Actively Recruiting

Phase 1
Phase 2
Age: 18Years +
All Genders
NCT04657068

A Study of ART0380 for the Treatment of Advanced or Metastatic Solid Tumors

Led by Artios Pharma Ltd · Updated on 2026-03-18

442

Participants Needed

79

Research Sites

357 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

This clinical trial is evaluating a drug called ART0380 in participants with advanced or metastatic solid tumors. The main goals of this study are to: * Find the recommended dose of ART0380 that can be given safely to participants alone and in combination with gemcitabine or irinotecan * Learn more about the side effects of ART0380 alone and in combination with gemcitabine or irinotecan * Learn more about the effectiveness of ART0380 alone and in combination with gemcitabine or irinotecan

CONDITIONS

Official Title

A Study of ART0380 for the Treatment of Advanced or Metastatic Solid Tumors

Who Can Participate

Age: 18Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Signed informed consent
  • Discontinued all previous cancer treatments for at least 21 days or 5 half-lives and recovered from acute effects to CTCAE Grade 3
  • Palliative radiotherapy completed at least 1 week before study treatment
  • Prior PARP inhibitor treatment if BRCA mutation or HRD positive cancer, unless contraindicated
  • At least 1 radiologically evaluable lesion suitable for RECIST v1.1 or PCWG-3 evaluation
  • Acceptable blood, kidney, liver, and coagulation function
  • Available non-irradiated tumor tissue sample for analysis
  • Use of highly effective contraception plus barrier method during and after study (duration depends on treatment)
  • Estimated life expectancy of at least 12 weeks
  • Willing and reliable to participate for study duration and follow procedures
  • ECOG performance status 0-1
  • For Part A1: advanced/metastatic cancer refractory to or lacking standard therapies
  • For Part A2: advanced/metastatic cancer appropriate for gemcitabine treatment
  • For Part A3: advanced/metastatic cancer appropriate for irinotecan treatment; ability to eat high-fat meal if in food effect cohort
  • For Part B1: advanced/metastatic solid tumors with ATM gene alterations and measurable disease; prior irinotecan treatment allowed for combination arms
  • For Part B2: high grade serous ovarian, fallopian tube or primary peritoneal carcinoma; platinum-resistant disease; prior PARP inhibitor treatment unless contraindicated; measurable disease
  • For Part B3: persistent or recurrent endometrial cancer; prior taxane/platinum chemotherapy unless contraindicated; measurable disease
  • For Part B4: advanced or metastatic solid cancers with biological selection; prior PD-1/PDL-1 inhibitor if approved; measurable disease; ECOG 0-1
  • For Part B5: metastatic colorectal cancer with ATM alterations; prior chemotherapy lines as appropriate; measurable disease
  • For Part B6: metastatic or locally advanced pancreatic ductal adenocarcinoma or acinar cell carcinoma with ATM alterations; prior chemotherapy regimen and disease progression or intolerance; measurable disease; serum albumin 3g/dL within 7 days before first dose
Not Eligible

You will not qualify if you...

  • Pregnant or breastfeeding women or planning pregnancy during study or within 7 months after last treatment
  • Men planning to father a child during study or within 5 months after last treatment
  • Serious systemic disorders compromising study adherence including recent HIV/AIDS-related infections, hepatitis B or C, chronic tuberculosis, or prior malignancy not in remission
  • Ongoing interstitial lung disease or pneumonitis
  • Moderate or severe cardiovascular disease
  • Severe or clinically significant valvulopathy
  • Major clinically significant ECG abnormalities
  • Symptomatic or uncontrolled brain metastases, spinal cord compression, or leptomeningeal disease needing treatment
  • Received live vaccine within 30 days before study treatment
  • Any condition, therapy, or lab abnormality interfering with study participation or safety
  • Major surgery within 4 weeks or minor surgery within 1 week prior to study
  • Drainage of ascites, pleural effusion or pericardial fluid within 4 weeks before first dose
  • Significant bleeding disorder or Grade 3 bleeding in past 12 weeks
  • Concurrent participation in incompatible clinical trials
  • For Parts A3, B1, B5, B6 with irinotecan: clinical deterioration symptoms
  • Known homozygous or combined heterozygous UGT1A1 *6/*28 genotypes
  • Use of strong UGT1A1 inhibitors within 2 weeks before first dose
  • For Part A3 fed-fasted cohort: use of acid reducing agents within 1 week before first dose
  • For Part B6: neuroendocrine or adenosquamous carcinoma pancreatic cancer

