Actively Recruiting

Phase 3
Age: 18Years - 74Years
All Genders
ID07144163

A Randomized, Double-Blind, Placebo-Controlled Study to Evaluate Safety and Efficacy of Atumelnant in Adults With Classic Congenital Adrenal Hyperplasia

Led by Crinetics Pharmaceuticals Inc. · Updated on 2026-06-04

150

Participants Needed

45

Research Sites

N/A

Total Duration

On this page

AI-Summary

What this Trial Is About

Researchers are evaluating the effects of atumelnant in adults with classic Congenital Adrenal Hyperplasia (CAH) due to 21-hydroxylase deficiency. This Phase 3, global, multicenter, randomized, double-blind, placebo-controlled study aims to assess the drug's efficacy, safety, pharmacokinetics, and pharmacodynamics in participants aged 18 to under 75 years who have been on stable glucocorticoid therapy for at least two months. Participants will be randomly assigned in a 2:1 ratio to receive either atumelnant 80 mg once daily or a matching placebo for 32 weeks. There is an option to increase the atumelnant dose to 120 mg daily at Week 20. Before treatment begins, a screening period of 3 to 6 weeks will determine eligibility. Approximately 150 participants may take part in this study. During the study, participants will be monitored for hormone levels related to CAH and glucocorticoid dosing, with primary outcomes measured at Week 32. Assessments include morning serum androstenedione levels and other hormone markers. Safety and adherence to study procedures will also be closely observed. The study period extends up to 32 weeks of treatment following screening, with detailed evaluations throughout.

CONDITIONS

Brief Title

A Study to Evaluate Atumelnant in Adults With Congenital Adrenal Hyperplasia

Who Can Participate

Age: 18Years - 74Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Male or female, aged 18 to under 75 years at consent
  • Willing and able to follow study procedures and treatment
  • Diagnosed with classic CAH due to 21-hydroxylase deficiency confirmed by investigator
  • Specific morning serum androstenedione (A4) levels and glucocorticoid dosing as defined
  • On stable glucocorticoid replacement therapy for at least 2 months before consent
  • If on mineralocorticoids, stable dose for at least 1 month without orthostatic hypotension and normal sodium and potassium levels
  • If on estrogen therapy, stable dose for at least 3 months before screening
Not Eligible

You will not qualify if you...

  • Diagnosis of any CAH form other than classic 21-hydroxylase deficiency
  • History of bilateral adrenalectomy, hypopituitarism, or other chronic glucocorticoid therapy
  • Significant medical conditions or abnormal labs unrelated to CAH as judged by investigator
  • Mental condition impairing understanding or compliance with study
  • History of cancer except treated non-melanoma skin or cervical carcinoma in situ
  • Pregnant or lactating women or those unwilling to use effective contraception; similarly for men
  • Known hypersensitivity to atumelnant or its ingredients
  • Increased risk of adrenal insufficiency as judged by investigator
  • Severe erythrocytosis as judged by investigator
  • Prior use of atumelnant before screening

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Your Study Journey

Screening

Duration - 3 to 6 weeks

Participants are screened for eligibility to participate in the trial.

1 visit (in-person)

Treatment

Duration - 32 weeks

Participants receive atumelnant or placebo tablets once daily to evaluate the safety and efficacy of atumelnant in adults with classic congenital adrenal hyperplasia.

Regular visits during treatment as per study protocol

Trial Site Locations

Total: 45 locations

1

Crinetics Study Site

Los Angeles, California, United States, 90027

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2

Crinetics Study Site

Atlanta, Georgia, United States, 30322

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3

Crinetics Study Site

Chicago, Illinois, United States, 60611

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4

Crinetics Study Site

Ann Arbor, Michigan, United States, 48109

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5

Crinetics Study Site

Minneapolis, Minnesota, United States, 55417

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6

Crinetics Study Site

Rochester, Minnesota, United States, 55905

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7

Crinetics Study Site

Pittsburgh, Pennsylvania, United States, 15213

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8

Crinetics Study Site

Dallas, Texas, United States, 75390

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9

Crinetics Study Site

Milwaukee, Wisconsin, United States, 53226

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10

Crinetics Study Site

Buenos Aires, Buenos Aires F.D., Argentina, 1405

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11

Crinetics Study Site

Buenos Aires, Buenos Aires F.D., Argentina, C1012AAR

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12

Crinetics Study Site

CABA, Buenos Aires F.D., Argentina, C1199ABB

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13

Crinetics Study Site

Córdoba, Córdoba Province, Argentina, X5000JRD

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14

Crinetics Study Site

Herston, Queensland, Australia, 4029

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15

Crinetics Study Site

Woolloongabba, Queensland, Australia, 4102

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16

Crinetics Study Site

Adelaide, South Australia, Australia, 5000

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17

Crinetics Study Site

Parkville, Victoria, Australia, 3050

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18

Crinetics Study Site

Nedlands, Western Australia, Australia, 6009

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19

Crinetics Study Site

Vienna, Austria, 1090

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20

Crinetics Study Site

Curitiba, Paraná, Brazil, 33172

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21

Crinetics Study Site

Rio de Janeiro, Rio de Janeiro, Brazil, 20231-092

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22

Crinetics Study Site

Rio de Janeiro, Rio de Janeiro, Brazil, 20551-030

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23

Crinetics Study Site

Botucatu, São Paulo, Brazil, 18618-686

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24

Crinetics Study Site

São Paulo, São Paulo, Brazil, 04024-002

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25

Crinetics Study Site

São Paulo, São Paulo, Brazil, 05403-000

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26

Crinetics Study Site

Angers, France, 49933

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27

Crinetics Study Site

Bron, France, 69500

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28

Crinetics Study Site

Nantes, France, 44093 Cedex 1

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29

Crinetics Study Site

Paris, France, 75013

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30

Crinetics Study Site

Pessac, France, 33604

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31

Crinetics Study Site

Vandœuvre-lès-Nancy, France, 54500

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32

Crinetics Study Site

Munich, Bavaria, Germany, 80336

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33

Crinetics Study Site

Würzburg, Germany, 97080

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34

Crinetics Study Site

Milan, Milano, Italy, 20149

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35

Crinetics Study Site

Rozzano, Milano, Italy, 20089

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36

Crinetics Study Site

Padova, Padova, Italy, 35128

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37

Crinetics Study Site

Palermo, Palermo, Italy, 90127

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38

Crinetics Study Site

Naples, Italy, 80131

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39

Crinetics Study Site

Roma, Italy, 00161

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40

Crinetics Study Site

Warsaw, Masovian Voivodeship, Poland, 00-189

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41

Crinetics Study Site

Lodz, Łódź Voivodeship, Poland, 93-338

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42

Crinetics Study Site

Gothenburg, Sweden, 413 46

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43

Crinetics Study Site

Stockholm, Sweden, 171 76

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44

Crinetics Study Site

London, United Kingdom, NW1 2PG

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45

Crinetics Study Site

Manchester, United Kingdom, M20 4BX

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Research Team

C

Crinetics Clinical Trials

How is the study designed?

Study Type

INTERVENTIONAL

Masking

TRIPLE

Allocation

RANDOMIZED

Model

PARALLEL

Primary Purpose

TREATMENT

Number of Arms

2

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