Actively Recruiting

Phase 2
Age: 18Years +
All Genders
NCT06397313

RVU120 in Patients With Intermediate or High-risk, Primary or Secondary Myelofibrosis

Led by Ryvu Therapeutics SA · Updated on 2025-09-23

230

Participants Needed

18

Research Sites

158 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

The objective of this clinical trial is to evaluate the efficacy (how well the drug works), safety, pharmacokinetics (PK), and pharmacodynamics (PD) of the study drug, RVU120, in treating adult patients with intermediate or high-risk, primary or secondary myelofibrosis. RVU120 will be given as a single agent or in combination with ruxolitinib.

CONDITIONS

Official Title

RVU120 in Patients With Intermediate or High-risk, Primary or Secondary Myelofibrosis

Who Can Participate

Age: 18Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Age 18 years or older
  • Diagnosis of primary or secondary myelofibrosis according to WHO criteria
  • Intermediate or high-risk myelofibrosis
  • Resistant, refractory, or suboptimal response to prior JAK inhibitor treatment or ineligible for JAK inhibitor treatment
  • Measurable splenomegaly with spleen palpable at least 5 cm below left costal margin or spleen volume ≥450 cm3 by MRI or CT
  • Active myelofibrosis symptoms with a symptom score of at least 5 on one symptom or 3 or greater on two symptoms
  • ECOG performance status of 0 to 2
  • Adequate hematologic function with absolute neutrophil count ≥1.0 × 10^9/L (without growth factor support)
  • Platelet count ≥50 × 10^9/L for Cohort 2 and Cohort 3 only
  • Adequate renal function with creatinine clearance ≥30 mL/min
  • Adequate liver function with AST and ALT ≤3 × upper limit of normal, ALP ≤2 × upper limit of normal (≤5 × for bone isozyme), and bilirubin <2 × upper limit normal or ≤3 × if due to Gilbert's disease
Not Eligible

You will not qualify if you...

  • Peripheral blood or bone marrow blast count ≥10%
  • Prior hematopoietic stem cell transplant
  • Participation in another investigational drug study within 4 weeks prior to Cycle 1 Day 1
  • Active second malignancy except treated basal or squamous cell carcinoma, in situ cervical cancer, Stage I cancer in remission ≥2 years, low-risk prostate cancer (Gleason <7, PSA <10 ng/mL), or other cancer disease-free ≥3 years
  • Known or suspected allergy to RVU120 or ruxolitinib
  • Gastrointestinal impairment or disease
  • Major surgery or significant injury within 28 days (vascular access or minor surgery allowed if healed)
  • Ongoing systemic infection requiring treatment (prophylactic allowed)
  • Significant cardiac dysfunction including recent myocardial infarction, advanced heart failure, uncontrolled dysrhythmias, poorly controlled angina, or left ventricular ejection fraction <40%
  • Use of certain medications or substances affecting CYP1A2 within 5 half-lives before Cycle 1 Day 1
  • History of ventricular arrhythmia or QTc ≥470 ms
  • Known active HIV infection
  • Current active liver disease
  • Pregnant or lactating females
  • Any other medical, psychiatric, or physical condition that may jeopardize safety or study objectives

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 18 locations

1

Policlinico Sant'Orsola-Malpighi

Bologna, Italy

Actively Recruiting

2

Azienda Socio Sanitaria Territoriale Degli Spedali Civili Di Brescia

Brescia, Italy

Actively Recruiting

3

Azienda Ospedaliero Universitaria Policlinico "G. Rodolico - San Marco"

Catania, Italy

Actively Recruiting

4

Istituto Romagnolo per lo Studio dei Tumori Dino Amadori IRST S.r.l.

Meldola, Italy

Actively Recruiting

5

Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico

Milan, Italy

Actively Recruiting

6

Wojewódzki Szpital Specjalistyczny w Białej Podlaskiej

Biała Podlaska, Poland

Actively Recruiting

7

Szpital Uniwersytecki nr 2 im. dr Jana Biziela

Bydgoszcz, Poland

Actively Recruiting

8

M2M Med. Sp. z o.o. Sp. j.

Chorzów, Poland

Actively Recruiting

9

Centrum Wsparcia Badań Klinicznych UCK Ośrodek Badań Klinicznych Wczesnych Faz

Gdansk, Poland

Actively Recruiting

10

Pratia Hematologia Sp. z o.o.

Katowice, Poland

Actively Recruiting

11

Świętokrzyskie Centrum Onkologii Samodzielny Publiczny Zakład Opieki Zdrowotnej

Kielce, Poland

Completed

12

Samodzielny Publiczny Zakład Opieki Zdrowotnej Szpital Uniwersytecki w Krakowie

Krakow, Poland

Actively Recruiting

13

Samodzielny Publiczny Szpital Kliniczny Nr 1 w Lublinie

Lublin, Poland

Actively Recruiting

14

Wojewódzki Szpital Zespolony im. L. Rydygiera w Toruniu

Torun, Poland

Actively Recruiting

15

Lux Med Onkologia Sp. z o.o.

Warsaw, Poland

Actively Recruiting

16

Wojskowy Instytut Medyczny Państwowy Instytut Badawczy

Warsaw, Poland

Actively Recruiting

17

Uniwersytecki Szpital Kliniczny im. Jana Mikulicza-Radeckiego we Wrocławiu

Wroclaw, Poland

Actively Recruiting

18

Szpital Uniwersytecki Imienia Karola Marcinkowskiego w Zielonej Gorze Sp. z o. o.

Zielona Góra, Poland

Completed

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Research Team

H

Head of Clinical Operations

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NON_RANDOMIZED

Model

PARALLEL

Primary Purpose

TREATMENT

Number of Arms

2

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