Actively Recruiting

Phase 2
Age: 18Years - 99Years
All Genders
ID06797518

A Multicenter, Single Arm, Open Label Biopsy Study to Evaluate Structural and Functional Changes in Kidneys of Adult Patients With IgA Nephropathy Receiving Iptacopan on Top of Supportive Care

Led by Novartis Pharmaceuticals · Updated on 2026-04-27

20

Participants Needed

18

Research Sites

N/A

Total Duration

On this page

AI-Summary

What this Trial Is About

This research aims to evaluate the impact of iptacopan treatment on the immune-related processes in adults with Immunoglobulin A Nephropathy (IgAN). The study focuses on changes in important clinical and molecular markers, including kidney tissue changes and kidney function indicators, over a 9-month period. It also examines complement activation and multiple biomarkers related to kidney damage and disease progression. Participants will undergo a screening period and a baseline visit, during which a kidney biopsy will be performed. Eligible adults with IgAN will receive iptacopan 200 mg twice daily orally for 9 months, alongside their usual stable doses of ACE inhibitors or angiotensin receptor blockers. At the end of the treatment period, a follow-up kidney biopsy will be done to assess changes in the kidney structure. Throughout the study, participants will be monitored via kidney biopsies, clinical assessments, and biomarker measurements. The main outcome is the reduction in complement C3c deposits in the kidney after 9 months. Secondary outcomes include changes in immune cell markers and immunoglobulin staining. Safety and adherence will be observed during the treatment period, with the total participation lasting about 9 months from baseline to study end.

CONDITIONS

Brief Title

Study to Evaluate the Impact of Iptacopan on Top of SOC on Biopsy Changes in Kidneys of Adult Patients With IgAN

Who Can Participate

Age: 18Years - 99Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Signed informed consent and ability to communicate and comply with study requirements
  • Male and female adults aged 18 years or older with biopsy-confirmed IgA nephropathy
  • Estimated glomerular filtration rate (eGFR) of 30 mL/min/1.73m2 or higher
  • Proteinuria with urine protein-to-creatinine ratio (UPCR) of 0.8 g/g or higher or 1 g/day or higher
  • Baseline kidney biopsy showing less than 50% tubulointerstitial fibrosis
  • On stable, maximally tolerated or approved doses of ACE inhibitors or angiotensin receptor blockers for approximately 90 days prior to baseline and throughout the study
  • Required vaccinations against Neisseria meningitidis and Streptococcus pneumoniae at least 2 weeks before treatment
  • Vaccination against Haemophilus influenzae if available, at least 2 weeks before treatment
Not Eligible

You will not qualify if you...

  • Secondary IgA nephropathy or IgA vasculitis Henoch-Scholein Purpura
  • Other kidney diseases diagnosed at baseline biopsy
  • Significant urinary obstruction or voiding difficulties
  • Use of homeopathic or herbal medications for IgAN progression
  • Acute kidney injury within 4 weeks prior to screening
  • Rapidly progressive glomerulonephritis or nephrotic syndrome
  • High blood pressure (systolic >140 mmHg or diastolic >90 mmHg) at screening
  • Recent use of immunosuppressive or immunomodulatory drugs within specified time frames
  • Use of other investigational drugs within 5 half-lives or 30 days before enrollment
  • Prior use of iptacopan or participation in iptacopan trials
  • History of any organ transplantation
  • Recurrent invasive infections by encapsulated organisms
  • Major concurrent severe medical conditions
  • Active infections or fever prior to study drug administration
  • Known HIV infection
  • Hypersensitivity to study drugs or similar compounds
  • Active liver disease or abnormal liver function tests
  • Recent history of malignancy within 5 years, except certain treated skin or cervical cancers
  • Pregnant or nursing women
  • Women of childbearing potential not using effective contraception during and shortly after treatment

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Your Study Journey

Screening

Duration - 2 to 4 weeks

Participants are screened for eligibility to participate in the trial.

Baseline Assessment and Biopsy

Duration - 1 day

Participants attend a baseline visit where a kidney biopsy is performed to assess initial structural and functional kidney status.

1 baseline visit (in-person)

Treatment

Duration - 9 months

Participants receive iptacopan 200 mg twice daily along with their standard supportive care for IgA nephropathy over a 9-month period.

End of Treatment Biopsy and Follow-up

Duration - 1 day

At the end of the 9-month treatment period, participants undergo a follow-up kidney biopsy to evaluate changes from baseline.

1 visit (in-person)

Trial Site Locations

Total: 18 locations

1

University of Alabama at Birmingham

Birmingham, Alabama, United States, 35294

Actively Recruiting

2

UCLA Medical Center

Los Angeles, California, United States, 90095

Actively Recruiting

3

Central Florida Kidney Specialists

Orlando, Florida, United States, 32806

Actively Recruiting

4

Georgia Nephrology Research Inst

Lawrenceville, Georgia, United States, 30046

Actively Recruiting

5

CaRe Research

Chubbuck, Idaho, United States, 83202

Actively Recruiting

6

DaVita Clinical Research

Las Vegas, Nevada, United States, 89146

Actively Recruiting

7

University Hospitals Cleveland Medical Center

Cleveland, Ohio, United States, 44106

Actively Recruiting

8

OSU Wexner Medical Center

Columbus, Ohio, United States, 43210

Actively Recruiting

9

Prolato Clinical Research Center

Houston, Texas, United States, 77054

Actively Recruiting

10

Novartis Investigative Site

CABA, Buenos Aires, Argentina, 1280

Actively Recruiting

11

Novartis Investigative Site

CABA, Buenos Aires, Argentina, 1425

Actively Recruiting

12

Novartis Investigative Site

Córdoba, Córdoba Province, Argentina, 5000

Actively Recruiting

13

Novartis Investigative Site

Ashdod, Israel, 7747629

Actively Recruiting

14

Novartis Investigative Site

Hadera, Israel, 3820302

Actively Recruiting

15

Novartis Investigative Site

Haifa, Israel, 3109601

Actively Recruiting

16

Novartis Investigative Site

Nahariya, Israel, 2210001

Actively Recruiting

17

Novartis Investigative Site

Kuala Lumpur, Selangor, Malaysia, 43000

Actively Recruiting

18

Novartis Investigative Site

Riyadh, Saudi Arabia, 11211

Actively Recruiting

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Research Team

N

Novartis Pharmaceuticals

N

Novartis Pharmaceuticals

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NA

Model

SINGLE_GROUP

Primary Purpose

TREATMENT

Number of Arms

1

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