Actively Recruiting

Phase 3
Age: 0 - 17Years
All Genders
NCT05319353

A Study to Evaluate the Safety and Tolerability, Pharmacokinetics, and Antiviral Activity of Maribavir for the Treatment of Cytomegalovirus (CMV) Infection in Children and Adolescents Who Have Received a Hematopoietic Stem Cell Transplant (HSCT) or a Solid Organ Transplant (SOT)

Led by Takeda · Updated on 2025-07-17

80

Participants Needed

47

Research Sites

166 weeks

Total Duration

On this page

Sponsors

T

Takeda

Lead Sponsor

T

Takeda Development Center Americas, Inc.

Collaborating Sponsor

AI-Summary

What this Trial Is About

The main aim of this study is to find out the safety, tolerability and pharmacokinetics (PK) of maribavir for the treatment of CMV infection in children and teenagers after HSCT or SOT and to identify the optimal dose of maribavir using a 200 milligrams (mg) tablet formulation or powder for oral suspension. The participants will be treated with maribavir for 8 weeks. Participants need to visit their doctor during 12-week follow-up period.

CONDITIONS

Official Title

A Study to Evaluate the Safety and Tolerability, Pharmacokinetics, and Antiviral Activity of Maribavir for the Treatment of Cytomegalovirus (CMV) Infection in Children and Adolescents Who Have Received a Hematopoietic Stem Cell Transplant (HSCT) or a Solid Organ Transplant (SOT)

Who Can Participate

Age: 0 - 17Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Parent or legally authorized representative must provide informed consent and participant assent as appropriate.
  • Male or female child or adolescent under 18 years of age at consent.
  • For children under 6 years, gestational age at least 39 weeks and minimum weight of 5 kg.
  • Recipient of a functioning solid organ transplant or hematopoietic stem cell transplant.
  • Documented CMV infection with specific viral load thresholds in blood or plasma confirmed twice within 14 days before first dose.
  • Absolute neutrophil count ≥ 500/mm³.
  • Platelet count ≥ 15,000/mm³.
  • Hemoglobin ≥ 8 g/dL.
  • Estimated glomerular filtration rate ≥ 30 mL/min/1.73 m².
  • Female of nonchildbearing potential or negative pregnancy test if of childbearing potential.
  • Agree to contraceptive requirements during treatment and for 90 days after last dose if sexually active.
  • Life expectancy of at least 8 weeks.
  • Willing and able to comply with study procedures.
  • Confirmed negative HIV test within 3 months or during screening.
Not Eligible

You will not qualify if you...

  • CMV tissue invasive disease involving central nervous system or retina.
  • Uncontrolled infection other than CMV.
  • History of alcohol or drug abuse interfering with compliance.
  • Receiving or expected to require valganciclovir, ganciclovir, cidofovir, foscarnet, leflunomide, letermovir, or artesunate during treatment.
  • Known hypersensitivity to maribavir or its ingredients.
  • Severe vomiting, diarrhea, or gastrointestinal illness preventing oral medication.
  • Need for mechanical ventilation or vasopressors at baseline.
  • Pregnant or nursing.
  • Prior participation or withdrawal from this study.
  • Use of investigational agents or devices within 30 days before treatment.
  • Previous maribavir or CMV vaccine use.
  • Significant medical or surgical conditions affecting safety or study results.
  • Severe liver disease or elevated liver enzymes.
  • Positive HIV test.
  • Active malignancy except nonmelanoma skin cancer.
  • Undergoing treatment for hepatitis B or C.
  • Need for strong CYP3A inducer treatment.
  • Low body weight causing excessive blood volume needed for study tests.

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 47 locations

1

University of Nebraska Medical Center -985400 Nebraska Medical Center

Omaha, Nebraska, United States, 68114-4113

Actively Recruiting

2

Cincinnati Children's Hospital Medical Center - PIN

Cincinnati, Ohio, United States, 45229-3026

Actively Recruiting

3

Cook Children's Health Care System

Fort Worth, Texas, United States, 76104-2733

Actively Recruiting

4

University of Texas MD Anderson Cancer Center - 1515 Holcombe Blvd

Houston, Texas, United States, 77030-4000

Actively Recruiting

5

Sydney Children's Hospital

Randwick, New South Wales, Australia, 2031

Actively Recruiting

6

Queensland Children's Hospital

South Brisbane, Queensland, Australia, 4101

Actively Recruiting

7

Royal Children's Hospital Melbourne - PIN

Parkville, Victoria, Australia, 3052

Actively Recruiting

8

Perth Children's Hospital

Nedlands, Western Australia, Australia, 6009

Actively Recruiting

9

Hôpital Universitaire des Enfants Reine Fabiola (HUDERF)

