Actively Recruiting

Phase 1
Age: 0 - 21Years
All Genders
NCT05101551

Study of Talazoparib in Combination With Chemotherapy in Relapsed Pediatric AML to Determine Safety and Efficacy

Led by Norman J. Lacayo · Updated on 2026-04-22

34

Participants Needed

9

Research Sites

214 weeks

Total Duration

On this page

Sponsors

N

Norman J. Lacayo

Lead Sponsor

G

Gateway for Cancer Research

Collaborating Sponsor

AI-Summary

What this Trial Is About

This is a Phase 1, open label, multicenter, dose finding study with dose expansion intended to evaluate the safety and tolerability of talazoparib in combination with conventional chemotherapy. Preliminary estimates of efficacy will be obtain through a dose expansion cohort receiving the maximum tolerated dose from the dose escalation phase of the study. This study aims to determine the safety of talazoparib in combination with conventional chemotherapy and to establish the maximum tolerated dose of all 3 drugs when given in combination. A preliminary estimate of efficacy through a dose expansion phase is a secondary aim.

CONDITIONS

Official Title

Study of Talazoparib in Combination With Chemotherapy in Relapsed Pediatric AML to Determine Safety and Efficacy

Who Can Participate

Age: 0 - 21Years
All Genders

Eligibility Criteria

Eligible

You may qualify if you...

  • Age 21 years or younger
  • Diagnosis of acute myeloid leukemia (AML) or acute leukemia of ambiguous lineage that is refractory or relapsed
  • Bone marrow with at least 5% leukemic blasts by flow cytometry or evidence of leukemia by specific tests or peripheral blood
  • More than 60 days since hematopoietic stem cell transplant
  • No active graft versus host disease and off calcineurin inhibitors for at least 28 days if previously transplanted
  • At least 14 days since last myelosuppressive therapy or gemtuzumab ozogamicin, with resolved toxicities
  • At least 24 hours since low-dose or non-myelosuppressive therapy
  • Lansky or Karnofsky performance score of 50 or higher
  • White blood cell count 50,000/uL or less, possibly controlled with cytoreductive therapy
  • Total bilirubin less than or equal to 2 times institutional upper limit of normal for age
  • AST and ALT less than or equal to 5 times upper limit of normal for age
  • Left ventricular ejection fraction 40% or higher or ECHO shortening fraction 25% or higher
  • Estimated serum creatinine clearance 60 mL/min/1.73m2 or higher
Not Eligible

You will not qualify if you...

  • Receiving or planning to receive any other cancer therapy including chemotherapy, radiation, immunotherapy, or biologic therapy
  • Diagnosis of Down syndrome
  • Diagnosis of Acute Promyelocytic Leukemia (APL) or Juvenile Myelomonocytic Leukemia (JMML)
  • Diagnosis of Bone Marrow Failure Syndrome
  • Pregnancy or unwillingness to use effective birth control
  • Female subjects with infants who do not agree to abstain from breastfeeding
  • Inability or unwillingness of legal guardian or representative to provide written informed consent
  • Uncontrolled systemic fungal, bacterial, viral, or other infections

AI-Screening

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Trial Site Locations

Total: 9 locations

1

Phoenix Children's Hospital

Phoenix, Arizona, United States, 85016

Actively Recruiting

2

Arkansas Children's Hospital

Little Rock, Arkansas, United States, 72202

Actively Recruiting

3

City of Hope

Duarte, California, United States, 91010

Actively Recruiting

4

Stanford University

Stanford, California, United States, 94305

Actively Recruiting

5

Cincinnati Children's Hospital

Cincinnati, Ohio, United States, 45229

Actively Recruiting

6

Pennsylvania State University Hershey Medical Center

Hershey, Pennsylvania, United States, 17033-0850

Actively Recruiting

7

St. Jude Children's Research Hospital

Memphis, Tennessee, United States, 38105

Actively Recruiting

8

University of Utah

Salt Lake City, Utah, United States, 84108

Actively Recruiting

9

University of Wisconsin Carbone Cancer Center

Madison, Wisconsin, United States, 53792

Actively Recruiting

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Research Team

S

Stefania Chirita

CONTACT

How is the study designed?

Study Type

INTERVENTIONAL

Masking

NONE

Allocation

NA

Model

SINGLE_GROUP

Primary Purpose

TREATMENT

Number of Arms

1

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Study of Talazoparib in Combination With Chemotherapy in Relapsed Pediatric AML to Determine Safety and Efficacy | DecenTrialz