Actively Recruiting

Phase 1
Phase 2
Age: 2Years +
All Genders
NCT04811560

A Phase 1/2 Study of Bleximenib in Participants With Acute Leukemia (cAMeLot-1)

Led by Janssen Research & Development, LLC · Updated on 2026-05-08

420

Participants Needed

103

Research Sites

487 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

The purpose of this study is to determine the recommended Phase 2 dose(s) (RP2D\[s\]) of bleximenib in phase 1 Part 1 (Dose Escalation) and to determine the safety and tolerability at RP2D in Phase 1 Part 2 (Dose expansion). The purpose of the Phase 2 part of the study is to evaluate the efficacy of bleximenib at the RP2D.

CONDITIONS

Official Title

A Phase 1/2 Study of Bleximenib in Participants With Acute Leukemia (cAMeLot-1)

Who Can Participate

Age: 2Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • For Phase 1 pediatric cohort: Age 2 years to less than 18 years; for all other cohorts: 18 years and older
  • Have relapsed or refractory acute leukemia and have exhausted or are ineligible for available treatment options
  • Acute leukemia with gene alterations in KMT2A, NPM1, or NUP98/NUP214
  • For Phase 2: Adults over 18 years with relapsed/refractory acute myeloid leukemia diagnosed by WHO 2022 criteria
  • AML must have KMT2A rearrangement or NPM1 mutations
  • Pretreatment lab values: WBC count ≤ 20 x 10^9/L; adults with kidney function (GFR) ≥ 30 mL/min; children with kidney function (GFR) ≥ 40 mL/min
  • ECOG performance status 0, 1, or 2; pediatric participants must have Lansky scale ≥ 70 if under 16 or Karnofsky scale ≥ 70 if 16 or older
  • Females of childbearing potential must have a negative pregnancy test at screening and within 48 hours before first dose
  • Agree to contraception requirements and avoid sperm or egg donation or freezing during and for specified time after treatment
Not Eligible

You will not qualify if you...

  • Diagnosis of acute promyelocytic leukemia, Down syndrome-associated leukemia, or juvenile myelomonocytic leukemia
  • Active central nervous system disease
  • Prior solid organ transplant
  • QTc interval ≥ 450 msec for males or ≥ 470 msec for females or family history of Long QT syndrome
  • Stem cell transplant within 3 months before first dose, graft versus host disease, donor lymphocyte infusion within 1 month, or need for immunosuppressive therapy beyond low-dose steroids
  • Prior cancer immunotherapy within 4 weeks or blinatumomab within 2 weeks before enrollment
  • Other cancer therapies within 4 weeks or 5 half-lives before enrollment, whichever is shorter

