Actively Recruiting

Phase 3
Age: 18Years +
All Genders
NCT07422480

A Study to Compare Elritercept With Epoetin Alfa to Treat Anemia in Adults With Very Low, Low, or Intermediate Risk Myelodysplastic Syndromes (MDS) Who Need Regular Blood Transfusions

Led by Takeda · Updated on 2026-03-09

300

Participants Needed

146

Research Sites

391 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

The main aim of this study is to assess how elritercept works in lowering the need for RBC (red blood cell) transfusions and how safe elritercept is when compared with epoetin alfa. Other aims are to learn if elritercept improves tiredness as reported by participants without needing RBC transfusion compared with epoetin alfa, the RBC transfusion burden and quality of life compared with epoetin alfa. The study also aims to find out the extent of the immune response to elritercept. The study will also check on the medical problems (safety) of elritercept.

CONDITIONS

Official Title

A Study to Compare Elritercept With Epoetin Alfa to Treat Anemia in Adults With Very Low, Low, or Intermediate Risk Myelodysplastic Syndromes (MDS) Who Need Regular Blood Transfusions

Who Can Participate

Age: 18Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Male or female aged 18 years or older at time of consent.
  • Able to understand and voluntarily sign informed consent.
  • Diagnosis of MDS per WHO 2016 with IPSS-R very low, low, or intermediate risk confirmed prior to randomization.
  • Bone marrow blast count less than 5% at screening.
  • Endogenous serum erythropoietin level below 500 U/L.
  • Requires 2 to 6 units of RBC transfusion every 8 weeks for at least 8 weeks before randomization.
  • Hemoglobin level less than or equal to 9.0 g/dL with anemia symptoms or less than 7 g/dL without symptoms at time of transfusion.
  • Hemoglobin less than 11.0 g/dL after last RBC transfusion before randomization.
  • Eastern Cooperative Oncology Group score of 0, 1, or 2.
Not Eligible

You will not qualify if you...

  • Prior treatment with epoetin alfa (with some exceptions), darbepoetin, certain growth factors, immunomodulatory drugs, hypomethylating agents, luspatercept, or immunosuppressive therapy within specified time frames before randomization.
  • History of hematopoietic cell transplant.
  • MDS associated with del(5q) cytogenetic abnormality, unclassifiable MDS, or secondary MDS.
  • Diagnosis of acute myeloid leukemia.
  • Anemia caused by other known conditions like thalassemia or vitamin deficiencies.
  • Clinically significant cardiovascular disease including severe heart failure, recent heart attack, or uncontrolled arrhythmia.
  • Ejection fraction less than 35%.
  • History of recent thromboembolic events.
  • Uncontrolled hypertension.
  • Prior malignancies except certain skin, cervical, breast, or prostate cancers if treated and disease-free for 3 years.
  • Active infections requiring recent antibiotic treatment.
  • Positive for HIV, active hepatitis B or C infections.
  • Body mass index 40 kg/m2 or higher.
  • Major surgery within 28 days before randomization.
  • Recent seizures or history of allergy to study drugs.
  • Laboratory abnormalities including low neutrophils or platelets, elevated liver enzymes, low kidney function, or low vitamin levels.
  • Participation in another interventional clinical trial.
  • Inability or unwillingness to comply with study requirements.
  • Childbearing potential without agreeing to use effective contraception.
  • Pregnancy or breastfeeding without agreeing to forego breastfeeding.
  • Additional country-specific restrictions for participants in France.

