Actively Recruiting

Early Phase 1
Age: 5Years - 18Years
MALE
NCT06345898

Safety and Efficacy of a Single Subretinal Injection of JWK002 Gene Therapy in Subjects With X-linked Retinoschisis(XLRS)

Led by West China Hospital · Updated on 2025-02-07

12

Participants Needed

1

Research Sites

523 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

This trial is to evaluate the safety and efficacy of JWK002 treatment of X-linked retinoschisis(XLRS). This study will enroll subjects aged 5-18 years old to receive a sub-retinal injection of JWK002.

CONDITIONS

Official Title

Safety and Efficacy of a Single Subretinal Injection of JWK002 Gene Therapy in Subjects With X-linked Retinoschisis(XLRS)

Who Can Participate

Age: 5Years - 18Years
MALE

Eligibility Criteria

Eligible

You may qualify if you...

  • Fully understand the trial purpose and agree to participate by signing informed consent
  • Male, aged 5 to under 18 years at consent
  • Clinically diagnosed with XLRS confirmed by RS1 gene mutation without other ophthalmic genetic mutations
  • Best corrected visual acuity (BCVA) between 34 and 63 letters (Snellen 20/200 to 20/63) in the study eye
Not Eligible

You will not qualify if you...

  • Use of carbonic anhydrase inhibitors within 3 months
  • Other eye conditions causing vision loss or affecting subretinal injection
  • Lens, cornea, or refractive issues affecting retinal observation
  • Eye conditions impacting study endpoints
  • Internal eye surgery within past 6 months
  • AAV8 neutralizing antibody titer 1:1000 or higher
  • Previous gene or cell therapy
  • Fertile subjects unwilling to use contraception
  • Active infections or positive tests for hepatitis B, hepatitis C, syphilis, or HIV
  • Malignant tumors diagnosed within 5 years before screening
  • Current or past systemic immune system disease
  • Significant abnormal lab values including liver enzymes, bilirubin, creatinine, or clotting times
  • Severe or known allergies to study drugs or treatments
  • Other conditions deemed inappropriate by the investigator

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

1
2
3
+1

Trial Site Locations

Total: 1 location

1

West China Hospital

Chengdu, Sichuan, China, 610023

Actively Recruiting

Loading map...

Research Team

L

Licong Liang

CONTACT

K

Kaiqin She

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

SINGLE

Allocation

NON_RANDOMIZED

Model

SEQUENTIAL

Primary Purpose

TREATMENT

Number of Arms

2

Not the Right Trial for You?

Explore thousands of other clinical trials that might be a better match.
Sign up to get personalized trial recommendations delivered to your inbox.

Already have an account? Log in here

Safety and Efficacy of a Single Subretinal Injection of JWK002 Gene Therapy in Subjects With X-linked Retinoschisis(XLRS) | DecenTrialz