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 103 locations

1

City of Hope Phoenix

Goodyear, Arizona, United States, 85338

Terminated

2

City of Hope

Duarte, California, United States, 91010

Actively Recruiting

3

University of California Irvine Medical Center

Orange, California, United States, 92868

Completed

4

University of California San Francisco

San Francisco, California, United States, 94143

Actively Recruiting

5

UCSF Benioff Children's Hospital

San Francisco, California, United States, 94158

Actively Recruiting

6

University of Chicago

Chicago, Illinois, United States, 60637

Actively Recruiting

7

St Francis Hospital & Health Centers Indiana Blood and Marrow Transplantation

Indianapolis, Indiana, United States, 46237

Actively Recruiting

8

Norton Cancer Institute

Louisville, Kentucky, United States, 40207

Completed

9

Massachusetts General Hospital

Boston, Massachusetts, United States, 02114

Actively Recruiting

10

Dana Farber Cancer Institute

Boston, Massachusetts, United States, 02115

Actively Recruiting

11

Karmanos Cancer Institute

Detroit, Michigan, United States, 48201 2013

Actively Recruiting

12

Start Midwest

Grand Rapids, Michigan, United States, 49546

Actively Recruiting

13

University of New Mexico

Albuquerque, New Mexico, United States, 87131

Actively Recruiting

14

Roswell Park Comprehensive Cancer Center

Buffalo, New York, United States, 14263

Actively Recruiting

15

NYU Langone Medical Center

New York, New York, United States, 10016

Actively Recruiting

16

Montefiore Medical Center

The Bronx, New York, United States, 10467

Actively Recruiting

17

Oregon Health And Science University

Portland, Oregon, United States, 97239

Actively Recruiting

18

Fox Chase Cancer Center

Philadelphia, Pennsylvania, United States, 19111

Actively Recruiting

19

Maine Health

Providence, Rhode Island, United States, 02903

Actively Recruiting

20

University of Tennessee Medical Center

Knoxville, Tennessee, United States, 37920

Actively Recruiting

21

Baylor University Medical Center

Dallas, Texas, United States, 75246

Actively Recruiting

22

Houston Methodist Hospital

Houston, Texas, United States, 77030-2740

Actively Recruiting

23

MD Anderson

Houston, Texas, United States, 77030

Actively Recruiting

24

San Antonio Methodist TX Transplant Physicians Group

San Antonio, Texas, United States, 78229

Actively Recruiting

25

Virginia Commonwealth University

Richmond, Virginia, United States, 23298

Actively Recruiting

26

Swedish Cancer Institute

Seattle, Washington, United States, 98104

Actively Recruiting

27

Medical College of WI at Froedtert

Milwaukee, Wisconsin, United States, 53226

Actively Recruiting

28

Monash Medical Centre

Clayton, Australia, 3168

Actively Recruiting

29

Royal Perth Hospital

Perth, Australia, 6000

Actively Recruiting

30

Gold Coast University Hospital

Southport, Australia, 4211

Actively Recruiting

31

Ghent University Hospital

Ghent, Belgium, 9000

Actively Recruiting

32

Instituto D Or de Pesquisa e Ensino

Brasília, Brazil, 70390 700

Actively Recruiting

33

Liga Norte Riograndense Contra O Cancer

Natal, Brazil, 59062 000

Actively Recruiting

34

Ministerio da Saude Instituto Nacional do Cancer

Rio de Janeiro, Brazil, 20230 130

Actively Recruiting

35

Fundacao Faculdade de Medicina Instituto do Cancer do Estado de Sao Paulo

São Paulo, Brazil, 01246 000

Actively Recruiting

36

Instituto D Or de Pesquisa e Ensino IDOR

São Paulo, Brazil, 01401 002

Actively Recruiting

37

Fundacao Antonio Prudente A C Camargo Cancer Center

São Paulo, Brazil, 01509 900

Actively Recruiting

38

Vancouver Coastal Health

Vancouver, British Columbia, Canada, V5Z 1M9

Actively Recruiting

39

Princess Margaret Cancer Centre University Health Network

Toronto, Ontario, Canada, M5G 1X6

Actively Recruiting

40

Hopital Maisonneuve Rosemont

Montreal, Quebec, Canada, H1T 2M4

Actively Recruiting

41

Peking University First Hospital

Beijing, China, 100034

Actively Recruiting

42

The First Hospital of Jilin University

Changchun, China, 130021

Actively Recruiting

43

West China Hospital Si Chuan University

Chengdu, China, 610041

Actively Recruiting

44

Nanfang Hospital of Southern Medical Hospital

Guangzhou, China, 510515

Actively Recruiting

45

First Affiliated Hospital Medical School of Zhejiang University

Hangzhou, China, 310009

Actively Recruiting

46

Qilu Hospital of Shandong University

Jinan, China, 250012

Actively Recruiting

47

The First Affiliated Hospital of NanChang University

Nanchang, China, 330006

Actively Recruiting

48

Zhongda Hospital Southeast University

Nanjing, China, 210009

Actively Recruiting

49

Institute of Hematology and Blood Diseases Hospital

Tianjin, China, 301609

Actively Recruiting

50

The First Affiliated Hospital of Wenzhou Medical University

Wenzhou, China, 325000

Actively Recruiting

51

Union Hospital Tongji Medical College of Huazhong University of Science and Technology

Wuhan, China, 430022

Actively Recruiting

52

Henan Cancer Hospital

Zhengzhou, China, 450003

Actively Recruiting

53

Hopital Jean Minjoz

Besançon, France, 25000

Actively Recruiting

54

Institut Paoli Calmettes

Marseille, France, 13009

Actively Recruiting

55

CHU de Nantes hotel Dieu

Nantes, France, 44093

Actively Recruiting

56

Hopital Saint Louis

Paris, France, 75010

Actively Recruiting

57

Hopital trousseau- APHP

Paris, France, 75012

Actively Recruiting

58

Centre Hospitalier Universitaire (CHU) de Bordeaux Hopital HautLeveque Centre Francois Magendie