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 146 locations

1

Hematology-Oncology Medical Group of Orange County, Inc - Orange - 1010 W. La Veta Avenue

Orange, California, United States, 92868

Not Yet Recruiting

2

BRCR Medical Center Inc

Tamarac, Florida, United States, 33321

Actively Recruiting

3

Emory University

Atlanta, Georgia, United States, 30322

Not Yet Recruiting

4

Orchard Healthcare Research Inc. (OHR) - Skokie

Skokie, Illinois, United States, 60077

Actively Recruiting

5

Norton Cancer Institute

Louisville, Kentucky, United States, 40207

Not Yet Recruiting

6

American Oncology Partners P.A. MidAmerica Cancer Care

Kansas City, Missouri, United States, 64132

Not Yet Recruiting

7

Albert Einstein College - Montefiore

The Bronx, New York, United States, 10467

Not Yet Recruiting

8

Novant Health Care Institute

Winston-Salem, North Carolina, United States, 27106

Not Yet Recruiting

9

Cleveland clinic OH

Cleveland, Ohio, United States, 44195

Not Yet Recruiting

10

Fox Chase Cancer Center

Philadelphia, Pennsylvania, United States, 19111

Not Yet Recruiting

11

Tennessee Oncology, PLLC

Nashville, Tennessee, United States, 37203

Not Yet Recruiting

12

Vanderbilt University Medical Center

Nashville, Tennessee, United States, 37232

Not Yet Recruiting

13

World Research Link

Baytown, Texas, United States, 77521

Not Yet Recruiting

14

The Center for Cancer and Blood Disorders

Fort Worth, Texas, United States, 76104

Not Yet Recruiting

15

The University of Texas-MD Anderson Cancer Center - Leukemia Center

Houston, Texas, United States, 77030

Not Yet Recruiting

16

Huntsman Cancer Institute

Salt Lake City, Utah, United States, 84124

Not Yet Recruiting

17

Virginia Commonwealth University (VCU)-Medical Center - North Hospital

Richmond, Virginia, United States, 23298

Not Yet Recruiting

18

West Virginia University Cancer Institute

Wheeling, West Virginia, United States, 26003

Not Yet Recruiting

19

Instituto Medico de la Fundacion Estudios Clinicos

Rosario, Santa Fe Province, Argentina, 2000

Not Yet Recruiting

20

Swiss Medical Center - Barrio Parque

Buenos Aires, Argentina, 1425

Not Yet Recruiting

21

Sanatorio Allende S.A. - Nueva Cordoba

Córdoba, Argentina, 5000

Not Yet Recruiting

22

Hospital Privado de Cordoba

Córdoba, Argentina, X5000

Not Yet Recruiting

23

Mid North Coast Local Health District - Mid North Coast Cancer Institute (MNCCI) - Coffs Harbour

Coffs Harbour, New South Wales, Australia, 2450

Not Yet Recruiting

24

South Eastern Sydney Local Health District

Sydney, New South Wales, Australia, 2217

Not Yet Recruiting

25

Calvary Mater Newcastle

Waratah, New South Wales, Australia, 2282

Not Yet Recruiting

26

Royal Adelaide Hospital

Adelaide, South Australia, Australia, 5000

Not Yet Recruiting

27

Flinders Medical Centre

Bedford Park, South Australia, Australia, 5042

Not Yet Recruiting

28

Monash University-Monash Medical Centre (MMC) - Clayton

Clayton, Victoria, Australia, 3168

Not Yet Recruiting

29

Eastern Haematology & Oncology Group or Austin Hospital

Heidelberg, Victoria, Australia, 3084

Not Yet Recruiting

30

Alfred Hospital

Melbourne, Victoria, Australia, 3004

Not Yet Recruiting

31

Fiona Stanley Hospital

Murdoch, Western Australia, Australia, 6150

Not Yet Recruiting

32

Chu-Ucl Namur Site Godinne

Yvoir, Namur, Belgium, 5530

Not Yet Recruiting

33

UZ Leuven

Leuven, Vlaams-Brabant, Belgium, 3000

Not Yet Recruiting

34

AZ Delta (H.-Hartziekenhuis Roeselare-Menen vzw (HHRM)) - Campus Rumbeke

Roeselare, West Flanders, Belgium, 8800

Not Yet Recruiting

35

D'OR Institute for Research and Education

Salvador, Estado de Bahia, Brazil, 41253-190

Not Yet Recruiting

36

Santa Casa de Misericordia-Porto Alegre

Porto Alegre, Rio Grande do Sul, Brazil, 90020090

Not Yet Recruiting

37

Porto Alegre Clinical Hospital (HCPA)

