Actively Recruiting

Age: 18Years +
All Genders
ID07191704

Characterization of PFIC-Related Genes in Adults With Idiopathic Recurrent and Chronic Cholestasis in Spain

Led by Ipsen · Updated on 2026-05-28

150

Participants Needed

10

Research Sites

N/A

Total Duration

On this page

AI-Summary

What this Trial Is About

Progressive Familial Intrahepatic Cholestasis (PFIC) is a group of inherited conditions affecting bile flow in the liver, which can cause serious liver problems. This research aims to observe genetic changes related to PFIC in adults with unexplained recurrent or chronic cholestasis in Spain to improve diagnosis and help develop personalized treatments. The study is observational and involves multiple centers in Spain over a 10-month period. During the study, each adult participant will attend a single visit where health information will be collected and a blood sample will be taken for routine tests and genetic analysis. This genetic testing will help identify variants in PFIC-related genes linked to their liver condition. No experimental treatments or interventions are involved. Participants will provide medical history and undergo laboratory tests including liver function and blood analyses. Researchers will measure the percentage of participants with genetic variants related to PFIC and collect demographic and clinical data. The study focuses on gathering detailed information to better understand the genetic causes of cholestasis. Participation lasts only for the one study visit with no follow-up treatments or procedures.

CONDITIONS

Brief Title

A Study to Assess the Genetic Variations in Bile Flow Disorders: Linking Progressive Familial Intrahepatic Cholestasis (PFIC)-Related Genes to Symptoms in Adults With Recurrent Cholestasis in Spain

Who Can Participate

Age: 18Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Adult patients 18 years old or older
  • Written informed consent prior to data collection and study procedures
  • Unexplained recurrent and/or chronic cholestasis defined as elevated alkaline phosphatase (ALP) or Gamma-Glutamyl Transferase (GGT) above the upper limit of normal
  • Ability to provide a blood sample for genetic analysis
Not Eligible

You will not qualify if you...

  • Patients with clearly diagnosed causes of cholestasis such as Primary Biliary Cholangitis
  • Patients with Primary or Secondary Sclerosing Cholangitis
  • Patients with bile duct obstruction
  • Patients with other liver diseases including cholestasis secondary to hepatocellular injury, viral hepatitis (Hepatitis A, B, or C), toxic or drug-induced hepatitis, autoimmune hepatitis
  • Patients with intestinal failure or total parenteral nutrition
  • Patients with Wilson's disease, choledochal cyst, Caroli Syndrome, or thick bile due to haemolysis

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

1
2
3
+1

Your Study Journey

Screening

Duration - 2 to 4 weeks

Participants are screened for eligibility to participate in the trial.

1 visit (in-person)

Diagnostic Evaluation

Duration - At enrollment

Participants provide demographic data, medical history, and undergo laboratory analyses to characterize genetic variations and liver-related health status.

1 visit (in-person)

Long-term Monitoring

Duration - Up to study completion

Participants with unexplained recurrent or chronic cholestasis are observed for ongoing health status without active intervention.

Visits as needed per routine healthcare

Trial Site Locations

Total: 10 locations

1

H. Clinic (first CEIm)

Barcelona, Spain

Actively Recruiting

2

H. Vall Hebron

Barcelona, Spain

Actively Recruiting

3

H. Reina Sofía

Córdoba, Spain

Actively Recruiting

4

H. Dr. Negrín

Las Palmas, Spain

Actively Recruiting

5

H. Gregorio Marañón

Madrid, Spain

Actively Recruiting

6

Hospital Universitario La Paz

Madrid, Spain

Actively Recruiting

7

H. Virgen del Rocío

Seville, Spain

Actively Recruiting

8

H. La Fe

Valencia, Spain

Actively Recruiting

9

H. Río Hortega

Valladolid, Spain

Actively Recruiting

10

H. Miguel Servet

Zaragoza, Spain

Actively Recruiting

Loading map...

Research Team

I

Ipsen Clinical Study Enquiries

How is the study designed?

Study Type

OBSERVATIONAL

Masking

N/A

Allocation

N/A

Model

N/A

Primary Purpose

N/A

Number of Arms

0

Similar Trials

PEARL - Pediatric Evaluation and Registry for Liver Cholesta...

PFIC - Progressive Familial Intrahepatic Cholestasis

Actively Recruiting

13 locations

Frequently Asked Questions

Have more questions? Get in touch with our team for quick support

Not the Right Trial for You?

Explore thousands of other clinical trials that might be a better match.
Sign up to get personalized trial recommendations delivered to your inbox.

Already have an account? Log in here