Actively Recruiting

Phase 2
Age: 1Year - 17Years
All Genders
ID06564493

A Prospective, Open-label, Randomized Controlled, Multicenter Clinical Study of Matched Sibling Donor Hematopoietic Stem Cell Transplantation Using a TBI or TMLI Conditioning Regimen for Pediatric Lymphoblastic Leukemia

Led by The First Affiliated Hospital of Zhengzhou University · Updated on 2025-02-18

170

Participants Needed

1

Research Sites

21 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

Researchers are comparing two different conditioning treatments for children with acute lymphoblastic leukemia (ALL) who are undergoing matched sibling donor hematopoietic stem cell transplantation (MSD-HSCT). The study evaluates Total Body Irradiation (TBI) against Total Marrow, Central Nervous System and Lymphoid Irradiation (TMLI), both combined with cyclophosphamide. The goal is to find which regimen better eliminates leukemia cells in bone marrow and lymphoid tissues while causing less damage to healthy tissues, potentially reducing relapse and transplant-related complications. Participants receive either the TMLI or TBI radiation therapy, each delivering a total dose of 12 Gy over three days with twice daily fractions. Both groups also receive cyclophosphamide at a total dose of 120 mg/kg given over two days. The study is randomized and open-label, conducted across multiple centers, focusing on pediatric patients aged 1 to 17 years. The treatments are given before the stem cell transplant to prepare the body. During the study, participants will be monitored for 2 years after transplantation to assess relapse-free survival, overall survival, and acute graft-versus-host disease within the first 100 days. Additional outcomes include transplant-related mortality, relapse rate, and adverse events related to conditioning. The study tracks patient health through clinical assessments to determine which conditioning approach offers better outcomes and lower toxicity in children with ALL.

CONDITIONS

Brief Title

A Prospective, Open-label, Randomized Controlled, Multicenter Clinical Study of MSD-HSCT Using a TBI or TMLI Conditioning Regimen for Pediatric ALL

Who Can Participate

Age: 1Year - 17Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Participants or guardians must voluntarily sign a written informed consent form.
  • Male or female participants aged 1 to 17 years.
  • Diagnosed with acute lymphoblastic leukemia (ALL) according to WHO criteria.
  • Leukemia must be in hematologic remission (complete remission) before transplantation.
  • Suitable matched sibling donor must be available.
  • Participant must consent to undergo matched sibling donor hematopoietic stem cell transplantation (MSD-HSCT).
  • Karnofsky Performance Status score of 70 or higher.
  • No significant organ dysfunction: cardiac function NYHA class II or lower, liver enzymes ALT and AST no more than 2.5 times normal, bilirubin no more than 2 times normal, renal creatinine no more than 1.5 times normal or creatinine clearance at least 60 ml/min.
  • No significant pulmonary issues such as dyspnea, oxygen therapy requirement, interstitial lung disease, or active pulmonary infections.
Not Eligible

You will not qualify if you...

  • Not in hematologic remission before transplantation.
  • Chose a donor other than a matched sibling donor.
  • Severe cardiac, liver, kidney, or lung diseases making conditioning intolerable.
  • Active or refractory infections or other life-threatening complications.
  • History of other cancers, psychiatric disorders, or HIV infection.
  • Refusal to sign informed consent or unwillingness to comply with clinical follow-up or data use.
  • Investigator deems patient unsuitable for any other reason.

AI-Screening

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Your Study Journey

Screening

Duration - 2 to 4 weeks

Participants are screened for eligibility to participate in the trial.

Conditioning

Duration - 7 days

Participants receive a conditioning regimen with either Total Body Irradiation (TBI) or Total Marrow, Central Nervous System and Lymphoid Irradiation (TMLI) plus Cyclophosphamide before transplantation.

Multiple visits over 7 days before transplantation

Hematopoietic Stem Cell Transplantation

Duration - 1 day

Participants undergo matched sibling donor hematopoietic stem cell transplantation (MSD-HSCT).

1 visit (in-person) for transplantation

Post-transplant Follow-up

Duration - Up to 2 years

Participants are monitored for transplant-related outcomes including graft versus host disease and survival.

Regular follow-up visits for up to 2 years

Trial Site Locations

Total: 1 location

1

The First Affiliated Hospital of Zhengzhou University

Zhengzhou, Henan, China, 450001

Actively Recruiting

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Research Team

Z

Zhilei Bian, PhD.

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

RANDOMIZED

Model

PARALLEL

Primary Purpose

TREATMENT

Number of Arms

2

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