Porto Alegre, Rio Grande do Sul, Brazil, 90035903

Not Yet Recruiting

38

Hospital Mae de Deus, Clinical Research Unit - Cancer Institute

Porto Alegre, Rio Grande do Sul, Brazil, 90110-270

Not Yet Recruiting

39

Centro de Hematologia e Oncologia (CHO)

Joinville, Santa Catarina, Brazil, 89201-260

Not Yet Recruiting

40

Hospital Amaral Carvalho (HAC)

Jaú, São Paulo, Brazil, 17210080

Not Yet Recruiting

41

Irmandade da Santa Casa da Misericordia de Santos (ISCMS)

Santos, São Paulo, Brazil, 11075-101

Not Yet Recruiting

42

Portuguese Charity of Sao Paulo, Clinical Hematology / Oncology Center

São Paulo, Brazil, 01321-001

Not Yet Recruiting

43

Hospital 9 de Julho (Rede Americas/DASA)

São Paulo, Brazil, 01409-000

Not Yet Recruiting

44

Dr. Pencho Georgiev - Outpatient Center for Individual Practice for Specialized Medical Care in Internal Medicine and Clinical Hematology (EOOD)

Plovdiv, Bulgaria, 4000

Not Yet Recruiting

45

Specialized Hospital for Active Treatment of Hematological Diseases, Sofia, Clinic of Hematology

Sofia, Bulgaria, 1756

Not Yet Recruiting

46

St. Paul's Hospital (SPH) - Vancouver

Vancouver, British Columbia, Canada, V6E 1M7

Not Yet Recruiting

47

London Health Sciences Centre (LHSC) - Victoria Hospital

London, Ontario, Canada, N6A 5W9

Not Yet Recruiting

48

Princess Margaret Cancer Centre

Toronto, Ontario, Canada, M5G 2M9

Not Yet Recruiting

49

Centre Hospitalier Universitaire Grenoble Alpes

La Tronche, Isere, France, 38700

Not Yet Recruiting

50

Poitiers University Hospital Center - Miletrie Site

Poitiers, Vienne, France, 86021

Not Yet Recruiting

51

Centre Hospitalier Universitaire (CHU) de Nice - Hopital L'Archet I - Hematologie Clinique

Nice, France, 06200

Not Yet Recruiting

52

Saint-Louis Hospital

Paris, France, 75010

Not Yet Recruiting

53

Gustave Roussy

Villejuif, France, 94805

Not Yet Recruiting

54

Universitatsklinikum Bayreuth, Med. Klinik IV

Bayreuth, Bavaria, Germany, 95445

Not Yet Recruiting

55

Gemeinschaftspraxis fuer Haematologie und Onkologie - Praxis Steinfurter Strasse

Münster, North Rhine-Westphalia, Germany, 48153

Not Yet Recruiting

56

University Hospital Halle (Saale), Department of Internal Medicine IV - Hematology and Oncology

Halle, Saxony-Anhalt, Germany, 06120

Not Yet Recruiting

57

Praxis am Volkspark

Berlin, Germany, 10715

Not Yet Recruiting

58

Charite Campus Benjamin Franklin

Berlin, Germany, 12200

Not Yet Recruiting

59

Laiko General Hospital

Athens, Central Athens, Greece, 11526

Not Yet Recruiting

60

National and Kapodistrian University of Athens (NKUA)-Laiko General Hospital

Goudi, Central Athens, Greece, 11527

Not Yet Recruiting

61

Democritus University of Thrace (DUTH) - University General Hospital of Alexandroupolis

Alexandroupoli, Evros, Greece, 68100

Not Yet Recruiting

62

General Hospital of Thessaloniki "Ippokratio"

