL 2017 criteria
  • For dose expansion, at least one measurable tumor site per RECIST v1.1 or RECIL 2017
  • Willingness to undergo mandatory tumor biopsies before and during treatment (dose expansion phase)
  • All prior cancer therapies stopped for at least 14 days (28 days for mitomycin C or nitrosoureas) before treatment start
  • Age over 18 years
  • ECOG performance status of 0 to 2
  • Normal organ and marrow function as defined by blood counts and liver/kidney tests
  • Negative pregnancy test for women of childbearing potential within 7 days before treatment
  • Ability to understand and sign informed consent
  • Use of effective contraception during and for 90 days after the trial for women and men if not surgically sterile
Not Eligible

You will not qualify if you...

  • Symptomatic brain metastases
  • Current treatment in another therapeutic clinical trial
  • Uncontrolled hypertension above 150/100 mm Hg despite medication
  • Active infection requiring intravenous treatment
  • Known HIV or AIDS-related illness
  • Certain serious heart or vascular events within the last 6 months
  • Other severe medical or psychiatric conditions increasing risk or interfering with study participation
  • Pregnancy or breastfeeding

AI-Screening

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Trial Site Locations

Total: 1 location

1

Fox Chase Cancer Center

Philadelphia, Pennsylvania, United States, 19111

Actively Recruiting

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Research Team

A

Anthony Olszanski, MD

CONTACT

M

Matthew Zibelman, MD

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NON_RANDOMIZED

Model

SEQUENTIAL

Primary Purpose

TREATMENT

Number of Arms

7

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