Actively Recruiting

Phase 1
Phase 2
Age: 12Years +
All Genders
NCT04521231

A Study of Subcutaneous Blinatumomab Administration in Participants With R/R and MRD+ B-ALL

Led by Amgen · Updated on 2026-05-01

281

Participants Needed

109

Research Sites

437 weeks

Total Duration

On this page

Sponsors

A

Amgen

Lead Sponsor

B

BeOne Medicines

Collaborating Sponsor

AI-Summary

What this Trial Is About

The Phase I part of the study aims to evaluate the safety, efficacy, and tolerability of subcutaneous (SC) blinatumomab for treatment of Relapsed or Refractory B cell Precursor Acute Lymphoblastic Leukemia (R/R B-ALL), to determine the maximum tolerated dose (MTD), and recommended phase 2 dose(s) (RP2D) of SC administered blinatumomab. The Phase II part of the study will evaluate the safety, efficacy, and tolerability of SC blinatumomab for treatment of R/R B-ALL and Minimum Residual Disease Positive (MRD+) B-ALL in participants 12 years old and greater. It will also conduct a clinical pharmacokinetic (PK) evaluation of SC1 and SC2 blinatumomab formulations.

CONDITIONS

Official Title

A Study of Subcutaneous Blinatumomab Administration in Participants With R/R and MRD+ B-ALL

Who Can Participate

Age: 12Years +
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • For Phase IIC, Dose Escalation, and Dose Expansion: 18 years or older (or legal adult age in your country if higher).
  • For Phase IIRa and IIMa: 17 years or older at consent.
  • For Phase IIRb and IIMb: between 12 and less than 17 years at consent.
  • Diagnosed with Relapsed or Refractory B-precursor ALL.
  • Relapsed or Refractory B-precursor ALL after first salvage therapy.
  • Relapsed B-precursor ALL after allogenic hematopoietic stem cell transplant.
  • Bone marrow blasts 5% or higher for Ph-IIR, Ph-IIC, Dose escalation, and Dose expansion.
  • Bone marrow blasts between 0.01% and less than 5% for Phase IIM.
  • Availability of appropriate bone marrow samples for Phase IIM.
  • ECOG performance status 0 to 2 for participants 18 years or older.
  • Karnofsky score 50% or higher for ages 16 to under 18.
  • Lansky score 50% or higher for under 16 years.
  • Participants intolerant or refractory to prior tyrosine kinase inhibitors are eligible.
  • For Phase IIM: Blood counts must meet minimum levels (ANC ≥ 500/μL, platelets ≥ 50,000/μL with transfusion allowed, hemoglobin ≥ 9 g/dL with transfusion allowed).
Not Eligible

You will not qualify if you...

  • Active leukemia in the central nervous system with clinical signs or cerebrospinal fluid involvement.
  • History or presence of serious central nervous system disorders such as epilepsy, seizures, stroke, severe brain injuries, dementia, Parkinson's disease, psychosis, or severe neurotoxicity from prior treatments.
  • Isolated extramedullary disease.
  • For Phase IIM: presence of current extramedullary disease or circulating leukemia blasts.
  • Current or history of autoimmune disease with risk of CNS involvement.
  • Active graft versus host disease requiring immunosuppressive treatment.
  • Acute or uncontrolled chronic infections or other conditions that could worsen with treatment.
  • Testicular leukemia.
  • History of other cancers within 3 years before starting study treatment (with some exceptions).
  • Stem cell transplant within 12 weeks before study treatment.
  • Recent chemotherapy within 2 weeks before study treatment (exceptions apply).
  • Immunotherapy within 4 weeks before study treatment.
  • Prior CD19-directed therapies allowed if treatment ended over 4 weeks ago with no CNS complications.
  • Participation in other investigational studies within 30 days or 5 half-lives.
  • Abnormal lab tests at screening.
  • Pregnant or breastfeeding females or planning pregnancy during treatment and shortly after.