Thessaloniki, Macedonia, Greece, 55133

Not Yet Recruiting

63

National and Kapodistrian University of Athens-University General Hospital Attikon

Athens, West Athens, Greece, 12462

Not Yet Recruiting

64

Faculty of Medicine, School of Health Sciences, University of Ioannina

Ioannina, Greece, 45500

Not Yet Recruiting

65

University of Debrecen Clinical Center, Clinic of Internal Medicine, Department of Hematology

Debrecen, Hajdú-Bihar, Hungary, 4032

Not Yet Recruiting

66

Szent Borbala Korhaz, Department of Internal Medicine and Haematology, Division of Hematology

Tatabánya, Komárom-Esztergom, Hungary, 2800

Not Yet Recruiting

67

AIMS, Kochi

Kochi, Kerala, India, 682041

Not Yet Recruiting

68

Sahyadri Hospitals, Pune

Pune, Maharashtra, India, 411004

Not Yet Recruiting

69

Christian Medical College

Vellore, Tamil Nadu, India, 632517

Not Yet Recruiting

70

Apollo Hospital Hyderabad

Hyderabad, Telangana, India, 500096

Not Yet Recruiting

71

Tata Medical Center, Kolkata

Kolkata, West Bengal, India, 700160

Not Yet Recruiting

72

Postgraduate Institute of Medical Education and Research (PGIMER), Chandigarh

Chandigarh, India, 160012

Not Yet Recruiting

73

Max SuperSpeciality Saket, Delhi

Delhi, India, 110017

Not Yet Recruiting

74

Cork University Hospital

Cork, Ireland, T12 DC4A

Not Yet Recruiting

75

Mater Misericordiae University Hospital

Dublin, Ireland, Dublin 7

Not Yet Recruiting

76

Azienda Ospedaliero Universitaria di Bologna - Policlinico S. Orsola-Malpighi - Istituto di Ematologia "Lorenzo e Ariosto Seragnoli"

Bologna, Italy, 40138

Not Yet Recruiting

77

Universita degli Studi di Firenze - Azienda Ospedaliero-Universitaria Careggi (AOUC)

Florence, Italy, 50141

Not Yet Recruiting

78

IRCCS Ospedale San Raffaele

Milan, Italy, 20132

Not Yet Recruiting

79

Ospedale Cardarelli

Naples, Italy, 80131

Not Yet Recruiting

80

Ospedale di Novara

Novara, Italy, 28100

Not Yet Recruiting

81

Universita degli Studi di Padova-Azienda Ospedaliera di Padova

Padova, Italy, 35128

Not Yet Recruiting

82

Polyclinic San Matteo, IRCCS, Department of Oncohematology, Operative Unit of Hematology

Pavia, Italy, 27100

Not Yet Recruiting

83

Universita Degli Studi di Roma "Tor Vergata"

Rome, Italy, 00133

Not Yet Recruiting

84

Policlinico Umberto I

Rome, Italy, 00161

Not Yet Recruiting

85

Gruppo Humanitas-Humanitas Research Hospital (Istituto Clinico Humanitas)

Rozzano, Italy, 20089

Not Yet Recruiting

86

Institute of Cancer Research and Treatment of Candiolo

Torino, Italy, 10060

Not Yet Recruiting

87

NHO Nagoya Medical Center

Naka-ku, Aichi-ken, Japan, 460-0001

Not Yet Recruiting

88

Gifu Municipal Hospital

Gifu, Gifu, Japan, 500-8323

Not Yet Recruiting

89

Chugoku Central Hospital

Fukuyama, Hiroshima, Japan, 720-0001

Not Yet Recruiting

90

Hyogo Prefectural Amagasaki General Medical Center

Amagasaki, Hyōgo, Japan, 660-8550

Not Yet Recruiting

91

Dokkyo Medical University Hospital

Kitakobayashi, Tochigi, Japan, 321-0293

Not Yet Recruiting

92

Fukushima Medical University Hospital

Fukushima, Tohoku, Japan, 960-1295

Not Yet Recruiting

93

Tokyo Metropolitan Cancer and Infectious diseases Center Komagome Hospital

Bunkyo-ku, Tokyo, Japan, 113-8677

Not Yet Recruiting

94

NTT Medical Center Tokyo

Shinagawa-ku, Tokyo, Japan, 141-8625

Not Yet Recruiting

95

Hospital of Lithuania University of Health Sciences Kaunas, Clinic of Oncology and Hematology

