Actively Recruiting

Phase 2
Age: 18Years - 75Years
All Genders
NCT06304103

A Study of Efficacy and Safety of AND017 in Patients With Myelodysplastic Syndrome

Led by Kind Pharmaceuticals LLC · Updated on 2026-02-27

63

Participants Needed

1

Research Sites

111 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

This is a Phase 2, multicenter, randomized, open-lable, dose ranging study to evaluate the efficacy and safety of AND017 for the treatment of anemia due to lower risk Myelodysplastic syndromes (MDS) in patients subjects who are Red blood cell (RBC) non-transfusion dependent (NTD) and low transfusion burden (LTB).

CONDITIONS

Official Title

A Study of Efficacy and Safety of AND017 in Patients With Myelodysplastic Syndrome

Who Can Participate

Age: 18Years - 75Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Diagnosed with primary myelodysplastic syndrome with a very low, low, or intermediate risk PISS-R grading at least 12 weeks before first dose
  • Non-5q(del)-associated myelodysplastic syndrome
  • Two non-transfused hemoglobin measurements between 6.0 and 10.0 g/dL during screening, at least one week apart, with no more than 1.3 g/dL difference
  • Non-transfused or low transfusion burden defined as specified red blood cell transfusion limits in the 16 weeks before randomization
  • Baseline erythropoietin (EPO) level less than or equal to 500 mU/mL
  • Platelet count of at least 30,000/mm3 and absolute neutrophil count of at least 800/mm3
  • Adequate liver function with total bilirubin less than 2 times upper limit of normal (or less than 3 times for Gilbert's syndrome), AST less than 3 times ULN, and ALT less than 3 times ULN
Not Eligible

You will not qualify if you...

  • Diagnosis of secondary myelodysplastic syndrome or anemia from other causes
  • Significant myelofibrosis with fibrosis grade 2 or higher
  • Planned chemotherapy or whole brain/spinal cord radiotherapy during study
  • Previous diagnosis of high or very high risk MDS IPSS-R
  • Prior or planned hematopoietic stem cell transplant during study
  • Recent treatment with G-CSF, thrombopoietin or receptor agonists within 8 weeks before first dose
  • Treatment with specific drugs (antithymocyte globulin, azacitidine, decitabine, cyclosporine, thalidomide, lenalidomide) within 12 weeks before first dose
  • Active infection or inflammatory disease requiring systemic therapy
  • Retinal neovascularization requiring treatment
  • Inability to take oral medications or gastrointestinal conditions affecting absorption
  • Significant bleeding within 4 weeks before first dose or uncorrected bleeding risk
  • Uncontrolled hypertension
  • Comorbid heart failure of NYHA class III or higher
  • Significant or active liver disease at screening
  • Prior treatment with hypoxia-inducing factor-prolyl hydroxylase inhibitor within 8 weeks
  • Prior treatment with erythropoietic ESA within 8 weeks
  • Prior treatment with androgenic anabolic steroids or similar agents within 8 weeks
  • Prior treatment with iron chelators within 8 weeks

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 1 location

1

First Affiliated Hospital of Zhejiang University School of Medicine

Hangzhou, Zhejiang, China, 30003

Actively Recruiting

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Research Team

Y

Yusha Zhu, MD, PhD

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

RANDOMIZED

Model

SEQUENTIAL

Primary Purpose

TREATMENT

Number of Arms

3

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