Actively Recruiting

Phase 1
Phase 2
Age: 18Years +
All Genders
NCT04581512

Study to Evaluate the Safety and Tolerability of EP0042

Led by Ellipses Pharma · Updated on 2025-10-14

70

Participants Needed

6

Research Sites

317 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

A research study looking at a new treatment for patients with advanced cancer, to investigate different doses of the experimental study drug, EP0042, in order to determine a dose, which is safe, well-tolerated and likely to be effective in treating AML (acute myeloid leukaemia).

CONDITIONS

Official Title

Study to Evaluate the Safety and Tolerability of EP0042

Who Can Participate

Age: 18Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Male or female patients aged 18 years or older with confirmed AML
  • Ability to provide written informed consent
  • Ability to swallow and retain oral medication
  • Life expectancy sufficient to complete at least one 28-day treatment cycle
  • Eastern Cooperative Oncology Group (ECOG) Performance Status of 0-2 at screening
  • Well-managed and stable medical conditions for at least 28 days before first study drug dose
  • Patients with relapsed or refractory AML, MDS, or CMML who failed or are not eligible for approved therapies
  • Patients with relapsed/refractory FLT3 WT AML
  • Previous exposure to venetoclax, hypomethylating agents, or FLT3 inhibitors allowed
  • Known mutation status at trial entry
  • Female patients must be non-child-bearing or agree to use effective contraception during and 6 months after treatment
  • Male patients must use double barrier contraception during and 6 months after treatment
Not Eligible

You will not qualify if you...

  • Symptomatic or untreated brain or leptomeningeal metastases requiring therapy
  • Acute promyelocytic leukemia (FAB:M3)
  • Anti-cancer therapy for the disease within 2 weeks before first study drug dose (up to 3 weeks if interaction risk)
  • Ongoing toxic effects of previous treatments not reduced to at least CTCAE Grade 1 (except alopecia or certain Grade 2 toxicities as per investigator)
  • Transplantation within last 90 days or active immunosuppressive therapy for graft versus host disease within 2 weeks
  • Creatinine clearance less than 50 mL/min
  • Liver function abnormalities: total bilirubin ≥1.5 times, ALT ≥3 times, AST ≥3 times upper limit of normal, or AST/ALT ≥5 times if leukemia involves liver

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 6 locations

1

Royal Perth Hospital

Perth, Western Australia, Australia, 6000

Actively Recruiting

2

Amsterdam UMC

Amsterdam, Amsterdam, Netherlands, 1081HV Amsterdam

Actively Recruiting

3

Erasmus MC

Rotterdam, Rotterdam, Netherlands, 3000 CA Rotterdam

Actively Recruiting

4

University College London Hospital

London, London, United Kingdom, W1T 7HA

Actively Recruiting

5

The Royal Marsden

London, UK, United Kingdom

Actively Recruiting

6

The Christie Hospital

Manchester, United Kingdom, M204BX

Actively Recruiting

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Research Team

C

Clinical Trials Team

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NON_RANDOMIZED

Model

SINGLE_GROUP

Primary Purpose

TREATMENT

Number of Arms

2

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