AI-Screening

AI-Powered Screening

Complete this quick 3-step screening to check your eligibility

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Trial Site Locations

Total: 109 locations

1

University of California San Francisco Fresno at Community Cancer Institute

Clovis, California, United States, 93611

Actively Recruiting

2

City of Hope National Medical Center

Duarte, California, United States, 91010

Actively Recruiting

3

University of Illinois Chicago

Chicago, Illinois, United States, 60612

Actively Recruiting

4

Johns Hopkins University

Baltimore, Maryland, United States, 21287

Actively Recruiting

5

C.S. Mott Children's Hospital - University of Michigan

Ann Arbor, Michigan, United States, 48109

Actively Recruiting

6

Roswell Park Comprehensive Cancer Center

Buffalo, New York, United States, 14263

Actively Recruiting

7

New York University Grossman School of Medicine and New York University Langone Hospitals

New York, New York, United States, 10016

Actively Recruiting

8

Albert Einstein College of Medicine - Montefiore Medical Center

The Bronx, New York, United States, 10467

Actively Recruiting

9

Childrens Hospital of Philadelphia

Philadelphia, Pennsylvania, United States, 19104

Actively Recruiting

10

St Jude Childrens Research Hospital

Memphis, Tennessee, United States, 38105

Actively Recruiting

11

University of Texas MD Anderson Cancer Center

Houston, Texas, United States, 77030

Actively Recruiting

12

Fred Hutchinson Cancer Center

Seattle, Washington, United States, 98109-1023

Actively Recruiting

13

Fred Hutchinson Cancer Center

Seattle, Washington, United States, 98109-1023

Completed

14

The Medical College of Wisconsin

Milwaukee, Wisconsin, United States, 53226

Actively Recruiting

15

Hospital Italiano de Buenos Aires

Ciudad Autonoma de Buenos Aires, Buenos Aires, Argentina, C1199ABB

Actively Recruiting

16

Sanatorio Allende

Córdoba, Córdoba Province, Argentina, X5000JHQ

Actively Recruiting

17

Instituto Alexander Fleming

Buenos Aires, Argentina, C1426ANZ

Actively Recruiting

18

Cemic - Centro de Educacion Medica e Investigaciones Clinicas Norberto Quirno

Ciudad Autonoma Buenos Aires, Argentina, C1431FWO

Actively Recruiting

19

Sydney Childrens Hospital

Randwick, New South Wales, Australia, 2031

Actively Recruiting

20

Westmead Hospital

Westmead, New South Wales, Australia, 2145

Actively Recruiting

21

Queensland Childrens Hospital

South Brisbane, Queensland, Australia, 4101

Actively Recruiting

22

Royal Adelaide Hospital

Adelaide, South Australia, Australia, 5000

Actively Recruiting

23

Monash Medical Centre

Clayton, Victoria, Australia, 3168

Actively Recruiting

24

Austin Health, Austin Hospital

Heidelberg, Victoria, Australia, 3084

Terminated

25

The Alfred Hospital

Melbourne, Victoria, Australia, 3004

Actively Recruiting

26

Perth Childrens Hospital

Nedlands, Western Australia, Australia, 6909

Actively Recruiting

27

Universitaetsklinikum Allgemeines Krankenhaus Wien

Vienna, Austria, 1090

Completed

28

Centre Hospitalier Universitaire-Universite Catholique de Louvain Namur-Site Godinne