Pessac, France, 33604

Completed

59

CHU Lyon Sud

Pierre-Bénite, France, 69310

Actively Recruiting

60

Hôpitaux Universitaires de Strasbourg - Hôpital de Hautepierre

Strasbourg, France, 67098

Actively Recruiting

61

Institut Universitaire du Cancer Toulouse Oncopole

Toulouse, France, 31059

Actively Recruiting

62

CHU Bretonneau

Tours, France, 37044

Actively Recruiting

63

CHRU de Nancy - Hopitaux de Brabois

Vandœuvre-lès-Nancy, France, 54500

Actively Recruiting

64

CHRU Nancy Brabois

Vandœuvre-lès-Nancy, France, 54511

Actively Recruiting

65

Gustave Roussy

Villejuif, France, 94805

Actively Recruiting

66

Carmel Medical Center

Haifa, Israel, 3436212

Actively Recruiting

67

Hadassah University Hospita Ein Kerem

Jerusalem, Israel, 9112001

Actively Recruiting

68

Sheba Medical Center

Ramat Gan, Israel, 52621

Actively Recruiting

69

Tel Aviv Sourasky Medical Center

Tel Aviv, Israel, 6423906

Actively Recruiting

70

Kyushu University Hospital

Fukuoka, Japan, 812-0054

Active, Not Recruiting

71

Fukushima Medical University Hospital

Fukushima, Japan, 960 1295

Active, Not Recruiting

72

Kanazawa University Hospital

Kanazawa, Japan, 920 8641

Active, Not Recruiting

73

National Cancer Center Hospital East

Kashiwa, Japan, 277-8577

Active, Not Recruiting

74

Kobe City Medical Center General Hospital

Kobe, Japan, 650 0047

Active, Not Recruiting

75

Gunmaken Saiseikai Maebashi Hospital

Maebashi, Japan, 371-0821

Active, Not Recruiting

76

Nagoya University Hospital

Nagoya, Japan, 466-8560

Completed

77

Hokkaido University Hospital

Sapporo, Japan, 060-8648

Active, Not Recruiting

78

NTT Medical Center Tokyo

Tokyo, Japan, 141-8625

Active, Not Recruiting

79

Yamagata University Hospital

Yamagata, Japan, 990 2331

Completed

80

University of Fukui Hospital

Yoshida, Japan, 910-1193

Completed

81

Seoul National University Hospital

Seoul, South Korea, 03080

Actively Recruiting

82

Asan Medical Center

Seoul, South Korea, 05505

Actively Recruiting

83

Samsung Medical Center

Seoul, South Korea, 06351

Actively Recruiting

84

Hosp Univ Vall D Hebron

Barcelona, Spain, 08035

Actively Recruiting

85

Hosp Clinic de Barcelona

Barcelona, Spain, 08036

Actively Recruiting

86

Hosp. Gral. Univ. Gregorio Maranon

Madrid, Spain, 28007

Actively Recruiting

87

Hospital Infantil Universitario Nino Jesus

Madrid, Spain, 28009

Actively Recruiting

88

Hosp Univ Fund Jimenez Diaz

Madrid, Spain, 28040

Actively Recruiting

89

Clinica Univ. de Navarra

Pamplona, Spain, 31008

Actively Recruiting

90

Hosp Clinico Univ de Salamanca

Salamanca, Spain, 37007

Actively Recruiting

91

Hosp. Virgen Del Rocio

Seville, Spain, 41013

Actively Recruiting

92

Hosp. Clinico Univ. de Valencia

Valencia, Spain, 46010

Actively Recruiting

93

China Medical University Hospital

Taichung, Taiwan, 404327

Actively Recruiting

94

National Cheng Kung University Hospital

Tainan, Taiwan, 704

Actively Recruiting

95

National Taiwan University Hospital

Taipei, Taiwan, 10043

Actively Recruiting

96

University Hospital of Wales

Cardiff, United Kingdom, CF14 4XW

Actively Recruiting

97

Leeds Teaching Hospitals NHS Trust

Leeds, United Kingdom, LS9 7TF

Actively Recruiting

98

The Clatterbridge Cancer Centre

Liverpool, United Kingdom, L7 8YA

Actively Recruiting

99

Guys and St Thomas NHS Foundation Trust

London, United Kingdom, SE1 9RT

Actively Recruiting

100

University College London Hospitals

London, United Kingdom, W1T 7HA

Actively Recruiting

101

The Christie Nhs Foundation Trust

Manchester, United Kingdom, M20 4BX

Actively Recruiting

102

Oxford University Hospitals NHS Trust

Oxfordshire, United Kingdom, OX3 7LE

Actively Recruiting

103

University Hospitals Plymouth NHS Trust

Plymouth, United Kingdom, PL6 8DH

Actively Recruiting

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Research Team

S

Study Contact

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NA

Model

SEQUENTIAL

Primary Purpose

TREATMENT

Number of Arms

1

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