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 79 locations

1

University of Alabama at Birmingham

Birmingham, Alabama, United States, 35294-3300

Actively Recruiting

2

Mayo Clinic (Arizona)

Scottsdale, Arizona, United States, 85259

Actively Recruiting

3

University of Arkansas - Winthrop P. Rockefeller Cancer Institute

Little Rock, Arkansas, United States, 72205

Actively Recruiting

4

USC Norris Comprehensive Cancer Center

Los Angeles, California, United States, 90033

Actively Recruiting

5

Sansum Clinic

Santa Barbara, California, United States, 93105

Actively Recruiting

6

Providence Medical Foundation

Santa Rosa, California, United States, 95403

Actively Recruiting

7

Rocky Mountain Cancer Center

Denver, Colorado, United States, 80218

Actively Recruiting

8

Sarah Cannon Research Institute at HealthONE

Denver, Colorado, United States, 80218

Actively Recruiting

9

Florida Cancer Specialists

Fort Myers, Florida, United States, 33901

Actively Recruiting

10

Mayo Clinic (Florida)

Jacksonville, Florida, United States, 32224

Actively Recruiting

11

Cancer Specialists of North Florida

Jacksonville, Florida, United States, 32256

Actively Recruiting

12

Florida Cancer Specialists

Orlando, Florida, United States, 32827

Completed

13

Florida Cancer Specialists

Sarasota, Florida, United States, 34232

Actively Recruiting

14

Florida Cancer Specialists

West Palm Beach, Florida, United States, 33401

Actively Recruiting

15

Hope and Healing Cancer Services

Hinsdale, Illinois, United States, 60521

Actively Recruiting

16

Community Health Network

Indianapolis, Indiana, United States, 46250

Actively Recruiting

17

Our Lady of the Lake

Baton Rouge, Louisiana, United States, 70808

Actively Recruiting

18

Maryland Oncology Hematology - Primary

Columbia, Maryland, United States, 21044

Actively Recruiting

19

Minnesota Oncology Hematology

Maple Grove, Minnesota, United States, 55369

Actively Recruiting

20

Mayo Clinic (Minnesota)

Rochester, Minnesota, United States, 55905

Actively Recruiting

21

Washington University

St Louis, Missouri, United States, 63110

Actively Recruiting

22

Hematology Oncology Associates of Central New York

East Syracuse, New York, United States, 13057

Actively Recruiting

23

Northwell Health Cancer Institute

Lake Success, New York, United States, 11042

Actively Recruiting

24

Oncology Hematology Care Primary

Cincinnati, Ohio, United States, 45242

Actively Recruiting

25

Taylor Cancer Research Center

Maumee, Ohio, United States, 43537

Actively Recruiting

26

Stephenson Cancer Center

Oklahoma City, Oklahoma, United States, 73104

Actively Recruiting

27

Oregon Health & Science University

Portland, Oregon, United States, 97239

Actively Recruiting

28

University of Pennsylvania / Abramson Cancer Center

Philadelphia, Pennsylvania, United States, 19104

Actively Recruiting

29

Thomas Jefferson University, Sidney Kimmel Cancer Center, Clinical Research Organization