Yvoir, Belgium, 5530

Actively Recruiting

29

Hospital Sirio Libanes Brasilia

Brasília, Federal District, Brazil, 70200-730

Actively Recruiting

30

Instituto Medicina Integral Imip

Recife, Pernambuco, Brazil, 50070-902

Actively Recruiting

31

Hosp de Clinicas de Porto Alegre

Porto Alegre, Rio Grande do Sul, Brazil, 90035-903

Actively Recruiting

32

Fundacao Amaral Carvalho

Jaú, São Paulo, Brazil, 17210-120

Actively Recruiting

33

Hosp Clin Fac Med Ribeirao Preto Usp

Ribeirão Preto, São Paulo, Brazil, 14048-900

Actively Recruiting

34

Instituto Onco Ped Graac Unifesp

São Paulo, São Paulo, Brazil, 04039-001

Actively Recruiting

35

Arthur J E Child Comprehensive Cancer Centre

Calgary, Alberta, Canada, T2N 2T9

Actively Recruiting

36

University of Alberta

Edmonton, Alberta, Canada, T6G 2P4

Actively Recruiting

37

Vancouver General Hospital, Gordon and Leslie Diamond Health Care Centre

Vancouver, British Columbia, Canada, V5Z 1M9

Actively Recruiting

38

The Hospital for Sick Children

Toronto, Ontario, Canada, M5G 1E8

Actively Recruiting

39

Princess Margaret Cancer Centre

Toronto, Ontario, Canada, M5G 2M9

Actively Recruiting

40

Beijing Childrens Hospital, Capital Medical University

Beijing, Beijing Municipality, China, 100045

Actively Recruiting

41

Fujian Medical University Union Hospital

Fuzhou, Fujian, China, 350001

Actively Recruiting

42

Zhujiang Hospital of Southern Medical Unversity

Guangzhou, Guangdong, China, 510280

Actively Recruiting

43

Nanfang Hospital, Southern Medical University

Guangzhou, Guangdong, China, 510515

Actively Recruiting

44

Henan Cancer Hospital

Zhengzhou, Henan, China, 450008

Actively Recruiting

45

Union Hospital Tongji Medical College Huazhong University of Science and Technology

Wuhan, Hubei, China, 430022

Actively Recruiting

46

Children's Hospital of Soochow University

Suzhou, Jiangsu, China, 215002

Actively Recruiting

47

The First Affiliated Hospital of Soochow University

Suzhou, Jiangsu, China, 215031

Actively Recruiting

48

The Affiliated Hospital of Qingdao University

Qingdao, Shandong, China, 266003

Actively Recruiting

49

The First Affiliated Hospital Of Xi'An Jiaotong Unversity

Xi’an, Shanxi, China, 710061

Actively Recruiting

50

Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences

Tianjin, Tianjin Municipality, China, 300020

Actively Recruiting

51

Institute of Hematology and Blood Diseases Hospital, Chinese Academy of Medical Sciences

Tianjin, Tianjin Municipality, China, 300020

Actively Recruiting

52

The First Affiliated Hospital of Zhejiang University School of Medicine

Hangzhou, Zhejiang, China, 310003

Actively Recruiting

53

The Childrens Hospital, Zhejiang University School of Medicine

Hangzhou, Zhejiang, China, 310005

Actively Recruiting

54

Centre Hospitalier de Versailles - Hopital Andre Mignot

Le Chesnay, France, 78157

Actively Recruiting

55

Centre Hospitalier Regional Universitaire de Lille - Hopital Claude Huriez

Lille, France, 59000

Actively Recruiting

56

Centre Hospitalier Universitaire de Nice - Hopital de l Archet

Nice, France, 06202

Actively Recruiting

57

Hopital Saint Louis

Paris, France, 75010

Actively Recruiting

58

Hopital Saint Antoine

Paris, France, 75012

Actively Recruiting

59

Hopital Robert Debre

Paris, France, 75019

Actively Recruiting

60

Hopital Lyon Sud

Pierre-Bénite, France, 69645

Actively Recruiting

61

Institut Universitaire du Cancer Toulouse Oncopole

Toulouse, France, 31059

Actively Recruiting

62

Universitaetsklinikum Augsburg

Augsburg, Germany, 86156

Actively Recruiting

63

Charite - Universitaetsmedizin Berlin, Campus Benjamin Franklin

Berlin, Germany, 12203

Actively Recruiting

64

Charite - Universitaetsmedizin Berlin, Campus Virchow

Berlin, Germany, 13353

Actively Recruiting

65

Universitaetsklinikum Koeln

Cologne, Germany, 50937

Actively Recruiting

66

Universitaetsklinikum Jena

Jena, Germany, 07747

Actively Recruiting

67

Universitaetsklinikum Leipzig

Leipzig, Germany, 04103

Actively Recruiting

68

Universitaetsklinikum Tuebingen

Tübingen, Germany, 72076

Completed

69

Universitaetsklinikum Tuebingen

Tübingen, Germany, 72076

Actively Recruiting

70

Universitatsklinikum Ulm

Ulm, Germany, 89081

Completed

71

Queen Mary Hospital, The University of Hong Kong

Hong Kong, Hong Kong

Actively Recruiting

72

Hong Kong Childrens Hospital

Kowloon Bay, Hong Kong

Actively Recruiting

73

Rambam Medical Center

Haifa, Israel, 3109601

Actively Recruiting

74

Rabin Medical Center - Beilinson Hospital

Petah Tikva, Israel, 4941492

Actively Recruiting

75

Azienda Socio Sanitaria Territoriale Papa Giovanni xxiii

Bergamo, Italy, 24127

Actively Recruiting

76

IRCCS Azienda Ospedaliero Universitaria di Bologna Policlinico di Sant Orsola

Bologna, Italy, 40138

Actively Recruiting

77

Azienda Socio Sanitaria Territoriale degli Spedali Civili di Brescia

Brescia, Italy, 25123

Actively Recruiting

78

Azienda Ospedaliero Universitaria Policlinico G Rodolico - San Marco Presidio Ospedaliero G Rodolico

