Actively Recruiting

Phase 3
Age: 18Years +
All Genders
ID06960213

STOP-HAE: A Phase 3, Randomized, Double-Blind, Placebo-Controlled Study of siRNA Targeting of Prekallikrein With ADX-324 in Participants With Hereditary Angioedema

Led by ADARx Pharmaceuticals, Inc. · Updated on 2026-05-18

90

Participants Needed

51

Research Sites

26 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

Researchers are evaluating the effectiveness and safety of ADX-324 in adults with Type 1 or Type 2 hereditary angioedema (HAE). This Phase 3 study aims to assess not only how well ADX-324 prevents HAE attacks but also its safety, how the body processes the drug (pharmacokinetics), its effects on the body (pharmacodynamics), and impacts on participants' quality of life. The study is sponsored by ADARx Pharmaceuticals, Inc. Participants will be randomly assigned to receive one of two dose levels of ADX-324, a small interfering RNA (siRNA) duplex oligonucleotide drug, or a placebo (saline). The study uses a double-blind design, meaning neither participants nor researchers know who receives the active drug or placebo. The treatment period focuses on evaluating outcomes from Day 22 through Week 25. During the trial, participants will be monitored for the number and quality of HAE attacks, along with assessments of drug safety and effects on quality of life. Researchers will track pharmacokinetics and pharmacodynamics to understand how the drug behaves in the body. Participation involves regular visits and evaluations throughout the study period, which lasts until the end of 2027. The main measurement is the efficacy of ADX-324 in preventing HAE attacks during the treatment window.

CONDITIONS

Brief Title

STOP-HAE: A Phase 3 Study of ADX-324 in HAE

Who Can Participate

Age: 18Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Age 18 years or older at the time of signing informed consent
  • Documented diagnosis of Type 1 or Type 2 hereditary angioedema (HAE-1/HAE-2)
  • At least 1 investigator-confirmed HAE attack in the first 4 weeks of screening or at least 2 investigator-confirmed HAE attacks in 8 weeks of screening
  • Ability to use at least one acute therapy for HAE attacks, such as plasma-derived or recombinant C1-INH concentrate or BK2-receptor antagonist
Not Eligible

You will not qualify if you...

  • Diagnosis of other recurrent angioedema types, including acquired angioedema, HAE with normal C1-INH, idiopathic angioedema, or recurrent angioedema with urticaria
  • Any clinically significant kidney (renal) disease
  • Any clinically significant liver (hepatic) disease
  • Use of C1-INH agents within 2 weeks prior to screening
  • Use of Berotralstat within 3 weeks prior to screening
  • Use of Lanadelumab within 8 weeks prior to screening
  • Use of androgens within 12 weeks prior to screening
  • Prior treatment with any RNA/DNA-based therapy for HAE or intolerance to such therapies (excluding vaccines)

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

1
2
3
+1

Your Study Journey

Screening

Duration - 2 to 4 weeks

Participants are screened for eligibility to participate in the trial.

1 visit (in-person)

Treatment

Duration - From Day 1 to Week 25

Participants receive ADX-324 or placebo to evaluate the efficacy in preventing hereditary angioedema (HAE) attacks.

