Actively Recruiting

Early Phase 1
Age: 18Years - 60Years
All Genders
NCT06719791

Sirolomus Adjuvant Treatment of Focal Refractory Epilepsy (SATFRE)

Led by Xuanwu Hospital, Beijing · Updated on 2024-12-31

15

Participants Needed

1

Research Sites

205 weeks

Total Duration

On this page

Sponsors

X

Xuanwu Hospital, Beijing

Lead Sponsor

P

Peking University

Collaborating Sponsor

AI-Summary

What this Trial Is About

The aim of this study is to evaluate the clinical efficacy of sirolimus as an adjunctive therapy for refractory epilepsy. The significance lies in addressing whether the mTOR inhibitor sirolimus has antiepileptic adjunctive effects for a broader range of patients with refractory epilepsy, with the hope of providing a new mTOR-targeted antiepileptic adjunctive medication regimen that is administered only during epileptic events and can be widely used for various types of refractory epilepsy.

CONDITIONS

Official Title

Sirolomus Adjuvant Treatment of Focal Refractory Epilepsy (SATFRE)

Who Can Participate

Age: 18Years - 60Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Age between 18 and 60 years
  • Diagnosed with focal seizures or focal seizures progressing to bilateral tonic-clonic seizures according to 2017 ILAE criteria
  • Diagnosed with refractory epilepsy, with ineffective treatment using at least two anti-epileptic drugs for 2 years
  • Stable doses of current anti-epileptic drugs for at least 12 weeks before enrollment and no drug interaction with sirolimus
  • Seizure duration of at least 1 minute with sensory impairment
  • At least 6 focal seizures within 12 weeks prior to enrollment
  • EEG or MRI/CT results within the past 2 years confirming focal epilepsy diagnosis
  • Use of vagus nerve stimulation or deep brain stimulation permitted if implanted at least 5 months ago and stable for 12 weeks before enrollment
  • Signed informed consent
Not Eligible

You will not qualify if you...

  • Diagnosed with generalized or hereditary epilepsy with ion channel gene mutations
  • Psychogenic non-epileptic seizures within the past 12 months
  • Treatable causes of epilepsy such as metabolic disorders, toxicity, infections, space occupying lesions, or identified genetic abnormalities
  • Patients with only non-motor focal seizures
  • Seizure clusters within the past 12 months
  • Tonic-clonic status epilepticus within the past 12 months
  • Major medical illnesses including cerebrovascular events within 6 months, progressive intracranial lesions
  • Severe uncontrolled diseases such as immunodeficiency, liver or kidney diseases, acute infections, or advanced tumors
  • Severe cardiovascular or peripheral vascular diseases including NYHA Class III-IV, malignant arrhythmias, significant ECG abnormalities, or recent myocardial infarction
  • Medical conditions or surgeries affecting drug absorption, distribution, or metabolism, or difficulty swallowing
  • Medical, mental health, cognitive, or intellectual conditions that increase risk or interfere with participation
  • Severe allergic reactions or hypersensitivity to sirolimus components
  • Laboratory abnormalities including ALT, AST, ALP greater than 2 times upper limit of normal, platelet count below 80 x10^9/L, neutrophil count below 1.8 x10^9/L, or creatinine clearance below 30 mL/min
  • Pregnancy, childbirth, or lactation
  • Alcohol abuse or drug misuse within 2 years prior to medication
  • Participation in another clinical study within 3 months

AI-Screening

AI-Powered Screening

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Trial Site Locations

Total: 1 location

1

Xuanwu Hospital

Beijing, China

Actively Recruiting

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Research Team

L

Liankun Ren, MD

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NA

Model

SINGLE_GROUP

Primary Purpose

TREATMENT

Number of Arms

1

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