Actively Recruiting

Phase 2
Age: 1Year - 17Years
All Genders
NCT05003986

Study of Sparsentan Treatment in Pediatrics With Proteinuric Glomerular Diseases

Led by Travere Therapeutics, Inc. · Updated on 2026-05-12

67

Participants Needed

47

Research Sites

295 weeks

Total Duration

On this page

AI-Summary

What this Trial Is About

To evaluate the safety, efficacy and tolerability of sparsentan oral suspension and tablets, and assess changes in proteinuria after once-daily dosing over 108 weeks.

CONDITIONS

Official Title

Study of Sparsentan Treatment in Pediatrics With Proteinuric Glomerular Diseases

Who Can Participate

Age: 1Year - 17Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • The child or parent/legal guardian is willing and able to provide signed informed consent/assent as required before screening.
  • The child has an estimated glomerular filtration rate (eGFR) of 30 mL/min/1.73 m2 or higher at screening.
  • The child's mean seated blood pressure is between the 5th and 95th percentile for their sex and height.
  • Population 1: Child is aged 1 to under 18 years with UP/C of 1.5 g/g or higher and has kidney biopsy-proven FSGS or MCD or a documented genetic mutation related to these diseases.
  • Population 2: Child is aged 2 to under 18 years with UP/C of 0.6 g/g or higher and has kidney biopsy-confirmed IgAN, IgAV, or AS, or genetic confirmation of Alport Syndrome.
  • Population 3: Child is aged 8 to under 18 years with UP/C of 1.0 g/g or higher, kidney biopsy-confirmed IgAN, weighs 40 kg or more, and has been on ACEI and/or ARB therapy for at least 12 weeks before screening.
Not Eligible

You will not qualify if you...

  • The child weighs less than 7.3 kg at screening.
  • FSGS or MCD caused by viral infections, drug toxicities, or malignancies.
  • IgA deposits not related to primary IgAN or IgAV (such as those caused by lupus or liver disease).
  • Acute onset or relapse of glomerular disease requiring new immunosuppressive treatment within 6 months before screening.
  • Unstable use of chronic immunosuppressive medications including systemic steroids within 1 month before screening.
  • Use of prohibited medications as defined in the study protocol.
  • History of organ transplantation except corneal transplants.
  • History of moderate to severe heart failure or related hospitalizations.
  • Significant cardiac valvular or congenital vascular disease.
  • Jaundice, hepatitis, hepatobiliary disease, or liver enzyme levels more than twice the upper normal limit.
  • History of malignancy within the past 2 years.
  • Low hematocrit (<27%) or hemoglobin (<9 g/dL) at screening.
  • High potassium levels (>5.5 mEq/L) at screening.
  • Any clinically significant abnormal laboratory results.
  • Allergy or hypersensitivity to sparsentan or its ingredients.
  • Pregnancy, breastfeeding, or unwillingness to use reliable contraception if of childbearing potential.
  • Participation in another investigational drug study within 28 days before screening.
  • Prior exposure to sparsentan.
  • Inability to comply with study requirements or, for Population 3, inability to swallow tablets whole.

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

1
2
3
+1

Trial Site Locations

Total: 47 locations

1

Cedars-Sinai Medical Center

Los Angeles, California, United States, 90048

Actively Recruiting

2

Nemours Children's Hospital

Wilmington, Delaware, United States, 19803

Actively Recruiting

3

University of Miami, Leonard M. Miller School of Medicine

Miami, Florida, United States, 33136

Actively Recruiting

4

Nicklaus Children's Hospital

Miami, Florida, United States, 33155

Actively Recruiting

5

University of Iowa, Stead Family Children's Hospital

Iowa City, Iowa, United States, 52242

Withdrawn

6

Floating Hospital for Children at Tufts Medical Center

Boston, Massachusetts, United States, 02111

Withdrawn

7

C.S. Mott Children's Hospital

Ann Arbor, Michigan, United States, 48109-5008

Actively Recruiting

8

University of Minnesota, Masonic Children's Hospital

Minneapolis, Minnesota, United States, 55454

Actively Recruiting

9

Children's Mercy Hospitals and Clinics

Kansas City, Missouri, United States, 64108

Actively Recruiting

10

Hackensack University Medical Center

Hackensack, New Jersey, United States, 07601

Actively Recruiting

11

Jersey Shore University Medical Center

Neptune City, New Jersey, United States, 07753

Actively Recruiting

12

Cohen Children's Medical Center

New Hyde Park, New York, United States, 11042

Actively Recruiting

13

Fink Children's Ambulatory Care Center

New York, New York, United States, 10016

Withdrawn

14

University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, United States, 27599

