Actively Recruiting
Sirolimus in the Treatment of Refractory/Relapsed wAIHA
Led by Peking Union Medical College Hospital · Updated on 2025-08-08
22
Participants Needed
1
Research Sites
127 weeks
Total Duration
On this page
AI-Summary
What this Trial Is About
Autoimmune hemolytic anemia (AIHA) is a rare and heterogeneous disorder characterized by the destruction of red blood cells through warm or cold antibodies. Glucocorticoid (combined with rituximab) is the first-line treatment. However, the recurrence rate is very high and some patients may not respond to steroids. Second-line therapies include cyclosporine A (CsA), cyclophosphamide, rituximab, azathioprine, and even splenectomy. Our previous study of sirolimus in refractory/relapsed AIHA and ES found an effective rate of 80%. Therefore, the investigators plan to explore the efficacy and safety of sirolimus in the treatment of refractory/relapsed wAIHA.
CONDITIONS
Official Title
Sirolimus in the Treatment of Refractory/Relapsed wAIHA
Who Can Participate
Eligibility Criteria
You may qualify if you...
- Age 18 years or older
- Diagnosed with primary warm autoimmune hemolytic anemia or Evans syndrome (primary or secondary)
- No active systemic treatment indication for other diseases if secondary Evans syndrome
- No response to glucocorticoid therapy or relapse after treatment
- Baseline liver enzymes (ALT, AST) less than twice the normal value
- No active infection
- Not pregnant or breastfeeding
- Signed consent form
You will not qualify if you...
- Connective tissue disease or involvement of other organs
- Infection or bleeding not controlled by standard treatment
- Active HIV, HCV, or HBV infection, cirrhosis, or portal hypertension
- Uncontrolled progressing malignant tumors or lymphoma
- Cirrhosis or portal hypertension
- Pregnant or breastfeeding
AI-Screening
AI-Powered Screening
Complete this quick 3-step screening to check your eligibility
Trial Site Locations
Total: 1 location
1
Peking Union Medical College Hospital
Beijing, Beijing Municipality, China, 100730
Actively Recruiting
How is the study designed?
Study Type
INTERVENTIONAL
Masking
NONE
Allocation
NA
Model
SINGLE_GROUP
Primary Purpose
TREATMENT
Number of Arms
1
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