Philadelphia, Pennsylvania, United States, 19107

Actively Recruiting

30

Tennessee Oncology, PLLC

Chattanooga, Tennessee, United States, 37404

Actively Recruiting

31

Baptist Cancer Center

Memphis, Tennessee, United States, 38120

Completed

32

SCRI Oncology Partners

Nashville, Tennessee, United States, 37203

Actively Recruiting

33

Texas Oncology - Central/South Texas

Austin, Texas, United States, 78705

Actively Recruiting

34

Mary Crowley Cancer Research

Dallas, Texas, United States, 75230

Actively Recruiting

35

Texas Oncology - Baylor Charles A. Sammons Cancer Center

Dallas, Texas, United States, 75246

Actively Recruiting

36

Texas Oncology - Northeast Texas

Flower Mound, Texas, United States, 75028

Actively Recruiting

37

Oncology Consultants

Houston, Texas, United States, 77030

Completed

38

Texas Oncology - San Antonio

San Antonio, Texas, United States, 78240

Actively Recruiting

39

Utah Cancer Specialists

Salt Lake City, Utah, United States, 84106

Actively Recruiting

40

Virginia Cancer Specialists

Fairfax, Virginia, United States, 22031

Actively Recruiting

41

Institut Gustave Roussy

Villejuif, Cedex, France, 94805

Actively Recruiting

42

Institut Bergonie

Bordeau, France, 33076

Actively Recruiting

43

Marseille University Hospital Timone

Marseille, France, 13005

Actively Recruiting

44

Saint-Louis Hospital

Paris, France, 75010

Actively Recruiting

45

Hospital de la Pitié-Salpêtrière

Paris, France, 75013

Actively Recruiting

46

Hospital General Universitario de Elche

Elche, Alicante, Spain, 03203

Actively Recruiting

47

H. Parc Tauli

Sabadell, Barcelona, Spain, 08208

Actively Recruiting

48

Next Oncology Barcelona, IOB

Barcelona, Catalonia, Spain, 08023

Actively Recruiting

49

Hospital Arnau de Vilanova

Lleida, Catalonia, Spain, 25198

Actively Recruiting

50

Hospital Universitario La Paz

Madrid, Madrid, Spain, 28046

Actively Recruiting

51

Next - Hospital Quironsalud Madrid

Pozuelo de Alarcón, Madrid, Spain, 28223

Actively Recruiting

52

Hospital Clínico Universitario Virgen de la Arrixaca

El Palmar, Murcia, Spain, 30120

Actively Recruiting

53

Clínica Universidad de Navarra

Madrid, Planta -2, Spain, 28027

Actively Recruiting

54

Hospital Clínico Universitario de Santiago (CHUS)

A Coruña, Spain, 00000

Actively Recruiting

55

Hospital Teresa Herrera (CHUAC)

A Coruña, Spain, 15006

Actively Recruiting

56

Institut Català d'Oncologia Badalona - Hospital Germans Trias i Pujol

Badalona, Spain, 08916

Actively Recruiting

57

Vall d'Hebron Institute of Oncology (VIHO)

Barcelona, Spain, 08035

Actively Recruiting

58

Hospital Clinic de Barcelona

Barcelona, Spain, 08036

Actively Recruiting

59

ICO Hospitalet

Barcelona, Spain, 08903

Actively Recruiting

60

Hospital Universitario Reina Sofia de Córdoba

Córdoba, Spain, 14004

Actively Recruiting

61

Hospital Universitari Doctor Josep Trueta- ICO de Girona

Girona, Spain, 17007

Actively Recruiting

62

Hospital General Universitario Gregorio Marañón

Madrid, Spain, 28007

Actively Recruiting

63

MD Anderson Cancer Center (Madrid

Madrid, Spain, 28033

Actively Recruiting

64

Hospital Clinico San Carlos

Madrid, Spain, 28040

Actively Recruiting

65

START Madrid Fundacion Jimenez Diaz

Madrid, Spain, 28040

Actively Recruiting

66

Hospital Universitario 12 de Octubre

Madrid, Spain, 28041

Actively Recruiting

67

START Madrid (Hospital San Chinarro)

Madrid, Spain, 28050

Actively Recruiting

68

Hospital Universitario Virgen de la Victoria

Málaga, Spain, 29010

Actively Recruiting

69

Hospital Universitario De Navarra

Pamplona, Spain, 31008

Actively Recruiting

70

START Rioja

Rioja, Spain, 26006

Actively Recruiting

71

Hospital Virgen Macarena

Seville, Spain, 41009

Actively Recruiting

72

Hospital Virgen del Rocío

Seville, Spain, 41013

Actively Recruiting

73

Instituto Valenciano de Oncología (IVO)

Valencia, Spain, 00000

Actively Recruiting

74

Incliva Biomedical Research Institute, University of Valencia

Valencia, Spain, 46010

Actively Recruiting

75

Hospital Universitario Miguel Servet

Zaragoza, Spain, 50009

Actively Recruiting

76

Beatson West of Scotland Cancer Centre

Glasgow, United Kingdom, G12 0YN

Actively Recruiting

77

Guy's and St Thomas' NHS Foundation Trust

London, United Kingdom, SE1 9RT

Actively Recruiting

78

Sarah Cannon Research Institute UK

London, United Kingdom, W1G 6AD

Actively Recruiting

79

The Christie NHS Foundation Trust - The Christie Clinic

Manchester, United Kingdom, M20 4BX

Actively Recruiting

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Research Team

S

Sarah Cannon Development Innovations

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NON_RANDOMIZED

Model

SEQUENTIAL

Primary Purpose

TREATMENT

Number of Arms

10

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