Kaunas, Lithuania, 50161

Not Yet Recruiting

96

Vilniaus Universiteto Ligonine Santaros Klinikos (VULSK) (Vilniaus Universiteto Ligonines Santariskiu Klinikos)

Vilnius, Lithuania, 08661

Not Yet Recruiting

97

Hospital Sultanah Aminah Johor Bahru (HSAJB)

Johor Bahru, Johor, Malaysia, 80100

Not Yet Recruiting

98

Hospital Sultanah Bahiyah (HSB) (Klinik Kesihatan Bandar Alor Setar/Hospital Alor Setar)

George Town, Kedah, Malaysia, 11450

Not Yet Recruiting

99

Universiti Malaya - Faculty of Medicine (FOM)

Kuala Lumpur, Kuala Lumpur, Malaysia, 59200

Not Yet Recruiting

100

Centro de Investigacion Clinica Chapultepec (CICC), S.A. de C.V

Morelia, Michoacán, Mexico, 58260

Not Yet Recruiting

101

Universidad Autonoma de Nuevo Leon-Hospital Universitario "Dr. Jose Eleuterio Gonzalez" - Servicio de Hematologia

Monterrey, Nuevo León, Mexico, 64460

Not Yet Recruiting

102

Oaxaca Site Management Organization S.C. - Oaxaca

Oaxaca City, Oaxaca, Mexico, 68000

Not Yet Recruiting

103

National Institute of Medical Sciences and Nutrition Salvado

México, Mexico, 14080

Not Yet Recruiting

104

Clinica Ruiz - Centro de Hematologia y Medicina Interna (CHMI)

Puebla City, Mexico, 72530

Not Yet Recruiting

105

Amsterdam UMC-Locatie VUMC (Vrije Universiteit Medisch Centrum)

Amsterdam, North Holland, Netherlands, 1081HV

Not Yet Recruiting

106

Sykehuset Vestfold HF

Tønsberg, Vestfold, Norway, 3116

Not Yet Recruiting

107

Helse Bergen HF

Bergen, Vest, Norway, 5021

Not Yet Recruiting

108

Oslo Universitetssykehus HF

Oslo, Norway, 0372

Not Yet Recruiting

109

Pratia Wroclaw

Wroclaw, Lower Silesian Voivodeship, Poland, 50-019

Not Yet Recruiting

110

Pratia MCM Krakow

Krakow, maAopolska, Poland, 50-727

Not Yet Recruiting

111

Warszawski Uniwersytet Medyczny (WUM) (Medical University of Warsaw)

Warsaw, Masovian Voivodeship, Poland, 02-172

Not Yet Recruiting

112

Pratia Onkologia Katowice

Katowice, Silesian Voivodeship, Poland, 40-519

Not Yet Recruiting

113

AidPort

Skorzewo, Wielkopolska, Poland, 60185

Not Yet Recruiting

114

Institutul Oncologic Prof. Dr. I. Chiricu

Cluj-Napoca, Cluj, Romania, 400124

Not Yet Recruiting

115

Seoul National University Bundang Hospital

Seongnam-si, Gyeonggi-do, South Korea, 13620

Not Yet Recruiting

116

Soon Chun Hyang University Hospital Seoul

Seoul, Yongsan-gu, South Korea, 04401

Not Yet Recruiting

117

Korea University Anam Hospital

Seoul, South Korea, 02841

Not Yet Recruiting

118

Seoul National University Hospital

Seoul, South Korea, 03080

Not Yet Recruiting

119

Samsung Medical Center

Seoul, South Korea, 06351

Not Yet Recruiting

120

The Catholic University of Korea, Seoul St. Mary's Hospital

Seoul, South Korea, 06591

Not Yet Recruiting

121

Institut Catala d'Oncologia (ICO) - Hospital Duran i Reynals Location

L'Hospitalet de Llobregat, Barcelona, Spain, 08908

Not Yet Recruiting

122

Hospital Universitario Virgen del Rocio (HUVR) - Instituto de Biomedicina de Sevilla (IBIS)

