Actively Recruiting

Phase 3
Age: 18Years - 75Years
All Genders
ID06744920

A Randomized, Double-blind, Placebo-controlled Study to Evaluate the Efficacy, Safety, and Tolerability of Remibrutinib in Adults With Generalized Myasthenia Gravis, Followed by an Open-label Extension

Led by Novartis Pharmaceuticals · Updated on 2026-06-01

180

Participants Needed

129

Research Sites

261 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

Researchers are evaluating remibrutinib compared to a placebo in adults with Generalized Myasthenia Gravis (gMG) who are already receiving stable standard-of-care treatments. This is a Phase III, randomized, double-blind, placebo-controlled study aiming to assess the efficacy, safety, and tolerability of remibrutinib in this patient group. The trial includes about 180 participants and is sponsored by Novartis Pharmaceuticals. Participants will be randomly assigned to one of two groups: one group will receive oral remibrutinib tablets, while the other will receive matching placebo tablets. The study has two parts: a 6-month core period where treatment is blinded, followed by an extension phase lasting up to 60 months where all participants receive open-label remibrutinib. During the study, participants will undergo regular assessments including measurements of daily living activities affected by myasthenia gravis using the MG-ADL scale, muscle strength tests, quality of life questionnaires, and monitoring for adverse events. Researchers will track changes from baseline scores to evaluate treatment effects over time. Safety and tolerability will also be closely monitored throughout both study phases, with total participation lasting up to 66 months.

CONDITIONS

Brief Title

A Study to Investigate the Efficacy, Safety and Tolerability of Remibrutinib Versus Placebo in Adult Patients With Generalized Myasthenia Gravis

Who Can Participate

Age: 18Years - 75Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Adults aged 18 to 75 years
  • Diagnosed with Myasthenia Gravis Foundation of America (MGFA) Class II-IV generalized myasthenia gravis
  • Positive serologic test for AChR or MuSK antibodies, or seronegative for both at screening
  • Baseline MG-ADL score of 6 or higher with at least 50% due to non-ocular symptoms
  • On a stable dose of standard-of-care treatment as specified in the protocol
  • Able to safely swallow the study medication based on clinical judgement and swallowing tests
Not Eligible

You will not qualify if you...

  • Treatment with intravenous immunoglobulins or plasma exchange in the past month before baseline
  • Treatment with rituximab in the past 6 months before baseline
  • Treatment with eculizumab in the past 2 months before baseline
  • Treatment with ravulizumab or other complement inhibitors in the past 3 months before baseline
  • Treatment with efgartigimod or other anti-FcRn therapies in the past 3 months before baseline
  • Thymectomy in the past 6 months before baseline or planned during the trial
  • Women of childbearing potential not using highly effective contraception during dosing and for one week after stopping study treatment
  • Other protocol-defined criteria may apply

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Your Study Journey

Screening

Duration - 2 to 4 weeks

Participants are screened for eligibility to participate in the trial.

1 visit (in-person)

Treatment

Duration - 6 months

Participants receive either remibrutinib or placebo tablets orally during the 6-month double-blind core part of the study.

Visits scheduled throughout the 6-month treatment period

Treatment

Duration - Up to 60 months

Participants receive open-label remibrutinib tablets orally during the extension part of the study.

