Actively Recruiting

Phase 1
Phase 2
Age: 0 - 17Years
All Genders
NCT04774718

A Study Evaluating the Safety, Pharmacokinetics, and Efficacy of Alectinib in Pediatric Participants With ALK Fusion-Positive Solid or CNS Tumors

Led by Hoffmann-La Roche · Updated on 2026-05-05

42

Participants Needed

33

Research Sites

545 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

This study will evaluate the safety, pharmacokinetics, and efficacy of alectinib in children and adolescents with ALK fusion-positive solid or CNS tumors for whom prior treatment has proven to be ineffective or for whom there is no satisfactory standard treatment available.

CONDITIONS

Official Title

A Study Evaluating the Safety, Pharmacokinetics, and Efficacy of Alectinib in Pediatric Participants With ALK Fusion-Positive Solid or CNS Tumors

Who Can Participate

Age: 0 - 17Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Histologically confirmed CNS or solid tumors with documented ALK gene fusions
  • Disease status: relapsed, refractory, or no satisfactory standard treatment available
  • Measurable and evaluable disease by RECIST v1.1, RANO, or INRC criteria
  • Available tumor tissue for submission or willingness to undergo biopsy prior to enrollment
  • Lansky Performance Status 50% for participants under 16 years
  • Karnofsky Performance Status 50% for participants 16 years or older
  • Adequate bone marrow function within 28 days before starting study drug
  • Willingness and ability to complete clinical outcome assessments
  • For females of childbearing potential: agreement to remain abstinent or use contraception and not donate eggs
  • For males not surgically sterile: agreement to remain abstinent or use contraception and not donate sperm
Not Eligible

You will not qualify if you...

  • Prior use of ALK inhibitors
  • Diagnosis of Anaplastic Large Cell Lymphoma (ALCL)
  • Gastrointestinal disorders affecting oral medication absorption
  • History of organ transplant or stem cell infusions
  • Substance abuse within 12 months prior to screening
  • Familial or personal history of congenital bone disorders or osteopenia
  • Treatment with investigational therapy within 28 days before study drug
  • Liver or kidney disease as defined by protocol
  • Grade 3 toxicities from prior therapy interfering with alectinib
  • Use of other anti-cancer therapies during the study
  • Active hepatitis B or C, HIV-positive status, or AIDS-related illness
  • Any condition interfering with study conduct or drug absorption
  • Psychological, familial, sociological, or geographical conditions hampering study compliance
  • Planned surgery or procedure during the study unless permitted
  • Uncontrolled or high-risk infections
  • Pregnancy, breastfeeding, or intention to become pregnant during or within 3 months after study

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 33 locations

1

Lucile Packard Children's Hospital

Palo Alto, California, United States, 94304

Actively Recruiting

2

Johns Hopkins All Children's Hospital

St. Petersburg, Florida, United States, 33701

Actively Recruiting

3

University of Michigan, C.S. Mott Children's Hospital

Ann Arbor, Michigan, United States, 48109

Actively Recruiting

4

Children's Minnesota

Minneapolis, Minnesota, United States, 55404

Actively Recruiting

5

Memorial Sloan Kettering Cancer Center

New York, New York, United States, 10065

Active, Not Recruiting

6

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, United States, 45229

Actively Recruiting

7

St. Jude Children'S Research Hospital

Memphis, Tennessee, United States, 38105

Actively Recruiting

8

Sydney Children's Hospital

Randwick, New South Wales, Australia, 2031

Actively Recruiting

9

Royal Children's Hospital

Parkville, Victoria, Australia, 3052

Actively Recruiting

10

Hospital de Cancer de Barretos

Barretos, São Paulo, Brazil, 14784-400

Actively Recruiting

11

Graacc-Grupo de Apoio ao adolescente e a crianca com cancer

São Paulo, São Paulo, Brazil, 04038-030

Actively Recruiting

12

The Hospital for Sick Children

Toronto, Ontario, Canada, M5G 1X8

Actively Recruiting

13

CHU Sainte-Justine

Montreal, Quebec, Canada, H3T 1C5

Actively Recruiting

14

Beijing Children's Hospital, Capital Medical University

Beijing, China, 100045

Actively Recruiting

15

Xinhua Hospital Affiliated to Shanghai Jiao Tong University School of Medicine

Shanghai, China, 200092

Actively Recruiting

16

Rigshospitalet

København Ø, Denmark, 2100

Actively Recruiting

17

Centre Léon Bérard, Institut d?Hémato-Oncologie Pédiatrique

Lyon, France, 69373

Actively Recruiting

18

Hôpital de la Timone, Oncologie Pédiatrique

Marseille, France, 13385

Actively Recruiting

19

Institut Curie - Centre de Lutte Contre le Cancer (CLCC) de Paris

Paris, France, 75248

Actively Recruiting

20

Universitätsklinikum Heidelberg

Heidelberg, Germany, 69120

Withdrawn

21

Istituto Giannina Gaslini-Ospedale Pediatrico IRCCS

Genoa, Liguria, Italy, 16147

Active, Not Recruiting

22

Istituto Nazionale Tumori di Milano

Milan, Lombardy, Italy, 20133

Actively Recruiting

23

Dipartimento di Scienze Pediatriche Adolescenza

Turin, Piedmont, Italy, 10126

Actively Recruiting

24

Seoul National University Hospital

Seoul, South Korea, 03080

Actively Recruiting

25

Asan Medical Center

Seoul, South Korea, 05505

Actively Recruiting

26

Samsung Medical Center

Seoul, South Korea, 06351

Actively Recruiting

27

Hospital Infantil Universitario Nino Jesus

Madrid, Spain, 28009

Actively Recruiting

28

Hospital Universitario Virgen del Rocio

Seville, Spain, 41 41013

Actively Recruiting

29

Hospital Universitari i Politecnic La Fe

Valencia, Spain, 46026

Actively Recruiting

30

Great Ormond Street Hospital

London, United Kingdom, WC1N 3JH

Actively Recruiting

31

Royal Manchester Childrens Hospital

Manchester, United Kingdom, M13 9WL

Actively Recruiting

32

Great North Children's Hospital

Newcastle upon Tyne, United Kingdom, NE1 4LP

Actively Recruiting

33

Royal Marsden Hospital (Sutton)

Sutton, United Kingdom, SM2 5PT

Actively Recruiting

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Research Team

R

Reference Study ID Number: GO42286 https://forpatients.roche.com/

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NA

Model

SINGLE_GROUP

Primary Purpose

TREATMENT

Number of Arms

1

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