Actively Recruiting

Phase 1
Age: 18Years +
All Genders
NCT05371964

A Study to Evaluate the Safety, Pharmacokinetics, Pharmacodynamics and Clinical Activity of Imetelstat in Combination With Ruxolitinib in Participants With Myelofibrosis

Led by Geron Corporation · Updated on 2026-01-06

36

Participants Needed

8

Research Sites

325 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

The purpose of the study is to identify the recommended Part 2 dose (R2PD) of imetelstat sodium in combination with ruxolitinib in participants with myelofibrosis (MF) in Part 1, and to evaluate the safety and preliminary clinical activity of the R2PD of imetelstat sodium in combination with ruxolitinib in participants with MF in Part 2.

CONDITIONS

Official Title

A Study to Evaluate the Safety, Pharmacokinetics, Pharmacodynamics and Clinical Activity of Imetelstat in Combination With Ruxolitinib in Participants With Myelofibrosis

Who Can Participate

Age: 18Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Diagnosis of primary myelofibrosis (PMF) by WHO criteria or post-essential thrombocythemia-MF or post-polycythemia vera by IWG-MRT criteria
  • DIPSS intermediate-1, intermediate-2, or high-risk myelofibrosis
  • Candidate for ruxolitinib treatment
  • Part 1 participants: On ruxolitinib at a stable dose for at least 12 weeks with 4 consecutive weeks before enrollment
  • Part 2 participants: Either have not been treated with a JAK inhibitor (Cohort A) or have been on stable ruxolitinib for at least 12 weeks prior (Cohort B)
  • Active myelofibrosis symptoms: Part 1 participants must have at least 2 symptoms with a score 61;1; Part 2 participants must have at least 2 symptoms with score 61;3 or a total score of at least 10
  • Ineligible for or unwilling to undergo stem cell transplant at study entry
  • Hematology and biochemical lab tests within protocol limits
  • ECOG performance status 0, 1, or 2
  • Follow protocol-defined contraceptive procedures
  • Women of childbearing potential must have a negative pregnancy test at screening
Not Eligible

You will not qualify if you...

  • Peripheral blood or bone marrow blast count 61;10%
  • Prior JAK inhibitor treatment (except dose-optimized participants before enrollment in Part 1 or Part 2 Cohort B)
  • Known allergies or intolerance to imetelstat, ruxolitinib, or excipients
  • Prior treatment with imetelstat
  • Major surgery within 28 days before enrollment
  • Use of investigational drugs, hydroxyurea, chemotherapy, immunomodulatory or immunosuppressive therapy, or high-dose corticosteroids within 14 days before enrollment (except dose-optimized ruxolitinib)
  • Prior hematopoietic stem cell transplant
  • Malignancy other than MF unless treated with curative intent and no active disease for at least 3 years or adequately treated skin or cervical cancer without evidence of disease
  • Clinically significant cardiovascular disease
  • Known HIV infection or uncontrolled active systemic infection requiring IV antibiotics
  • Active systemic hepatitis requiring treatment or acute/chronic liver disease unless related to MF; hepatitis virus carriers allowed

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 8 locations

1

City of Hope

Duarte, California, United States, 91010

Actively Recruiting

2

City of Hope

Irvine, California, United States, 92618

Actively Recruiting

3

University of Miami

Coral Gables, Florida, United States, 33146

Actively Recruiting

4

H. Lee Moffitt Cancer Center and Research Institute, Inc.

Tampa, Florida, United States, 33612

Actively Recruiting

5

Icahn School of Medicine at Mount Sinai

New York, New York, United States, 10029

Actively Recruiting

6

Texas Oncology

Denison, Texas, United States, 75020

Withdrawn

7

Texas Oncology

Tyler, Texas, United States, 75702

Withdrawn

8

Fred Hutchinson Cancer Center

Seattle, Washington, United States, 98109

Actively Recruiting

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Research Team

M

Michelle Mudge-Riley, DO

CONTACT

J

Judy Ho

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NA

Model

SEQUENTIAL

Primary Purpose

TREATMENT

Number of Arms

2

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