Visits scheduled throughout the extension treatment period

Trial Site Locations

Total: 129 locations

1

Neuromuscular Research Center

Phoenix, Arizona, United States, 85013

Actively Recruiting

2

Honor Health Research Institute

Scottsdale, Arizona, United States, 85258

Actively Recruiting

3

Fullerton Neuro and Headache Ctr

Fullerton, California, United States, 92835

Actively Recruiting

4

University Of Southern California

Los Angeles, California, United States, 90033

Actively Recruiting

5

Univ Cali Irvine ALS Neuromuscular

Orange, California, United States, 92868

Actively Recruiting

6

California Pacific Medical Center

Sacramento, California, United States, 94115

Actively Recruiting

7

Medstar Washington Hospital Center

Washington D.C., District of Columbia, United States, 20010-2975

Actively Recruiting

8

SFM Clinical Research LLC

Boca Raton, Florida, United States, 33487

Actively Recruiting

9

Homestead Assoc In Research Inc

Homestead, Florida, United States, 33033

Actively Recruiting

10

Neurology Associates PA

Maitland, Florida, United States, 32751

Actively Recruiting

11

AdventHealth

Orlando, Florida, United States, 32804

Actively Recruiting

12

Neurological Services of Orlando PA

Orlando, Florida, United States, 32806

Actively Recruiting

13

University of Chicago Medical Centr

Chicago, Illinois, United States, 60637

Actively Recruiting

14

Mid Atlantic Epilepsy and Sleep Ctr

Bethesda, Maryland, United States, 20817-1807

Actively Recruiting

15

Neuromuscular Diagnostic Center

Boston, Massachusetts, United States, 02114

Actively Recruiting

16

Michigan State University-Department of Neurology

East Lansing, Michigan, United States, 48824

Actively Recruiting

17

Dent Neurological Institute

Buffalo, New York, United States, 14209

Actively Recruiting

18

Univ of Cincinnati Medical Center

Cincinnati, Ohio, United States, 45219

Actively Recruiting

19

Cleveland Clinic Foundation

Cleveland, Ohio, United States, 44195

Actively Recruiting

20

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, United States, 15213

Actively Recruiting

21

Houston Methodist Hospital

Houston, Texas, United States, 77030

Actively Recruiting

22

UT Health Science Center

Houston, Texas, United States, 77030

Actively Recruiting

23

University of WA Division of Cardio

Seattle, Washington, United States, 98195

Actively Recruiting

24

Center for Neurological Disorders G

Greenfield, Wisconsin, United States, 53228-1321

Actively Recruiting

25

Novartis Investigative Site

Rosario, Santa Fe Province, Argentina, 2000

Actively Recruiting

26

Novartis Investigative Site

Caba, Argentina, C1055AAF

Actively Recruiting

27

Novartis Investigative Site

Capital Federal, Argentina, C1023AAB

Actively Recruiting

28

Novartis Investigative Site

San Miguel de Tucumán, Argentina, 4000

Actively Recruiting

29

Novartis Investigative Site

Kogarah, New South Wales, Australia, 2217

Actively Recruiting

30

Novartis Investigative Site

Fitzroy, Victoria, Australia, 3065

Actively Recruiting

31

Novartis Investigative Site

Southport, Australia, 4215

Actively Recruiting

32

Novartis Investigative Site

Leuven, Vlaams Brabant, Belgium, 3000

Actively Recruiting

33

Novartis Investigative Site

Salvador, Estado de Bahia, Brazil, 40050-410

Actively Recruiting

34

Novartis Investigative Site

Brasília, Federal District, Brazil, 70200-730

Actively Recruiting

35

Novartis Investigative Site

Caxias do Sul, Rio Grande do Sul, Brazil, 95070-560

Actively Recruiting

36

Novartis Investigative Site

Porto Alegre, Rio Grande do Sul, Brazil, 90035-903

Actively Recruiting

37

Novartis Investigative Site

Porto Alegre, Rio Grande do Sul, Brazil, 90480-110

Actively Recruiting

38

Novartis Investigative Site

São Paulo, Brazil, 05403-000

Actively Recruiting

39

Novartis Investigative Site

Edmonton, Alberta, Canada, T6G 2B7

Actively Recruiting