Weekly visits for up to 25 weeks

Trial Site Locations

Total: 51 locations

1

ADARx Clinical Site

Litchfield Park, Arizona, United States, 85340

Actively Recruiting

2

ADARx Clinical Site

Little Rock, Arkansas, United States, 72205

Actively Recruiting

3

ADARx Clinical Site

San Diego, California, United States, 92122

Actively Recruiting

4

ADARx Clinical Site

Walnut Creek, California, United States, 94598

Actively Recruiting

5

ADARx Clinical Site

Orlando, Florida, United States, 32807

Actively Recruiting

6

ADARx Clinical Site

Chevy Chase, Maryland, United States, 20815

Actively Recruiting

7

ADARx Clinical Site

Wheaton, Maryland, United States, 20902

Actively Recruiting

8

ADARx Clinical Site

Detroit, Michigan, United States, 48202

Actively Recruiting

9

ADARx Clinical Site

St Louis, Missouri, United States, 63141

Actively Recruiting

10

ADARx Clinical Site

Las Vegas, Nevada, United States, 89128

Actively Recruiting

11

ADARx Clinical Site

New York, New York, United States, 10029

Actively Recruiting

12

ADARx Clinical Site

Cincinnati, Ohio, United States, 45236

Actively Recruiting

13

ADARx Clinical Site

Columbus, Ohio, United States, 43235

Actively Recruiting

14

ADARx Clinical Site

Toledo, Ohio, United States, 43617

Actively Recruiting

15

ADARx Clinical Site

Hershey, Pennsylvania, United States, 17033

Actively Recruiting

16

ADARx Clinical Site

Capital Federal, Buenos Aires, Argentina, C1425BEN

Not Yet Recruiting

17

ADARx Clinical Site

Buenos Aires, Buenos Aires F.D., Argentina, C1035AAT

Actively Recruiting

18

ADARx Clinical Site

Adelaide, South Australia, Australia, 5000

Actively Recruiting

19

ADARx Clinical Site

Vienna, Austria, 1090

Actively Recruiting

20

ADARx Clinical Site

Edegem, Antwerpen, Belgium, 2650

Not Yet Recruiting

21

ADARx Clinical Site

Sofia, Bulgaria, 1000

Actively Recruiting

22

ADARx Clinical Site

Edmonton, Alberta, Canada, T6G 2R3

Not Yet Recruiting

23

ADARx Clinical Site

Ottawa, Ontario, Canada, K1H 1E4

Actively Recruiting

24

ADARx Clinical Site

Montreal, Quebec, Canada, H2W 1R7

Not Yet Recruiting

25

ADARx Clinical Site

Beijing, China, 100730

Actively Recruiting

26

ADARx Clinical Site

Harbin, China, 150001

Not Yet Recruiting

27

ADARx Clinical Site

Zhengzhou, China, 450003

Not Yet Recruiting

28

ADARx Clinical Site

Split, Croatia, 21000

Actively Recruiting

29

ADARx Clinical Site

Zagreb, Croatia, 10000

Actively Recruiting

30

ADARx Clinical Site

Hradec Králové, Czechia, 500 05

Actively Recruiting

31

ADARx Clinical Site

Prague, Czechia, 15000

Actively Recruiting

32

ADARx Clinical Site

Nice, Alpes-Maritimes, France, 06300

Not Yet Recruiting

33

ADARx Clinical Site

Tours, Indre-et-Loire, France, 37000

Actively Recruiting

34

ADARx Clinical Site

Montpellier, France, 34295

Not Yet Recruiting

35

ADARx Clinical Site

Paris, France, 75012

Actively Recruiting

36

ADARx Clinical Site

Tübingen, Baden-Wurttemberg, Germany, 72076

Actively Recruiting

37

ADARx Clinical Site

Hong Kong, Hong Kong, 111

Not Yet Recruiting

38

ADARx Clinical Site

Budapest, Hungary, 1088

Actively Recruiting

39

ADARx Clinical Site

Ramat Gan, Tel Aviv, Israel, 5262100

Not Yet Recruiting

40

ADARx Clinical Site

Ashkelon, Israel, 7830604

Not Yet Recruiting

41

ADARx Clinical Site

Tel Aviv, Israel, 64239

Not Yet Recruiting

42

ADARx Clinical Site

Krakow, Poland

Actively Recruiting

43

ADARx Clinical Site

Lodz, Poland, 92-213

Actively Recruiting

44

ADARx Clinical Site

Wroclaw, Poland, 50-556

Actively Recruiting

45

ADARx Clinical Site

Barcelona, Spain, 08907

Actively Recruiting

46

ADARx Clinical Site

Madrid, Spain, 28007

Actively Recruiting

47

ADARx Clinical Site

Taichung, Taiwan, 40705

Actively Recruiting

48

ADARx Clinical Site

Cambridge, United Kingdom, CB2 0QQ

Actively Recruiting

49

ADARx Clinical Site

Cardiff, United Kingdom, CF14 4YS

Actively Recruiting

50

ADARx Clinical Site

London, United Kingdom, E1 1BB

Actively Recruiting

51

ADARx Clinical Site

Southampton, United Kingdom, SO16 6YD

Actively Recruiting

Loading map...

Research Team

L

Lupe Gallegos

How is the study designed?

Study Type

INTERVENTIONAL

Masking

QUADRUPLE

Allocation

RANDOMIZED

Model

PARALLEL

Primary Purpose

TREATMENT

Number of Arms

3

Similar Trials

Hemorrhoidal Artery Embolization: Longitudinal Impact On Sym...

Internal Hemorrhoids

Actively Recruiting

1 location

Institutional Registries of Rare Diseases at Hospital Italia...

Rare Diseases

Actively Recruiting

1 location

Phase 3 Extension Study of siRNA Targeting Prekallikrein Wit...

Hereditary Angioedema (HAE)

Actively Recruiting

48 locations

Frequently Asked Questions

Have more questions? Get in touch with our team for quick support

Not the Right Trial for You?

Explore thousands of other clinical trials that might be a better match.
Sign up to get personalized trial recommendations delivered to your inbox.

Already have an account? Log in here