Actively Recruiting

15

Atrium Health Levine Children's Hospital

Charlotte, North Carolina, United States, 28203

Completed

16

Duke Molecular Physiology Institute

Durham, North Carolina, United States, 22710

Actively Recruiting

17

Nationwide Children's Hospital

Columbus, Ohio, United States, 43205

Actively Recruiting

18

University of Oklahoma Health Sciences Center (OUHSC)

Oklahoma City, Oklahoma, United States, 73104

Actively Recruiting

19

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States, 19104

Actively Recruiting

20

St. Christopher's Hospital for Children

Philadelphia, Pennsylvania, United States, 19134

Withdrawn

21

Texas Children's Hospital

Houston, Texas, United States, 77030

Actively Recruiting

22

UT Health - John P. and Kathrine G. McGovern Medical School

Houston, Texas, United States, 77030

Withdrawn

23

Seattle Children's Hospital

Seattle, Washington, United States, 98105

Actively Recruiting

24

Uniklinik Köln, Klinik und Poliklinik für Kinder- und Jugendmedizin

Cologne, Germany, 50937

Actively Recruiting

25

Universitätsklinikum Hamburg-Eppendorf

Hamburg, Germany, 20246

Actively Recruiting

26

Universitätsklinikum Heidelberg - Angelika Lautenschläger - Kinderklinik

Heidelberg, Germany, 69120

Actively Recruiting

27

Policlinico Bari Ospedale Pediatrico Giovanni XXIII

Bari, Italy, 70126

Actively Recruiting

28

IRCCS Istituto Giannina Gaslini

Genova, Italy, 16147

Actively Recruiting

29

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico

Milan, Italy, 20122

Actively Recruiting

30

Azienda Ospedale Università di Padova

Padova, Italy, 35128

Actively Recruiting

31

Ospedale Pediatrico Bambino Gesù

Roma, Italy, 00165

Actively Recruiting

32

Emma Kinderziekenhuis

Amsterdam, Netherlands, 1105 AZ

Actively Recruiting

33

Radboud Universitair Medisch Centrum

Nijmegen, Netherlands, 6525 GA

Withdrawn

34

Uniwersytecki Szpital Dziecięcy w Krakowie

Krakow, Poland, 30-663

Actively Recruiting

35

Instytut Centrum Zdrowia Matki Polki

Lodz, Poland, 93-338

Withdrawn

36

Instytut Pomnik - Centrum Zdrowia Dziecka

Warsaw, Poland, 04-730

Withdrawn

37

Hospital Universitari Vall d'Hebrón

Barcelona, Spain, 08035

Actively Recruiting

38

Hospital Universitario 12 de Octubre

Madrid, Spain, 28041

Actively Recruiting

39

Hospital Universitario La Paz

Madrid, Spain, 28046

Actively Recruiting

40

Hospital Universitario Virgen del Rocío

Seville, Spain, 41013

Actively Recruiting

41

Drottning Silvias Barn- och Ungdomssjukhus

Gothenburg, Sweden, 416 85

Actively Recruiting

42

Karolinska Universitetssjukhuset Huddinge

Stockholm, Sweden, 141 86

Actively Recruiting

43

University Hospitals Bristol and Weston NHS Foundation Trust, Bristol Royal Hospital for Children

Bristol, United Kingdom, BS2 8BJ

Actively Recruiting

44

NHS Greater Glasgow and Clyde, Royal Hospital for Children

Glasgow, United Kingdom, G51 4TF

Actively Recruiting

45

Alder Hey Children's NHS Foundation Trust

Liverpool, United Kingdom, L12 2AP

Actively Recruiting

46

Great Ormond Street Hospital for Children NHS Foundation Trust

London, United Kingdom, WC1N3JH

Actively Recruiting

47

Manchester University NHS Foundation Trust

Manchester, United Kingdom, M13 9WL

Actively Recruiting

Loading map...

Research Team

T

Travere Call Center

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NON_RANDOMIZED

Model

PARALLEL

Primary Purpose

TREATMENT

Number of Arms

3

Not the Right Trial for You?

Explore thousands of other clinical trials that might be a better match.
Sign up to get personalized trial recommendations delivered to your inbox.

Already have an account? Log in here