40

Novartis Investigative Site

London, Ontario, Canada, N6A 5W9

Actively Recruiting

41

Novartis Investigative Site

Ottawa, Ontario, Canada, K1H 8L6

Actively Recruiting

42

Novartis Investigative Site

Québec, Quebec, Canada, G1J 1Z4

Actively Recruiting

43

Novartis Investigative Site

Hefei, Anhui, China, 230001

Actively Recruiting

44

Novartis Investigative Site

Guangzhou, Guangdong, China, 510030

Actively Recruiting

45

Novartis Investigative Site

Shijiazhuang, Hebei, China, 50030

Actively Recruiting

46

Novartis Investigative Site

Zhengzhou, Henan, China, 450003

Actively Recruiting

47

Novartis Investigative Site

Wuhan, Hubei, China, 430030

Actively Recruiting

48

Novartis Investigative Site

Wuxi, Jiangsu, China, 214023

Actively Recruiting

49

Novartis Investigative Site

Changchun, Jilin, China, 130021

Actively Recruiting

50

Novartis Investigative Site

Beijing, China, 100034

Actively Recruiting

51

Novartis Investigative Site

Beijing, China, 100730

Actively Recruiting

52

Novartis Investigative Site

Qingdao, China, 266000

Actively Recruiting

53

Novartis Investigative Site

Shanghai, China, 200040

Actively Recruiting

54

Novartis Investigative Site

Shanghai, China, 200080

Actively Recruiting

55

Novartis Investigative Site

Bordeaux, France, 33076

Actively Recruiting

56

Novartis Investigative Site

Nice, France, 06001

Actively Recruiting

57

Novartis Investigative Site

Paris, France, 75013

Actively Recruiting

58

Novartis Investigative Site

Paris, France, 75940

Actively Recruiting

59

Novartis Investigative Site

Strasbourg, France, 67081

Actively Recruiting

60

Novartis Investigative Site

Toulouse, France, 31059

Actively Recruiting

61

Novartis Investigative Site

Kutaisi, Georgia, 4600

Actively Recruiting

62

Novartis Investigative Site

Tbilisi, Georgia, 0114

Actively Recruiting

63

Novartis Investigative Site

Tbilisi, Georgia, 0144

Actively Recruiting

64

Novartis Investigative Site

Frankfurt am Main, Hesse, Germany, 60590

Actively Recruiting

65

Novartis Investigative Site

Gummersbach, Germany, 51643

Actively Recruiting

66

Novartis Investigative Site

Hamburg, Germany, 20246

Actively Recruiting

67

Novartis Investigative Site

Münster, Germany, 48149

Actively Recruiting

68

Novartis Investigative Site

Gurugram, Haryana, India, 122011

Actively Recruiting

69

Novartis Investigative Site

Mangalore, Karnataka, India, 575002

Actively Recruiting

70

Novartis Investigative Site

Nashik, Maharashtra, India, 422005

Actively Recruiting

71

Novartis Investigative Site

New Delhi, National Capital Territory of Delhi, India, 110029

Actively Recruiting

72

Novartis Investigative Site

Ludhiana, Punjab, India, 141001

Actively Recruiting

73

Novartis Investigative Site

Vellore, Tamil Nadu, India, 632 004

Actively Recruiting

74

Novartis Investigative Site

Hyderabad, Telangana, India, 500082

Actively Recruiting

75

Novartis Investigative Site

Lucknow, Uttar Pradesh, India, 226007

Actively Recruiting

76

Novartis Investigative Site

Bergamo, BG, Italy, 24127

Actively Recruiting

77

Novartis Investigative Site

Orbassano, TO, Italy, 10043

Actively Recruiting

78

Novartis Investigative Site

Naples, Italy, 80131

Actively Recruiting

79

Novartis Investigative Site

Sapporo, Hokkaido, Japan, 0608543

Actively Recruiting

80

Novartis Investigative Site

Sapporo, Hokkaido, Japan, 0630005

Actively Recruiting

81

Novartis Investigative Site

Nishinomiya, Hyōgo, Japan, 6638501

Actively Recruiting

82

Novartis Investigative Site

Hanamaki, Iwate, Japan, 0250082

Actively Recruiting

83

Novartis Investigative Site

Sendai, Miyagi, Japan, 9838520

Actively Recruiting

84

Novartis Investigative Site

Suita, Osaka, Japan, 565-0871

Actively Recruiting

85

Novartis Investigative Site

Higashi-Matsuyama, Saitama, Japan, 355-0005

Actively Recruiting

86

Novartis Investigative Site