Brussels, Brussels Capital, Belgium, 1020

Actively Recruiting

10

Cliniques Universitaires Saint-Luc

Woluwe-Saint-Lambert, Brussels Capital, Belgium, 1200

Actively Recruiting

11

UZ Gent

Ghent, Oost-Vlaanderen, Belgium, 9000

Actively Recruiting

12

Irmandade Da Santa Casa de Misericordia de Porto Alegre

Porto Alegre, Rio Grande do Sul, Brazil, 90020-090

Actively Recruiting

13

Hospital de Clinicas de Porto Alegre (HCPA) - PPDS

Porto Alegre, Rio Grande do Sul, Brazil, 90035-903

Actively Recruiting

14

Hospital das Clínicas da Faculdade de Medicina da Universidade de São Paulo

Porto Alegre, Rio Grande do Sul, Brazil, 90160-093

Actively Recruiting

15

Hospital Do Rim E Hipertensão

São Paulo, Brazil, 04038-002

Actively Recruiting

16

Children's Hospital Capital Institute of Pediatrics

Beijing, Beijing Municipality, China, 100020

Actively Recruiting

17

Beijing Children's Hospital, Capital Medical University - PIN

Beijing, Beijing Municipality, China, 100045

Actively Recruiting

18

Shanghai Children's Medical Center

Shanghai, Shanghai Municipality, China, 200127

Actively Recruiting

19

Institute of Hematology and Blood Diseases Hospital Chinese Academy of Medical Sciences - PPDS

Tianjin, Tianjin Municipality, China, 300020

Actively Recruiting

20

CHU de Rennes - Hôpital Pontchaillou

Rennes, Ille-et-Vilaine, France, 35200

Actively Recruiting

21

CHU de Grenoble Alpes - Hôpital Michallon

La Tronche, Isère, France, 38700

Actively Recruiting

22

CHRU Nantes

Nantes, Loire-Atlantique, France, 44000

Actively Recruiting

23

Hopital Necker

Paris, France, 75015

Actively Recruiting

24

Universitätsklinikum Würzburg

Würzburg, Bavaria, Germany, 97080

Actively Recruiting

25

Universitätsklinikum Münster

Münster, North Rhine-Westphalia, Germany, 48149

Actively Recruiting

26

Universitatsklinikum Jena - Am Klinikum 1-Erlanger Allee 101

Jena, Thuringia, Germany, 07745

Actively Recruiting

27

Universitätsklinikum Hamburg Eppendorf

Hamburg, Germany, 20246

Actively Recruiting

28

Medizinische Hochschule Hannover

Hanover, Germany, 30625

Actively Recruiting

29

The Chaim Sheba Medical Center - PPDS

Ramat Gan, Tel Aviv, Israel, 52394

Actively Recruiting

30

Tel Aviv Sourasky Medical Center Ichilov - PPDS

Tel Aviv, Tel Aviv, Israel, 64239

Actively Recruiting

31

Rambam Health Care Campus - PPDS

Haifa, Israel, 31096

Actively Recruiting

32

Hadassah Medical Center- Ein Kerem - PPDS

Petah Tikva, Israel, 4920235

Actively Recruiting

33

National Center for Child Health and Development

Nagoya, Aiti, Japan, 453-0046

Actively Recruiting

34

Saitama Children's Medical Center

Isehara-Shi, Kanagawa, Japan, 259-1143

Actively Recruiting

35

Shizuoka Children's Hospital

Aoi-ku, Shizuoka, Japan, 420-8660

Actively Recruiting

36

Hyogo Prefectural Kobe Children's Hospital

Chiba, Japan, 650-0047

Actively Recruiting

37

Osaka Women's and Children's Hospital

Izumi-Shi, Ôsaka, Japan, 594-1101

Actively Recruiting

38

Hospital Sant Joan de Deu - PIN

Espluges de Llobregat, Barcelona, Spain, 08950

Actively Recruiting

39

Hospital Universitario La Paz - PPDS

Horcajo de la Sierra, Madrid, Spain, 28755

Actively Recruiting

40

Hospital Regional Universitario de Malaga - Hospital Materno-Infantil

Málaga, Málaga, Spain, 29011

Actively Recruiting

41

Hospital Universitario Vall d´Hebron- PPDS

Barcelona, Spain, 08035

Actively Recruiting

42

Hospital Infantil Universitario Niño Jesus - PIN

Madrid, Spain, 28009

Actively Recruiting

43

King's College Hospital

London, Lambeth, United Kingdom, SE5 9RS

Actively Recruiting

44

Royal Manchester Children's Hospital - PIN

Manchester, Lancashire, United Kingdom, M13 9WL

Actively Recruiting

45

Nottingham University Hospitals NHS Trust

Nottingham, Nottinghamshire, United Kingdom, NG5 1PB

Actively Recruiting

46

Birmingham Women's and Children's NHS Foundation Trust

Birmingham, West Midlands, United Kingdom, B4 6NH

Actively Recruiting

47

Great Ormond Street Hospital

London, United Kingdom, WC1N 3JH

Actively Recruiting

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Research Team

T

Takeda Contact

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NON_RANDOMIZED

Model

SINGLE_GROUP

Primary Purpose

TREATMENT

Number of Arms

3

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A Study to Evaluate the Safety and Tolerability, Pharmacokinetics, and Antiviral Activity of Maribavir for the Treatment of Cytomegalovirus (CMV) Infection in Children and Adolescents Who Have Received a Hematopoietic Stem Cell Transplant (HSCT) or a Solid Organ Transplant (SOT) | DecenTrialz