Seville, Seville, Spain, 41013

Not Yet Recruiting

123

Hospital Universitari Vall d'Hebron-Institut de Recerca (VHIR)

Barcelona, Spain, 08035

Not Yet Recruiting

124

University Hospital Ramon y Cajal

Madrid, Spain, 28034

Not Yet Recruiting

125

Hospital Universitario Virgen de la Victoria (HUVV)

Málaga, Spain, 29010

Not Yet Recruiting

126

Universidad de Salamanca - Hospital Universitario de Salamanca

Salamanca, Spain, 37007

Not Yet Recruiting

127

University and Polytechnic Hospital La Fe

Valencia, Spain, 46026

Not Yet Recruiting

128

Chang Bing Show Chwan Memorial Hospital

Changhua, Taiwan, 505029

Not Yet Recruiting

129

Kaohsiung Medical University Chung-Ho Memorial Hospital

Kaohsiung City, Taiwan, 807

Not Yet Recruiting

130

China Medical University Hospital

Taichung, Taiwan, 404

Not Yet Recruiting

131

National Cheng Kung University Hospital

Tainan, Taiwan, 704

Not Yet Recruiting

132

National Taiwan University Hospital - East Campus

Taipei, Taiwan, 100225

Not Yet Recruiting

133

Taipei Veterans General Hospital

Taipei, Taiwan, 112201

Not Yet Recruiting

134

Banphaeo General Hospital

Ban Phaeo, Samutsakorn, Thailand, 74120

Not Yet Recruiting

135

King Chulalongkorn Memorial Hospital

Bangkok, Thailand, 10330

Not Yet Recruiting

136

Maharaj Nakorn Chiangmai Hospital

Chiang Mai, Thailand, 50200

Not Yet Recruiting

137

Ondokuz Mayis University School of Medicine, Department of Hematology

Samsun, Atakum, Turkey (Türkiye), 55270

Not Yet Recruiting

138

Mersin Medicalpark Hospital

Mersin, Mezitli, Turkey (Türkiye), 33000

Not Yet Recruiting

139

Ankara Universitesi, TAp FakAltesi, Hematoloji BD

Ankara, Turkey (Türkiye), 06520

Not Yet Recruiting

140

Istanbul Florence Nightingale Hospital

Istanbul, Turkey (Türkiye), 34381

Not Yet Recruiting

141

Ege University Medical Faculty

Izmir, Turkey (Türkiye), 35100

Not Yet Recruiting

142

Pilgrim Hospital

Boston, Lincolnshire, United Kingdom, PE227BU

Not Yet Recruiting

143

Churchill Hospital

Oxford, OXON, United Kingdom, OX3 7LE

Not Yet Recruiting

144

Queen Elizabeth Hospital Birmingham

Birmingham, West Midlands, United Kingdom, B15 2TH

Not Yet Recruiting

145

King's College Hospital

London, United Kingdom, SE5 9RS

Not Yet Recruiting

146

The Christie NHS Foundation Trust

Manchester, United Kingdom, M20 4BX

Not Yet Recruiting

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Research Team

T

Takeda Contact

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

RANDOMIZED

Model

PARALLEL

Primary Purpose

TREATMENT

Number of Arms

2

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A Study to Compare Elritercept With Epoetin Alfa to Treat Anemia in Adults With Very Low, Low, or Intermediate Risk Myelodysplastic Syndromes (MDS) Who Need Regular Blood Transfusions | DecenTrialz