Koshigaya, Saitama, Japan, 343-8555

Actively Recruiting

87

Novartis Investigative Site

Shinjuku Ku, Tokyo, Japan, 160-0023

Actively Recruiting

88

Novartis Investigative Site

Chiba, Japan, 2608677

Actively Recruiting

89

Novartis Investigative Site

Fukuoka, Japan, 8128582

Actively Recruiting

90

Novartis Investigative Site

Fukushima, Japan, 9601295

Actively Recruiting

91

Novartis Investigative Site

Hiroshima, Japan, 7348551

Actively Recruiting

92

Novartis Investigative Site

Lublin, Lublin Voivodeship, Poland, 20-064

Actively Recruiting

93

Novartis Investigative Site

Lublin, Lublin Voivodeship, Poland, 20-080

Actively Recruiting

94

Novartis Investigative Site

Krakow, POL, Poland, 31-505

Actively Recruiting

95

Novartis Investigative Site

Bydgoszcz, Woj Kujawsko Pomorskie, Poland, 85-796

Actively Recruiting

96

Novartis Investigative Site

Bydgoszcz, Poland, 85-065

Actively Recruiting

97

Novartis Investigative Site

Katowice, Poland, 40-689

Actively Recruiting

98

Novartis Investigative Site

Lodz, Poland, 93-113

Actively Recruiting

99

Novartis Investigative Site

Lublin, Poland, 20-410

Actively Recruiting

100

Novartis Investigative Site

Lublin, Poland, 20-701

Actively Recruiting

101

Novartis Investigative Site

Poznan, Poland, 61-731

Actively Recruiting

102

Novartis Investigative Site

Rzeszów, Poland, 35-323

Actively Recruiting

103

Novartis Investigative Site

Skorzewo, Poland, 60-185

Actively Recruiting

104

Novartis Investigative Site

Szczecin, Poland, 71-252

Actively Recruiting

105

Novartis Investigative Site

Warsaw, Poland, 01-684

Actively Recruiting

106

Novartis Investigative Site

Warsaw, Poland, 02-172

Actively Recruiting

107

Novartis Investigative Site

Brasov, Romania, 500283

Actively Recruiting

108

Novartis Investigative Site

Bucharest, Romania, 040215

Actively Recruiting

109

Novartis Investigative Site

Sibiu, Romania, 550245

Actively Recruiting

110

Novartis Investigative Site

Belgrade, Serbia, 11000

Actively Recruiting

111

Novartis Investigative Site

Niš, Serbia, 18108

Actively Recruiting

112

Novartis Investigative Site

Novi Sad, Serbia, 21000

Actively Recruiting

113

Novartis Investigative Site

Busan, South Korea, 49241

Actively Recruiting

114

Novartis Investigative Site

Seoul, South Korea, 03080

Actively Recruiting

115

Novartis Investigative Site

Seoul, South Korea, 03722

Actively Recruiting

116

Novartis Investigative Site

Seoul, South Korea, 134 727

Actively Recruiting

117

Novartis Investigative Site

Santiago Compostela, A Coruna, Spain, 15706

Actively Recruiting

118

Novartis Investigative Site

L'Hospitalet de Llobregat, Barcelona, Spain, 08907

Actively Recruiting

119

Novartis Investigative Site

Barcelona, Spain, 08035

Actively Recruiting

120

Novartis Investigative Site

Lleida, Spain, 25198

Actively Recruiting

121

Novartis Investigative Site

Madrid, Spain, 28034

Actively Recruiting

122

Novartis Investigative Site

Málaga, Spain, 29010

Actively Recruiting

123

Novartis Investigative Site

Valencia, Spain, 46026

Actively Recruiting

124

Novartis Investigative Site

Kaohsiung City, Taiwan, 83301

Actively Recruiting

125

Novartis Investigative Site

Tainan, Taiwan, 704302

Actively Recruiting

126

Novartis Investigative Site

Taipei, Taiwan, 10002

Actively Recruiting

127

Novartis Investigative Site

Taipei, Taiwan, 111045

Actively Recruiting

128

Novartis Investigative Site

Taoyuan, Taiwan, 33305

Actively Recruiting

129

Novartis Investigative Site

London, United Kingdom, NW1 2BU

Actively Recruiting

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Research Team

N

Novartis Pharmaceuticals

N

Novartis Pharmaceuticals

How is the study designed?

Study Type

INTERVENTIONAL

Masking

DOUBLE

Allocation

RANDOMIZED

Model

PARALLEL

Primary Purpose

TREATMENT

Number of Arms

2

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