Actively Recruiting

Phase 4
Age: 12Years - 100Years
All Genders
ID04647227

Safety of SEVENFACT® for Treating Bleeding Events in Patients With Hemophilia A or B With Inhibitors

Led by American Thrombosis and Hemostasis Network · Updated on 2026-01-12

55

Participants Needed

21

Research Sites

26 weeks

Total Duration

On this page

Sponsors

A

American Thrombosis and Hemostasis Network

Lead Sponsor

L

LFB USA, Inc.

Collaborating Sponsor

AI-Summary

What this Trial Is About

Researchers are evaluating the safety of SEVENFACT®, a recombinant clotting factor, for treating bleeding episodes in people with Hemophilia A or B who have developed inhibitors. This Phase IV, open-label, multi-center study focuses on participants aged 12 years and older in the US. It includes those on long-term prophylactic treatments and those who are not, aiming to better understand SEVENFACT's safety in real-world use. Participants will receive SEVENFACT® doses guided by their physician during bleeding events. Each participant will be supplied with nine doses of 75 µg/kg each, aligning with the recommended dosing schedule. Dosing can be self-administered under medical guidance or given at a treatment facility. The study will continue for up to approximately four years, following participants from enrollment onward. During the study, participants will document bleeding events and medication use through a mobile app or paper diary. Researchers will monitor adverse events, including allergic reactions, and collect safety data from consent through three days after the last dose. The main measure is the number and percentage of safety events related to SEVENFACT®. Participants may have regular assessments and follow-ups throughout the study duration to ensure thorough safety evaluation.

CONDITIONS

Brief Title

SEVENFACT® for Bleeding Events in Hemophilia With Inhibitors

Who Can Participate

Age: 12Years - 100Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Diagnosis of Hemophilia A or B with inhibitors
  • Age 12 years or older
  • Able to understand and comply with the study protocol or have a legal guardian who can
  • Signed and understood informed consent/assent
  • Able to provide medical evidence of previous inhibitor levels
  • Willing and able to use the ATHN mobile app or paper diary to record bleeding events and medication use
Not Eligible

You will not qualify if you...

  • Additional bleeding disorders besides Hemophilia A or B
  • Known intolerance or allergy to SEVENFACT® or its ingredients
  • Allergy or hypersensitivity to rabbits or rabbit proteins
  • Receiving prophylactic treatment with a drug or biologic not FDA-approved for this use
  • Implantation of an investigational medical device within the last 6 months
  • Received an investigational drug within 30 days before baseline visit
  • Planned elective surgery during study participation
  • Life-threatening disease or other conditions that may pose hazard or interfere with the study (including history of non-responsiveness to bypassing products or thromboembolic disease)

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Your Study Journey

Screening

Duration - 2 to 4 weeks

Participants are screened for eligibility to participate in the trial.

1 visit (in-person)

Treatment

Duration - Up to approximately 4 years from enrollment

Participants receive SEVENFACT® to treat bleeding episodes. Dosing is administered either by the participant or at a treatment facility during bleeding events.

Visits occur as needed during bleeding episodes for treatment and monitoring

Follow-up

Duration - Up to 3 days after last dose of SEVENFACT® per bleeding episode

Participants are monitored for safety events including adverse events and treatment-emergent adverse events during and up to 3 days after the last dose of SEVENFACT®.

Monitoring visits as needed following treatment of bleeding episodes

Trial Site Locations

Total: 21 locations

1

Arizona Hemophilia and Thrombosis Center at Phoenix Children's Hospital

Phoenix, Arizona, United States, 85016

Completed

2

Arkansas Center for Bleeding Disorders

Little Rock, Arkansas, United States, 72202

Actively Recruiting

3

Orthopaedic Institute for Children

Los Angeles, California, United States, 90007

Actively Recruiting

4

University of California at Davis UC Davis Hemostasis and Thrombosis Center

Sacramento, California, United States, 95817

Actively Recruiting

5

Children's National Hemophilia Center

Washington D.C., District of Columbia, United States, 20010

Completed

6

Arnold Palmer Hospital for Children - The Haley Center for Children's Cancer and Blood Disorders

Orlando, Florida, United States, 32806

Completed

7

Hemophilia of Georgia Center for Bleeding and Clotting Disorders of Emory, Adult Division

Atlanta, Georgia, United States, 31404

Actively Recruiting

8

Willett Children's Hospital at Memorial University Medical Center

Savannah, Georgia, United States, 31404

Actively Recruiting

9

Massachusetts General Hospital Comprehensive Hemophilia and Thrombosis Treatment Center

Boston, Massachusetts, United States, 02114

Actively Recruiting

10

Children's Hospital of Michigan

Detroit, Michigan, United States, 48201

Actively Recruiting

11

Henry Ford Health System

Detroit, Michigan, United States, 48202

Actively Recruiting

12

MSU Center for Bleeding and Clotting Disorders

Lansing, Michigan, United States, 48912

Actively Recruiting

13

Center for Bleeding and Clotting Disorders, University of Minnesota

Minneapolis, Minnesota, United States, 55455

Not Yet Recruiting

14

Mayo Comprehensive Hemophilia Center

Rochester, Minnesota, United States, 55905

Completed

15

Kansas City Regional Hemophilia Center

Kansas City, Missouri, United States, 64108

Actively Recruiting

16

Northwell Health, Long Island Jewish

New Hyde Park, New York, United States, 11040

Actively Recruiting

17

Brody School of Medicine at East Carolina University

Greenville, North Carolina, United States, 27834

Not Yet Recruiting

18

University Hospitals Health System Cleveland

Cleveland, Ohio, United States, 44106

Actively Recruiting

19

Oklahoma Center for Bleeding and Clotting Disorders

Oklahoma City, Oklahoma, United States, 73104

Actively Recruiting

20

Vanderbilt University Medical Center

Nashville, Tennessee, United States, 37212

Actively Recruiting

21

Gulf States Hemophilia and Thrombophilia Center-University of Texas Health Science Center @Houston

Houston, Texas, United States, 77030

Actively Recruiting

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Research Team

C

Carol Fedor, ND, RN, CCRC

J

Jessica Callis

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NA

Model

SINGLE_GROUP

Primary Purpose

TREATMENT

Number of Arms

1

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