Catania, Italy, 95123

Actively Recruiting

79

IRCCS Ospedale San Raffaele

Milan, Italy, 20132

Completed

80

Azienda Ospedaliera di Rilievo Nazionale Santobono Pausilipon

Naples, Italy, 80123

Actively Recruiting

81

Azienda Ospedaliera Policlinico Umberto I

Roma, Italy, 00161

Actively Recruiting

82

IRCCS Ospedale Pediatrico Bambino Gesu

Roma, Italy, 00165

Actively Recruiting

83

Akita University Hospital

Akita, Akita, Japan, 010-8543

Actively Recruiting

84

National Cancer Center Hospital East

Kashiwa-shi, Chiba, Japan, 277-8577

Actively Recruiting

85

Fukushima Medical University Hospital

Fukushima, Fukushima, Japan, 960-1295

Actively Recruiting

86

Yokohama City University Medical Center

Yokohama, Kanagawa, Japan, 232-0024

Actively Recruiting

87

Kanagawa Childrens Medical Center

Yokohami-shi, Kanagawa, Japan, 232-8555

Actively Recruiting

88

Erasmus Medisch Centrum

Rotterdam, Netherlands, 3015 CN

Actively Recruiting

89

Prinses Maxima Centrum

Utrecht, Netherlands, 3584 CS

Actively Recruiting

90

Institutul Oncologic Prof Dr Ion Chiricuta

Cluj-Napoca, Romania, 400015

Actively Recruiting

91

Chonnam National University Hwasun Hospital

Hwasun-gun, Jeollanam-do, South Korea, 58128

Actively Recruiting

92

Seoul National University Hospital

Seoul, South Korea, 03080

Actively Recruiting

93

The Catholic University of Korea Seoul St Marys Hospital

Seoul, South Korea, 06591

Actively Recruiting

94

Hospital Universitario Virgen del Rocio

Seville, Andalusia, Spain, 41013

Completed

95

Hospital Universitario Marques de Valdecilla

Santander, Cantabria, Spain, 39008

Actively Recruiting

96

Complejo Asistencial Universitario de Salamanca Hospital Universitario de Salamanca

Salamanca, Castille and León, Spain, 37007

Actively Recruiting

97

Institut Catala d Oncologia Badalona Hospital Universitari Germans Trias i Pujol

Badalona, Catalonia, Spain, 08916

Actively Recruiting

98

Hospital Universitari Vall d Hebron

Barcelona, Catalonia, Spain, 08035

Actively Recruiting

99

Hospital Sant Joan de Deu

Esplugues de Llobregat, Catalonia, Spain, 08950

Actively Recruiting

100

Institut Catala d Oncologia Hospitalet Hospital Duran i Reynals

L'Hospitalet de Llobregat, Catalonia, Spain, 08908

Actively Recruiting

101

Clinica Universidad de Navarra

Pamplona, Navarre, Spain, 31008

Actively Recruiting

102

Hospital Clinico Universitario de Valencia

Valencia, Valencia, Spain, 46010

Actively Recruiting

103

Hospital Universitario Infantil Niño Jesus

Madrid, Spain, 28009

Actively Recruiting

104

Hospital Universitario 12 de Octubre

Madrid, Spain, 28041

Actively Recruiting

105

Saglik Bilimleri Universitesi Gulhane Egitim ve Arastirma Hastanesi

Ankara, Turkey (Türkiye), 06010

Actively Recruiting

106

Ankara Bilkent Sehir Hastanesi

Ankara, Turkey (Türkiye), 06800

Actively Recruiting

107

Bagcilar Medipol Mega Universite Hastanesi

Istanbul, Turkey (Türkiye), 34214

Actively Recruiting

108

Istanbul Florence Nightingale Hastanesi

Istanbul, Turkey (Türkiye), 34214

Actively Recruiting

109

Izmir Ekonomi Universitesi Medical Point Hastanesi

Izmir, Turkey (Türkiye), 35575

Actively Recruiting

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Research Team

A

Amgen Call Center

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NON_RANDOMIZED

Model

SEQUENTIAL

Primary Purpose

TREATMENT

Number of Arms

5

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