Actively Recruiting

Phase 1
Phase 2
Age: 18Years +
All Genders
NCT05308264

Study of R289 in Patients With Lower-risk Myelodysplastic Syndromes (LR MDS)

Led by Rigel Pharmaceuticals · Updated on 2025-10-21

86

Participants Needed

15

Research Sites

220 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

Phase 1b Study of R289 in Patients with Lower-risk Myelodysplastic Syndromes (LR MDS)

CONDITIONS

Official Title

Study of R289 in Patients With Lower-risk Myelodysplastic Syndromes (LR MDS)

Who Can Participate

Age: 18Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Patient must be 18 years of age or older at the time of signing the informed consent
  • Definitive diagnosis of MDS with very low, low, or intermediate-1 risk (IPSS-R 6 3.5) and 6 5% bone marrow myeloblasts
  • Relapsed, refractory/resistant, intolerant, or inadequate response to prior therapies like EPOs, luspatercept, or hypomethylating agents; patients with del (5q) must have failed lenalidomide
  • DOSE ESCALATION PHASE: symptomatic anemia with hemoglobin < 9.0 g/dL and no RBC transfusion within 16 weeks of registration or RBC transfusion dependent receiving 6 2 units PRBCs within 8 weeks in the previous 16 weeks for hemoglobin < 9.0 g/dL
  • DOSE EXPANSION PHASE: relapsed, refractory to or ineligible for ESAs with prior approved therapies for LR-MDS and RBC transfusion dependent
  • EXPLORATORY PHASE 1b COHORT: transfusion-dependent LR-MDS refractory or intolerant to, or ineligible for ESAs; no prior therapy for MDS; no del 5q cytogenetic abnormality; RBC transfusion dependent
  • Documented marrow iron stores or transferrin saturation > 20% or serum ferritin > 100 ng/100 mL
  • ECOG performance status 0 to 2 at screening
  • Adequate organ function: AST and ALT 6 1.5 times upper limit of normal, total bilirubin 6 1.5 times upper limit of normal; creatinine clearance > 60 mL/min or blood creatinine < 1.5 mg/dL
Not Eligible

You will not qualify if you...

  • Prior MDS treatment ended less than 4 weeks before study treatment
  • Anemia caused by iron, B12 or folate deficiencies, autoimmune or hereditary hemolysis, or gastrointestinal bleeding
  • MDS secondary to radiotherapy, chemotherapy, or immunotherapy for other diseases
  • Diagnosis of chronic myelomonocytic leukemia
  • History of uncontrolled seizures
  • Uncontrolled bacterial or viral infections including HIV, hepatitis B or C
  • History of other malignancies that could affect study compliance or results, except certain treated cancers in remission for 2 or more years
  • History or active significant disorders affecting heart, lungs, gastrointestinal, kidney, liver, nervous system, psychiatric, musculoskeletal, genitourinary, skin, or other systems that could affect study or drug metabolism
  • Prior autologous or allogeneic stem cell transplantation
  • Significant prolongation of QT/QTc interval or risk factors for Torsades de Pointes
  • Receiving concurrent chemotherapy, radiotherapy, or immunotherapy within 2 weeks of study treatment or unresolved toxicity from prior treatment
  • Use of medications that prolong QT/QTc interval or are strong CYP3A or CYP2B6 inhibitors or inducers during study treatment

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

1
2
3
+1

Trial Site Locations

Total: 15 locations

1

University of California, Los Angeles

Los Angeles, California, United States, 90095

Actively Recruiting

2

University of California, Irvine

Orange, California, United States, 92868

Actively Recruiting

3

Stanford Cancer Institute

Palo Alto, California, United States, 94304

Not Yet Recruiting

4

University of Miami

Miami, Florida, United States, 33136

Actively Recruiting

5

Mount Sinai Medical Center

Miami Beach, Florida, United States, 33140

Withdrawn

6

WashU Medicine

St Louis, Missouri, United States, 63110

Not Yet Recruiting

7

Oncology Clinical Research Referral Office

Hackensack, New Jersey, United States, 07601

Actively Recruiting

8

Rutgers Cancer Institute of New Jersey

New Brunswick, New Jersey, United States, 09083

Withdrawn

9

Ichan School of Medicine at Mount Sinai

New York, New York, United States, 10029

Actively Recruiting

10

Duke Cancer Institute

Durham, North Carolina, United States, 27705

Not Yet Recruiting

11

Cleveland Clinic

Cleveland, Ohio, United States, 44195

Actively Recruiting

12

The Ohio State University Comprehensive Cancer Center

Columbus, Ohio, United States, 43210

Not Yet Recruiting

13

University of Texas, Southwestern

Dallas, Texas, United States, 75390

Actively Recruiting

14

MD Anderson Cancer Center

Houston, Texas, United States, 77030

Actively Recruiting

15

Intermountain Healthcare

Salt Lake City, Utah, United States, 84009

Actively Recruiting

Loading map...

Research Team

S

Strait Hicklin

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NA

Model

SEQUENTIAL

Primary Purpose

TREATMENT

Number of Arms

1

Not the Right Trial for You?

Explore thousands of other clinical trials that might be a better match.
Sign up to get personalized trial recommendations delivered to your inbox.

Already have an account? Log in here