In vivo generation of anti-BCMA CAR-T cells in relapsed or refractory multiple myeloma: a phase 1 study.
Ning An, Di Wang, Peiling Zhang...
https://pubmed.ncbi.nlm.nih.gov/41882404Actively Recruiting
Led by Chunrui Li · Updated on 2025-02-11
24
Participants Needed
1
Research Sites
N/A
Total Duration
C
Chunrui Li
Lead Sponsor
S
Shenzhen Pregene Biopharma Co., Ltd.
Collaborating Sponsor
This research aims to evaluate ESO-T01 injection for patients with relapsed or refractory multiple myeloma. This early-phase clinical study focuses on observing the safety, tolerability, preliminary efficacy, pharmacokinetics, and pharmacodynamics of ESO-T01, a third-generation lentiviral vector that targets T cells in vivo with a BCMA-directed CAR. The study is designed for patients who have had prior treatments but continue to experience disease progression. ESO-T01 is given through infusion after patients receive preventive medications acetaminophen and diphenhydramine. The study uses a dose-escalation design with four different dose levels labeled A, B, C, and D. Following infusion, participants will be monitored closely for two years to assess various outcomes. Participants will have multiple assessments including evaluation of dose-limiting toxicities, immune-related side effects like cytokine release syndrome and neurotoxicity up to 28 days post-infusion, and treatment-related adverse effects for two years. Researchers will also measure response rates, survival outcomes, and detailed pharmacokinetic parameters at scheduled intervals up to two years. Continuous monitoring will help understand the treatment's effects and safety profile over time.
CONDITIONS
A Study of ESO-T01 in Treating Relapsed/ Refractory Multiple Myeloma
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Complete this quick 3-step screening to check your eligibility
Duration - 2 to 4 weeks
Participants are screened for eligibility to participate in the trial.
1 visit (in-person)
Duration - 28 days
Participants receive a single infusion of ESO-T01 drug with prior prophylaxis medication and dose escalation through four dose groups.
1 infusion visit and multiple monitoring visits up to Day 28
Duration - Up to 2 years
Participants are followed for safety and efficacy assessments for up to 2 years after treatment.
Regular visits for assessments at Day 14, Day 28, Month 2, Month 3, Month 6, Month 9, Month 12, Month 18, and Month 24
Total: 1 location
1
Tongji Hospital, Tongji Medical College
Wuhan, Hubei, China, 430000
Actively Recruiting
C
Chunrui Li
Study Type
INTERVENTIONAL
Masking
NONE
Allocation
NA
Model
SINGLE_GROUP
Primary Purpose
TREATMENT
Number of Arms
1
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Ning An, Di Wang, Peiling Zhang...
https://pubmed.ncbi.nlm.nih.gov/41882404