Actively Recruiting

Phase 2
Age: 18Years +
All Genders
NCT04423185

PLATFORM Study of Precision Medicine for Rare Tumors

Led by Cancer Institute and Hospital, Chinese Academy of Medical Sciences · Updated on 2025-02-11

770

Participants Needed

1

Research Sites

411 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

A Phase II, open label, non-randomized, multiple-arm, single-center clinical trial in patients with advanced rare solid tumors who failed to standard treatment.

CONDITIONS

Official Title

PLATFORM Study of Precision Medicine for Rare Tumors

Who Can Participate

Age: 18Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Male or female aged 18 years or older at the time of consent
  • Confirmed advanced or metastatic rare solid tumor by tissue diagnosis
  • ECOG performance score of 0 or 1 evaluated within 7 days before first treatment
  • Expected survival of at least 12 weeks
  • At least one measurable lesion by imaging with clear disease progression before or after radiotherapy
  • Disease progressed after standard treatment per NCCN or CSCO guidelines, no standard effective treatment, not suitable for standard treatment, or patient refuses standard treatment
  • Provide fresh biopsy tissue samples within 12 weeks before first drug use and peripheral blood samples for molecular typing
  • Must have primary or metastatic paraffin tissue specimen (without radiotherapy) within 2 years, 15-20 slices, 4-6 micrometers thick
  • If pleural or peritoneal effusion present, provide 300 ml samples for pathological cytology
  • If metastatic lesion biopsy possible, provide fresh tissue specimen (optional)
  • Patients with specific actionable mutations will enroll targeted therapy sub-studies; others will enroll immunotherapy sub-study
  • After disease progression, fresh tissue samples should be obtained if possible
  • Toxicity from previous treatment recovered to Grade 1 or baseline (except hair loss)
  • Negative pregnancy test for women of childbearing potential; all patients agree to use effective contraception during and for 8 weeks after treatment
  • Signed informed consent and willingness to follow study and report adverse events
Not Eligible

You will not qualify if you...

  • Prior treatment with PD-1 or PD-L1 drugs
  • Prior treatment with targeted drugs used in this study
  • Allergic reactions to study drug ingredients or excipients
  • History of interstitial lung disease or radiation pneumonitis
  • Unstable brain metastases or requiring increased steroids for CNS disease
  • Uncontrolled large pleural effusion or ascites
  • Failure to meet sub-study inclusion criteria
  • Major surgery or incomplete wound healing within 28 days before first treatment; chest radiotherapy over 30 Gy within 6 months
  • Use of other investigational drugs within 14 days or 5 half-lives prior to first dose
  • Use of live vaccines within 30 days prior to first dose (except seasonal influenza without live virus)
  • Hypersensitivity to study drugs or chemically similar drugs
  • Active infection needing systemic treatment or HIV, active hepatitis B or C, active tuberculosis, or positive syphilis antibody
  • Uncontrolled systemic diseases including severe mental, neurological, respiratory, cardiovascular, liver, kidney diseases, or uncontrolled severe hypertension
  • Myocardial infarction, coronary artery or cerebrovascular events within 3 months
  • Diagnosis of another malignant tumor within 5 years (except certain resected carcinomas)
  • History of organ transplantation including stem cell transplantation (except corneal or hair transplantation without immunosuppression)
  • Significant cardiovascular disease or arrhythmias requiring treatment
  • Abnormal heart conduction or QT interval prolongation beyond specified limits
  • Left ventricular ejection fraction below 50%
  • Abnormal laboratory values indicating inadequate bone marrow or organ function
  • History of swallowing dysfunction or gastrointestinal diseases affecting oral drug absorption
  • Pregnant or breastfeeding women
  • Serious medical or mental illness affecting treatment compliance
  • Any other risks deemed unsuitable by investigators

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 1 location

1

Cancer hospital Chinese Academy of Medical Sciences

Beijing, China, 100021

Actively Recruiting

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Research Team

N

Ning Li, Doctor

CONTACT

S

Shuhang Wang, Doctor

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NON_RANDOMIZED

Model

PARALLEL

Primary Purpose

TREATMENT

Number of Arms

17

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